Choice of Frontline Tyrosine-Kinase Inhibitor and Early Events in Very Elderly Patients With Chronic Myeloid Leukemia in Chronic Phase: A "Campus CML" Study.

chronic myeloid leukemia comorbidities dose optimization efficacy older safety tyrosine kinase inhibitor very elderly

Journal

European journal of haematology
ISSN: 1600-0609
Titre abrégé: Eur J Haematol
Pays: England
ID NLM: 8703985

Informations de publication

Date de publication:
12 Sep 2024
Historique:
revised: 14 08 2024
received: 11 03 2024
accepted: 16 08 2024
medline: 12 9 2024
pubmed: 12 9 2024
entrez: 12 9 2024
Statut: aheadofprint

Résumé

The study aimed to evaluate the utilization of frontline TKI therapy in a large cohort of elderly CP-CML patients. A retrospective analysis was conducted on 332 CP-CML patients aged 75 years or older among 1929 diagnosed from January 2012 to December 2019 followed at 36 participating Hematology Centers involved in the "Campus CML" project. Among the patients analyzed, 85.8% received imatinib (IM) while 14.2% received second-generation TKIs (2G-TKI), 59.5% dasatinib, and 40.5% nilotinib. Most patients initiated IM at standard dose (67.3%) while 32.7% at reduced dose. A similar trend was observed with 2G-TKIs. The cumulative incidence of permanent TKI discontinuation at 12 months was 28.4%, primarily due to primary resistance (10.1%) and extra-hematologic toxicity (9.5%), with no significant difference between IM and 2G-TKI groups. Following the introduction of generic IM in Italy in 2018, IM usage increased significantly compared with 2G-TKIs. IM was in our Centers the preferred frontline therapy for older CP-CML patients, with increasing utilization after the introduction of generic formulations. However, 2G-TKIs are still used in a substantial proportion of patients, suggesting individualized physician assessments regarding patient suitability and expectations. Further investigation is needed to assess efficacy and safety of reduced TKI doses in this patient population.

Identifiants

pubmed: 39263855
doi: 10.1111/ejh.14299
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Informations de copyright

© 2024 The Author(s). European Journal of Haematology published by John Wiley & Sons Ltd.

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Auteurs

C Bucelli (C)

Hematology Division, Foundation IRCCS Ca' Granda-Ospedale Maggiore Policlinico, Milan, Italy.

I Capodanno (I)

Hematology Unit, Azienda Unità Sanitaria Locale-IRCCS, Reggio Emilia, Italy.

M C Miggiano (MC)

Hematology Department, San Bortolo Hospital, Vicenza, Italy.

F Cavazzini (F)

Hematology Unit, University of Ferrara, Ferrara, Italy.

S Leonetti Crescenzi (SL)

Hematology, San Giovanni Hospital, Rome, Italy.

S Russo (S)

Hematology, University of Messina, Messina, Italy.

I Carmosino (I)

Hematology, Department of Translational and Precision Medicine, Policlinico Umberto I-Sapienza University, Rome, Italy.

M Annunziata (M)

Hematology Unit, Cardarelli Hospital, Naples, Italy.

F Sorà (F)

Institute of Hematology, Policlinico Universitario A. Gemelli, "Cattolica" University, Rome, Italy.

M Bonifacio (M)

Department of Medicine, Section of Hematology, University of Verona, Verona, Italy.

L Luciano (L)

Hematology, University Federico II, Naples, Italy.

G Caocci (G)

Department of Medical Sciences and Public Health, University of Cagliari, Cagliari, Italy.

G Loglisci (G)

Hematology, Vito Fazzi Hospital, Lecce, Italy.

C Elena (C)

Hematology, Policlinico San Matteo, University of Pavia, Pavia, Italy.

F Lunghi (F)

Division of Hematology and BMT, IRCCS San Raffaele Hospital, Milan, Italy.

R Mullai (R)

Division of Hematology and BMT, Department of Medical Area, University of Udine, Udine, Italy.

I Attolico (I)

Hematology and Transplantation Unit, University of Bari, Bari, Italy.

G Binotto (G)

Department of Medicine, Hematology and Clinical Immunology, University of Padua, Padua, Italy.

E Crisà (E)

Hematology, Ospedale Maggiore, Novara, Italy.

P Sportoletti (P)

Hematology, University of Perugia, Perugia, Italy.

A Di Veroli (A)

Hematology, Belcolle Hospital, Viterbo, Italy.

A R Scortechini (AR)

Hematology Unit, Azienda Ospedaliero Universitaria Ospedali Riuniti, Ancona, Italy.

A P Leporace (AP)

Hematology Unit Azienda Ospedaliero Universitaria Sant'Andrea, Roma, Italy.

A Maggi (A)

Hematology, San Giuseppe Moscati Hospital, Taranto, Italy.

M Crugnola (M)

Hematology, University of Parma, Parma, Italy.

F Stagno (F)

Hematology, Ferrarotto Hospital, Catania, Italy.

R Sancetta (R)

Hematology Unit, Dell'Angelo Hospital, Venezia-Mestre, Italy.

P Murgano (P)

Division of Hematology, Sant'Elia Hospital, Caltanissetta, Italy.

D Rapezzi (D)

Hematology, AO Santa Croce e Carle, Cuneo, Italy.

D Luzi (D)

Onco-Hematology Department, AO Santa Maria, Terni, Italy.

D I Vincelli (DI)

Hematology, Bianchi-Melacrino-Morelli Hospital, Reggio Calabria, Italy.

S Galimberti (S)

Department of Clinical and Experimental Medicine, Hematology, University of Pisa, Pisa, Italy.

M Bocchia (M)

Hematology, AOU Senese, Siena, Italy.

C Fava (C)

Hematology, Mauriziano Hospital, Torino, Italy.

A Malato (A)

Hematology, Cervello Hospital, Palermo, Italy.

E Abruzzese (E)

Hematology, Sant'Eugenio Hospital, Roma, Italy.

G Saglio (G)

Department of Clinical and Biological Sciences, University of Turin, Torino, Italy.

G Specchia (G)

School of Medicine, University of Bari, Bari, Italy.

M Breccia (M)

Hematology, Department of Translational and Precision Medicine, Policlinico Umberto I-Sapienza University, Rome, Italy.

A Iurlo (A)

Hematology Division, Foundation IRCCS Ca' Granda-Ospedale Maggiore Policlinico, Milan, Italy.

M Tiribelli (M)

Division of Hematology and BMT, Department of Medical Area, University of Udine, Udine, Italy.

R Latagliata (R)

Hematology, Belcolle Hospital, Viterbo, Italy.

Classifications MeSH