Hereditary Transthyretin Amyloidosis Polyneuropathy.


Journal

Seminars in neurology
ISSN: 1098-9021
Titre abrégé: Semin Neurol
Pays: United States
ID NLM: 8111343

Informations de publication

Date de publication:
15 Oct 2024
Historique:
medline: 16 10 2024
pubmed: 16 10 2024
entrez: 15 10 2024
Statut: aheadofprint

Résumé

In the last decade, we have witnessed dramatic improvements in the diagnosis, workup, management, and monitoring of patients with hereditary transthyretin amyloidosis (ATTRv). Updated imaging techniques (e.g.,

Identifiants

pubmed: 39406377
doi: 10.1055/s-0044-1791519
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Informations de copyright

Thieme. All rights reserved.

Déclaration de conflit d'intérêts

Chafic Karam has served as consultant and/or advisory board for Acceleron: Alpine, Alexion, Alnylam, Annexon, Argenx, Astra Zeneca, Corino, Biogen, CSL Behring, Genentech, Ionis, Neuroderm, Novo Nordisk, Octapharma, Pfizer, Sanofi, UCB, Takeda, and Zai lab. He has received research funding from Argenx, Astra Zeneca, Ionis and Genzyme.

Auteurs

Taha Qarni (T)

Department of Neurology, University of Pennsylvania, Philadelphia, Pennsylvania.

Orly Moshe-Lilie (O)

Department of Neurology, Boston University, Boston, Massachusetts.

Michelle C Kaku (MC)

Department of Neurology, Icahn School of Medicine at Mount Sinai, New York, New York.

Chafic Karam (C)

Department of Neurology, University of Pennsylvania, Philadelphia, Pennsylvania.

Classifications MeSH