Comprehensive Screening of Genetic Variants in the Coding Region of

F8 FVIII hemophilia A inhibitors mutation pathogenic variants whole sequence exome

Journal

Life (Basel, Switzerland)
ISSN: 2075-1729
Titre abrégé: Life (Basel)
Pays: Switzerland
ID NLM: 101580444

Informations de publication

Date de publication:
21 Aug 2024
Historique:
received: 22 07 2024
revised: 08 08 2024
accepted: 15 08 2024
medline: 31 8 2024
pubmed: 31 8 2024
entrez: 29 8 2024
Statut: epublish

Résumé

Hemophilia A is an X-linked disorder characterized by quantitative deficiency of coagulation factor VIII (FVIII) caused by pathogenic variants in the factor 8 (

Identifiants

pubmed: 39202783
pii: life14081041
doi: 10.3390/life14081041
pmc: PMC11355106
pii:
doi:

Types de publication

Journal Article

Langues

eng

Références

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Auteurs

Samuel Sarmiento Doncel (S)

Integral Solutions SD SAS, Integral Solutions Research, Bogota 110121, Colombia.
Life Sciences and Health Research Group, Graduates School, CES University, Medellin 050021, Colombia.
Doctoral School, Catholic University of Valencia San Vicente Mártir (UCV), 46002 Valencia, Spain.

Ronald Guillermo Peláez (RG)

Life Sciences and Health Research Group, Graduates School, CES University, Medellin 050021, Colombia.

Pablo Lapunzina (P)

Instituto de Genética Médica y Molecular (INGEMM), IdiPaz, Hospital Universitario La Paz, 28046 Madrid, Spain.
CIBERER, Centro de Investigación en Red de Enfermedades Raras, Instituto de Salud Carlos III, 28029 Madrid, Spain.
ITHACA, European Reference Network on Rare Congenital Malformations and Rare Intellectual Disability, 75019 Paris, France.

Fernando F Corrales-Medina (FF)

Division of Pediatric Hematology-Oncology, Department of Pediatrics, University of Miami-Miller School of Medicine, Miami, FL 33136, USA.
University of Miami-Hemophilia Treatment Center, Miami, FL 33136, USA.

Gina Alejandra Díaz Mosquera (GA)

Integral Solutions SD SAS, Integral Solutions Research, Bogota 110121, Colombia.

Santiago Bonanad (S)

Hospital Universitario y Politécnico La Fe, 46026 Valencia, Spain.

Javier Mauricio Cortes (JM)

Integral Solutions SD SAS, Integral Solutions Research, Bogota 110121, Colombia.

Mario Cazalla (M)

Instituto de Genética Médica y Molecular (INGEMM), IdiPaz, Hospital Universitario La Paz, 28046 Madrid, Spain.
CIBERER, Centro de Investigación en Red de Enfermedades Raras, Instituto de Salud Carlos III, 28029 Madrid, Spain.

Natalia Gallego (N)

Instituto de Genética Médica y Molecular (INGEMM), IdiPaz, Hospital Universitario La Paz, 28046 Madrid, Spain.
CIBERER, Centro de Investigación en Red de Enfermedades Raras, Instituto de Salud Carlos III, 28029 Madrid, Spain.
ITHACA, European Reference Network on Rare Congenital Malformations and Rare Intellectual Disability, 75019 Paris, France.

Felipe Querol-Giner (F)

Physiotherapy in Motion Multispeciality Research Group (PTinMOTION), Department of Physiotherapy, University of Valencia, 46010 Valencia, Spain.

Jair Tenorio (J)

Instituto de Genética Médica y Molecular (INGEMM), IdiPaz, Hospital Universitario La Paz, 28046 Madrid, Spain.
CIBERER, Centro de Investigación en Red de Enfermedades Raras, Instituto de Salud Carlos III, 28029 Madrid, Spain.
ITHACA, European Reference Network on Rare Congenital Malformations and Rare Intellectual Disability, 75019 Paris, France.
BITGENETIC LAB, Qube Technology Park, Tres Cantos, 28460 Madrid, Spain.

José A López Guerrero (JA)

Doctoral School, Catholic University of Valencia San Vicente Mártir (UCV), 46002 Valencia, Spain.
Department of Pathology, Medical School, Catholic University of Valencia, San Vicente Martir, 46010 Valencia, Spain.
Laboratory of Molecular Biology, Fundación Instituto Valenciano de Oncología, 46009 Valencia, Spain.

Classifications MeSH