2q31 microdeletion syndrome with the velocardiofacial phenotype and review of the literature: a case report.


Journal

BMC pediatrics
ISSN: 1471-2431
Titre abrégé: BMC Pediatr
Pays: England
ID NLM: 100967804

Informations de publication

Date de publication:
09 Oct 2024
Historique:
received: 30 11 2022
accepted: 17 05 2024
medline: 10 10 2024
pubmed: 10 10 2024
entrez: 9 10 2024
Statut: epublish

Résumé

The 2q31 deletion results in a distinct phenotype characterized by varying degrees of developmental delay, short stature, facial dysmorphism, and variable limb defects. Dysmorphic features include microcephaly, downslanting palpebral fissures, a long and flat philtrum, micrognathia, and dysplastic, low-set ears. To date, comparative genomic hybridization has identified this deletion in 38 patients. Consequently, additional patients with comprehensive clinical data are required to fully understand the spectrum of clinical manifestation associated with a deletion in the 2q31 cytoband. We present the case of an 8-year-old female patient with clinical features of velocardiofacial syndrome, which include facial dysmorphism, congenital heart disease (persistent truncus arteriosus and ostium secundum-type atrial septal defect), and a seizure syndrome. Array comparative genomic hybridization revealed a non-continous deletion spanning cytobands 2q31.1-to 2q31.3, confirming a diagnosis of 2q31 microdeletion syndrome. The patient has undergone supportive therapies for swallowing and speech. Additionally, we provide a review of the literature on previous cases to give context. In this report, we present the first documented case of a complex, discontinuous deletion spanning in the 2q31-2q32 regions. This case contributes to our understanding of the phenotypic and mutational spectrum observed in individuals with deletions in these cytobands. It underscores the significance of employing high-resolution techniques and comprenhensive analysis in diagnosing patients with complex phenotypes. Such approaches are crucial for differentiating this condition from more common microdeletion syndromes, such as the 22q11 deletion syndrome.

Sections du résumé

BACKGROUND BACKGROUND
The 2q31 deletion results in a distinct phenotype characterized by varying degrees of developmental delay, short stature, facial dysmorphism, and variable limb defects. Dysmorphic features include microcephaly, downslanting palpebral fissures, a long and flat philtrum, micrognathia, and dysplastic, low-set ears. To date, comparative genomic hybridization has identified this deletion in 38 patients. Consequently, additional patients with comprehensive clinical data are required to fully understand the spectrum of clinical manifestation associated with a deletion in the 2q31 cytoband.
CASE PRESENTATION METHODS
We present the case of an 8-year-old female patient with clinical features of velocardiofacial syndrome, which include facial dysmorphism, congenital heart disease (persistent truncus arteriosus and ostium secundum-type atrial septal defect), and a seizure syndrome. Array comparative genomic hybridization revealed a non-continous deletion spanning cytobands 2q31.1-to 2q31.3, confirming a diagnosis of 2q31 microdeletion syndrome. The patient has undergone supportive therapies for swallowing and speech. Additionally, we provide a review of the literature on previous cases to give context.
CONCLUSION CONCLUSIONS
In this report, we present the first documented case of a complex, discontinuous deletion spanning in the 2q31-2q32 regions. This case contributes to our understanding of the phenotypic and mutational spectrum observed in individuals with deletions in these cytobands. It underscores the significance of employing high-resolution techniques and comprenhensive analysis in diagnosing patients with complex phenotypes. Such approaches are crucial for differentiating this condition from more common microdeletion syndromes, such as the 22q11 deletion syndrome.

Identifiants

pubmed: 39385145
doi: 10.1186/s12887-024-04843-7
pii: 10.1186/s12887-024-04843-7
doi:

Types de publication

Journal Article Case Reports Review

Langues

eng

Sous-ensembles de citation

IM

Pagination

641

Informations de copyright

© 2024. The Author(s).

Références

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Auteurs

Estephania Candelo (E)

Fundacion Valle del Lili, Cali, Colombia.
Congenital and rare disease center (CIACER), Universidad Icesi, Cali, Colombia.

Sebastian Giraldo-Ocampo (S)

Congenital and rare disease center (CIACER), Universidad Icesi, Cali, Colombia.

Julian Nevado (J)

Hospital Universitario La Paz, Madrid, Spain.

Pablo Lapunzina (P)

Hospital Universitario La Paz, Madrid, Spain.

Harry Pachajoa (H)

Congenital and rare disease center (CIACER), Universidad Icesi, Cali, Colombia. hmpachajoa@icesi.edu.co.
Genetics Division, Fundación Valle del Lili, Carrera 98 # 18-49, Cali, Colombia. hmpachajoa@icesi.edu.co.

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