Clinical utility of BRCA and ATM mutation status in circulating tumour DNA for treatment selection in advanced pancreatic cancer.


Journal

British journal of cancer
ISSN: 1532-1827
Titre abrégé: Br J Cancer
Pays: England
ID NLM: 0370635

Informations de publication

Date de publication:
28 Aug 2024
Historique:
received: 27 12 2023
accepted: 20 08 2024
revised: 10 08 2024
medline: 31 8 2024
pubmed: 31 8 2024
entrez: 28 8 2024
Statut: aheadofprint

Résumé

Identification of homologous recombination deficiency (HRD) remains a challenge in advanced pancreatic cancer (APC). We investigated the utility of circulating tumour DNA (ctDNA) profiling in the assessment of BRCA1/2 and ATM mutation status and treatment selection in APC. We analysed clinical and ctDNA data of 702 patients with APC enroled in GOZILA, a ctDNA profiling study using Guardant360. Inactivating BRCA1/2 and ATM mutations were detected in 4.8% (putative germline, 3.7%) and 4.4% (putative germline, 0.9%) of patients, respectively. Objective response (63.2% vs. 16.2%) and PFS (HR 0.55, 95% CI 0.32-0.93) on platinum-containing chemotherapy were significantly better in patients with putative germline BRCA1/2 (gBRCA) mutation than those without. In contrast, putative gBRCA mutation had no impact on the efficacy of gemcitabine plus nab-paclitaxel. In 2 patients treated with platinum-containing therapy, putative BRCA2 reversion mutations were detected. Three of seven patients with somatic BRCA mutations responded to platinum-containing therapy, while only one of four with putative germline ATM mutations did. One-third of somatic ATM mutations were in genomic loci associated with clonal haematopoiesis. Comprehensive ctDNA profiling provides clinically relevant information regarding HRD status. It can be a practical, convenient option for HRD screening in APC.

Sections du résumé

BACKGROUND BACKGROUND
Identification of homologous recombination deficiency (HRD) remains a challenge in advanced pancreatic cancer (APC). We investigated the utility of circulating tumour DNA (ctDNA) profiling in the assessment of BRCA1/2 and ATM mutation status and treatment selection in APC.
METHODS METHODS
We analysed clinical and ctDNA data of 702 patients with APC enroled in GOZILA, a ctDNA profiling study using Guardant360.
RESULTS RESULTS
Inactivating BRCA1/2 and ATM mutations were detected in 4.8% (putative germline, 3.7%) and 4.4% (putative germline, 0.9%) of patients, respectively. Objective response (63.2% vs. 16.2%) and PFS (HR 0.55, 95% CI 0.32-0.93) on platinum-containing chemotherapy were significantly better in patients with putative germline BRCA1/2 (gBRCA) mutation than those without. In contrast, putative gBRCA mutation had no impact on the efficacy of gemcitabine plus nab-paclitaxel. In 2 patients treated with platinum-containing therapy, putative BRCA2 reversion mutations were detected. Three of seven patients with somatic BRCA mutations responded to platinum-containing therapy, while only one of four with putative germline ATM mutations did. One-third of somatic ATM mutations were in genomic loci associated with clonal haematopoiesis.
CONCLUSION CONCLUSIONS
Comprehensive ctDNA profiling provides clinically relevant information regarding HRD status. It can be a practical, convenient option for HRD screening in APC.

Identifiants

pubmed: 39198618
doi: 10.1038/s41416-024-02834-0
pii: 10.1038/s41416-024-02834-0
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Informations de copyright

© 2024. The Author(s), under exclusive licence to Springer Nature Limited.

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Auteurs

Kentaro Sudo (K)

Department of Gastroenterology, Chiba Cancer Center, Chiba, Japan.

Yoshiaki Nakamura (Y)

Department of Gastroenterology and Gastrointestinal Oncology, National Cancer Center Hospital East, Kashiwa, Japan. yoshinak@east.ncc.go.jp.
Translational Research Support Office, Department for the Promotion of Drug and Diagnostic Development, National Cancer Center Hospital East, Kashiwa, Japan. yoshinak@east.ncc.go.jp.

Makoto Ueno (M)

Department of Gastroenterology, Kanagawa Cancer Center, Yokohama, Japan.

Masayuki Furukawa (M)

Department of Hepato-Biliary-Pancreatology, National Hospital Organization Kyushu Cancer Center, Fukuoka, Japan.

Nobumasa Mizuno (N)

Department of Gastroenterology, Aichi Cancer Center Hospital, Nagoya, Japan.

Yasuyuki Kawamoto (Y)

Division of Cancer Center, Hokkaido University Hospital, Sapporo, Japan.

Naohiro Okano (N)

Department of Medical Oncology, Kyorin University Faculty of Medicine, Mitaka, Japan.

Kumiko Umemoto (K)

Department of Clinical Oncology, St. Marianna University School of Medicine, Kawasaki, Japan.

Akinori Asagi (A)

Department of Gastrointestinal Medical Oncology, National Hospital Organization Shikoku Cancer Center, Matsuyama, Japan.

Masato Ozaka (M)

Department of Hepato-Biliary-Pancreatic Medicine, Cancer Institute Hospital of Japanese Foundation for Cancer Research, Tokyo, Japan.

Koushiro Ohtsubo (K)

Department of Medical Oncology, Kanazawa University Hospital, Kanazawa, Japan.

Satoshi Shimizu (S)

Department of Gastroenterology, Saitama Cancer Center, Saitama, Japan.

Nobuhisa Matsuhashi (N)

Department of Gastroenterological Surgery and Pediatric Surgery, Gifu University, Graduate School of Medicine, Gifu, Japan.
Center for One Medicine Innovative Translational Research (COMIT), Gifu University, Gifu, Japan.

Shinji Itoh (S)

Department of Surgery and Science, Graduate School of Medical Sciences, Kyushu University, Fukuoka, Japan.

Toshihiko Matsumoto (T)

Department of Medical Oncology, Kobe City Medical Center General Hospital, Kobe, Japan.

Taroh Satoh (T)

Center for Cancer Genomics and Precision Medicine, Osaka University Hospital, Suita, Japan.

Hiroyuki Okuyama (H)

Department of Medical Oncology, Kagawa University Hospital, Kagawa, Japan.

Masahiro Goto (M)

Cancer Chemotherapy Center, Osaka Medical and Pharmaceutical University Hospital, Osaka, Japan.

Hiroko Hasegawa (H)

Department of Gastroenterology and Hepatology, NHO, Osaka National Hospital, Osaka, Japan.

Yoshiyuki Yamamoto (Y)

Department of Gastroenterology, University of Tsukuba Hospital, Tsukuba, Japan.

Justin I Odegaard (JI)

Guardant Health, Redwood City, CA, USA.

Hideaki Bando (H)

Department of Gastroenterology and Gastrointestinal Oncology, National Cancer Center Hospital East, Kashiwa, Japan.
Translational Research Support Office, Department for the Promotion of Drug and Diagnostic Development, National Cancer Center Hospital East, Kashiwa, Japan.

Takayuki Yoshino (T)

Department of Gastroenterology and Gastrointestinal Oncology, National Cancer Center Hospital East, Kashiwa, Japan.

Masafumi Ikeda (M)

Department of Hepatobiliary and Pancreatic Oncology, National Cancer Center Hospital East, Kashiwa, Japan.

Chigusa Morizane (C)

Department of Hepatobiliary and Pancreatic Oncology, National Cancer Center Hospital, Tokyo, Japan.

Classifications MeSH