Efficacy of cisplatin-gemcitabine-durvalumab in patients with advanced biliary tract cancer experiencing early vs late disease relapse after surgery: a large real-life worldwide population.

advanced disease biliary tract cancer cholangiocarcinoma durvalumab immunotherapy real-world evidence surgery

Journal

The oncologist
ISSN: 1549-490X
Titre abrégé: Oncologist
Pays: England
ID NLM: 9607837

Informations de publication

Date de publication:
19 Oct 2024
Historique:
received: 16 08 2024
accepted: 23 08 2024
medline: 20 10 2024
pubmed: 20 10 2024
entrez: 19 10 2024
Statut: aheadofprint

Résumé

In the TOPAZ-1, patients with biliary tract cancers (BTC) and recurrence within 6 months after surgery were excluded, even if this event is frequently observed in clinical practice. Our study aimed to assess if the efficacy of cisplatin-gemcitabine-durvalumab (CGD) in this population is comparable to that reported in the phase 3 trial. The study cohort included patients with BTC who underwent surgery on the primary tumor, experienced disease recurrence occurring ≤6 months or >6 months after surgery or after the end of adjuvant therapy and started CGD. The primary objectives were overall survival (OS) and progression free survival (PFS). A total of 178 patients were enrolled. No significant differences were observed between early and late relapse groups in OS (23.4 months vs not reached; HR 1.26; 95% CI, 0.67-2.37; P = .45) and PFS [7.0 months vs 9.8 months; HR 1.3(95% CI, 0.9-2.1) P = .13]. Overall response rate and disease control rate (P = .33 and P = .62) were comparable between the 2 groups, as the overall safety profile. In addition, we compared survival outcomes between the selected population and a historical cohort of patients with BTC treated with cisplatin-gemcitabine (CG) and found that despite the absence of statistical significance, CGD showed an outcome trend compared with CG regardless of the time of recurrence after surgery or adjuvant chemotherapy [(CG ≤ 6 vs CGD ≤ 6 months: HR 0.59, 95%CI, 0.35-1.01, P = .05; HR 0.70; 95%CI, 0.46-1.06, P = .09, OS and PFS, respectively) and (CG > 6 vs. CGD > 6 months: HR 0.50; 95%CI, 0.29-0.88, P = 0.0165; HR 0.54; 95%CI, 0.35-0.84, P = .0068, OS and PFS, respectively)]. Our analysis suggests that CGD retains its efficacy independently of the timing of relapse after surgery or completion of adjuvant treatment in patients with advanced BTC.

Sections du résumé

BACKGROUND BACKGROUND
In the TOPAZ-1, patients with biliary tract cancers (BTC) and recurrence within 6 months after surgery were excluded, even if this event is frequently observed in clinical practice. Our study aimed to assess if the efficacy of cisplatin-gemcitabine-durvalumab (CGD) in this population is comparable to that reported in the phase 3 trial.
METHODS METHODS
The study cohort included patients with BTC who underwent surgery on the primary tumor, experienced disease recurrence occurring ≤6 months or >6 months after surgery or after the end of adjuvant therapy and started CGD. The primary objectives were overall survival (OS) and progression free survival (PFS).
RESULTS RESULTS
A total of 178 patients were enrolled. No significant differences were observed between early and late relapse groups in OS (23.4 months vs not reached; HR 1.26; 95% CI, 0.67-2.37; P = .45) and PFS [7.0 months vs 9.8 months; HR 1.3(95% CI, 0.9-2.1) P = .13]. Overall response rate and disease control rate (P = .33 and P = .62) were comparable between the 2 groups, as the overall safety profile. In addition, we compared survival outcomes between the selected population and a historical cohort of patients with BTC treated with cisplatin-gemcitabine (CG) and found that despite the absence of statistical significance, CGD showed an outcome trend compared with CG regardless of the time of recurrence after surgery or adjuvant chemotherapy [(CG ≤ 6 vs CGD ≤ 6 months: HR 0.59, 95%CI, 0.35-1.01, P = .05; HR 0.70; 95%CI, 0.46-1.06, P = .09, OS and PFS, respectively) and (CG > 6 vs. CGD > 6 months: HR 0.50; 95%CI, 0.29-0.88, P = 0.0165; HR 0.54; 95%CI, 0.35-0.84, P = .0068, OS and PFS, respectively)].
CONCLUSION CONCLUSIONS
Our analysis suggests that CGD retains its efficacy independently of the timing of relapse after surgery or completion of adjuvant treatment in patients with advanced BTC.

Identifiants

pubmed: 39427227
pii: 7828199
doi: 10.1093/oncolo/oyae256
pii:
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Informations de copyright

© The Author(s) 2024. Published by Oxford University Press.

Auteurs

Federica Lo Prinzi (F)

Operative Research Unit of Medical Oncology, Fondazione Policlinico Universitario Campus Bio-Medico, Via Alvaro del Portillo, 200 - 00128 Roma, Italy.

Francesca Salani (F)

Unit of Medical Oncology 2, Azienda Ospedaliero-Universitaria Pisana, 56126 Pisa, Italy.
Department of Translational Research and New Technologies in Medicine and Surgery, University of Pisa, 56126 Pisa, Italy.

Margherita Rimini (M)

Department of Oncology, Vita-Salute San Raffaele University, IRCCS San Raffaele Scientific Institute Hospital, 20132 Milan, Italy.

Mario Domenico Rizzato (MD)

Department of Oncology, Veneto Institute of Oncology IOV - IRCCS, 35128 Padua, Italy.

Lorenzo Antonuzzo (L)

Clinical Oncology Unit, Department of Experimental and Clinical Medicine, Careggi University Hospital, University of Florence, 50134 Florence, Italy.
Thoracic Surgery Unit, Department of Experimental and Clinical Medicine, Careggi University Hospital, University of Florence, 50134 Florence, Italy.

Silvia Camera (S)

Department of Oncology, Vita-Salute San Raffaele University, IRCCS San Raffaele Scientific Institute Hospital, 20132 Milan, Italy.

Tomoyuki Satake (T)

Department of Hepatobiliary and Pancreatic Oncology, National Cancer Center Hospital East, Kashiwa 277-8577, Japan.

Hanne Vandeputte (H)

Digestive Oncology, University Hospitals Leuven, 3000 Leuven, Belgium.

Caterina Vivaldi (C)

Unit of Medical Oncology 2, Azienda Ospedaliero-Universitaria Pisana, 56126 Pisa, Italy.
Department of Translational Research and New Technologies in Medicine and Surgery, University of Pisa, 56126 Pisa, Italy.

Tiziana Pressiani (T)

Medical Oncology and Hematology Unit, Humanitas Cancer Center, IRCCS Humanitas Research Hospital, Rozzano, 20089 Milan, Italy.

Jessica Lucchetti (J)

Operative Research Unit of Medical Oncology, Fondazione Policlinico Universitario Campus Bio-Medico, Via Alvaro del Portillo, 200 - 00128 Roma, Italy.

Jin Won Kim (JW)

Division of Hematology/Medical Oncology, Department of Internal Medicine, Seoul National University Bundang Hospital, Seoul National University College of Medicine, Gumi-ro 173 Beon-gil, Bundang-gu, Seongnam-si, Gyeonggi-do 13620, Republic of Korea.

Oluseyi Abidoye (O)

Department of Internal Medicine, Mayo Clinic, Phoenix, AZ 5777, United States.

Ilario Giovanni Rapposelli (IG)

Department of Medical Oncology, IRCCS Istituto Romagnolo per lo Studio dei Tumori (IRST) "Dino Amadori", 47014 Meldola, Italy.

Stefano Tamberi (S)

Medical Oncology, Santa Maria delle Croci hospital, Ravenna AUSL, 48121 Romagna, Italy.

Fabian Finkelmeier (F)

Medical Clinic 1, Department of Gastroenterology, University Hospital Frankfurt, 60596 Frankfurt am Main, Germany.

Guido Giordano (G)

Unit of Medical Oncology and Biomolecular Therapy, Policlinico Riuniti, 71122 Foggia, Italy.
Department of Medical and Surgical Sciences, University of Foggia, 71122 Foggia, Italy.

Chiara Pircher (C)

Department of Medical Oncology, Fondazione IRCCS Istituto Nazionale dei Tumori, 20133 Milan, Italy.

Hong Jae Chon (HJ)

Division of Medical Oncology, Department of Internal Medicine, CHA Bundang Medical Center, CHA University School of Medicine, Seongnam 59, South Korea.

Chiara Braconi (C)

University of Glasgow (School of Cancer Sciences), Beatson West of Scotland Cancer Centre, CRUK Scotland Centre, Glasgow G61 1BD, United Kingdom.

Alessandro Pastorino (A)

IRCCS Ospedale Policlinico San Martino, Medical Oncology Unit 1, 16132 Genova, Italy.

Florian Castet (F)

Gastrointestinal and Endocrine Tumor Unit, Vall d'Hebron Institute of Oncology (VHIO), Hospital Universitari Vall d'Hebron, Vall d'Hebron Barcelona Hospital Campus, 08035 Barcelona, Spain.

Emiliano Tamburini (E)

Department of Oncology and Palliative Care, Cardinale G Panico, Tricase City Hospital, 73039 Tricase, Italy.

Changhoon Yoo (C)

ASAN Medical Center, University of Ulsan College of Medicine, Seoul 138-736, Republic of Korea.

Alessandro Parisi (A)

Clinica Oncologica e Centro Regionale di Genetica Oncologica, Università Politecnica delle Marche, Azienda Ospedaliero-Universitaria delle Marche, Via Conca 71, 60126 Ancona, Italy.

Anna Diana (A)

Oncology Unit, Ospedale del Mare, 80147 Napoli, Italy.

Mario Scartozzi (M)

Medical Oncology, University and University Hospital, 09124 Cagliari, Italy.

Gerald W Prager (GW)

Department of Medicine I, Clinical Division of Oncology, Medical University of Vienna, 1090 Vienna, Austria.

Antonio Avallone (A)

Experimental Clinical Abdominal Oncology Unit, Istituto Nazionale Tumori - IRCCS - Fondazione G. Pascale, 80131 Naples, Italy.

Marta Schirripa (M)

Medical Oncology Unit, Department of Oncology and Hematology, Belcolle Hospital, 01100 Viterbo, Italy.

Il Hwan Kim (IH)

Division of Oncology, Department of Internal Medicine, Haeundae Paik Hospital, Inje University College of Medicine, Busan 875, Republic of Korea.

Lukas Perkhofer (L)

Internal Medicine 1, University Hospital Ulm, 89081 Ulm, Germany.
Institute of Molecular Oncology and Stem Cell Biology, Ulm University Hospital, 89081 Ulm, Germany.

Ester Oneda (E)

Dipartimento di Oncologia medica, Fondazione Poliambulanza, 25124 Brescia, Italy.

Monica Verrico (M)

UOC Oncologia A, Department of Hematology, Oncology and Dermatology, Policlinico Umberto I University Hospital, Sapienza University o f Rome, Viale Regina Elena, 324, 00161 Rome, Italy.

Jorge Adeva (J)

12 de Octubre University Hospital, Spanish Society of Medical Oncology (SEOM), 28041 Madrid, Spain.

Stephen L Chan (SL)

State Key Laboratory of Translational Oncology, Department of Clinical Oncology, Prince of Wales Hospital, The Chinese University of Hong Kong, Hong Kong 30, China.

Gian Paolo Spinelli (GP)

UOC Oncologia Territoriale, Polo Pontino, La Sapienza Università Di Roma, 04100 Latina, Italy.

Nicola Personeni (N)

Medical Oncology Unit, P.O. Manerbio - ASST Garda, 25025 Manerbio, Brescia, Italy.

Ingrid Garajova (I)

Medical Oncology Unit, University Hospital of Parma, 43126 Parma, Italy.

Maria Grazia Rodriquenz (MG)

Oncology Unit, Fondazione IRCCS "Casa Sollievo della Sofferenza", 71013 San Giovanni Rotondo, Italy.

Silvana Leo (S)

Division of Oncology, Vito Fazzi Hospital, 73100 Lecce, Italy.

Cecilia Melo Alvim (C)

Medical Oncology Department, Hospital de Santa Maria, Centro Hospitalar Universitário Lisboa Norte, 1649-035 Lisbon, Portugal.

Ricardo Roque (R)

Portuguese Institute of Oncology of Coimbra, 3000-075 Coimbra, Portugal.

Lorenzo Fornaro (L)

Unit of Medical Oncology 2, Azienda Ospedaliero-Universitaria Pisana, 56126 Pisa, Italy.

Antonio De Rosa (A)

Department of Oncology, Veneto Institute of Oncology IOV - IRCCS, 35128 Padua, Italy.
Department of Surgery, Oncology and Gastroenterology, University of Padua, 35121 Padua, Italy.

Daniele Lavacchi (D)

Clinical Oncology Unit, Department of Experimental and Clinical Medicine, Careggi University Hospital, University of Florence, 50134 Florence, Italy.

Federico Rossari (F)

Department of Oncology, Vita-Salute San Raffaele University, IRCCS San Raffaele Scientific Institute Hospital, 20132 Milan, Italy.

Masafumi Ikeda (M)

Department of Hepatobiliary and Pancreatic Oncology, National Cancer Center Hospital East, Kashiwa 277-8577, Japan.

Jeroen Dekervel (J)

Digestive Oncology, University Hospitals Leuven, 3000 Leuven, Belgium.

Monica Niger (M)

Department of Medical Oncology, Fondazione IRCCS Istituto Nazionale dei Tumori, 20133 Milan, Italy.

Rita Balsano (R)

Medical Oncology and Hematology Unit, Humanitas Cancer Center, IRCCS Humanitas Research Hospital, Rozzano, 20089 Milan, Italy.
Department of Biomedical Sciences, Humanitas University, 20072 Pieve Emanuele (Milan), Italy.

Giuseppe Tonini (G)

Department of Medicine and Surgery, Università Campus Bio-Medico di Roma, Via Alvaro del Portillo, 21 - 00128 Roma, Italy.

Minsu Kang (M)

Division of Hematology/Medical Oncology, Department of Internal Medicine, Seoul National University Bundang Hospital, Seoul National University College of Medicine, Gumi-ro 173 Beon-gil, Bundang-gu, Seongnam-si, Gyeonggi-do 13620, Republic of Korea.

Tanios Bekaii-Saab (T)

Department of Internal Medicine, Mayo Clinic, Phoenix, AZ 5777, United States.

Massimo Giuseppe Viola (MG)

Department of Oncology and Palliative Care, Cardinale G Panico, Tricase City Hospital, 73039 Tricase, Italy.

Lucrezia Silvestro (L)

Experimental Clinical Abdominal Oncology Unit, Istituto Nazionale Tumori - IRCCS - Fondazione G. Pascale, 80131 Naples, Italy.

Luca Esposito (L)

Department of Medical Oncology, IRCCS Istituto Romagnolo per lo Studio dei Tumori (IRST) "Dino Amadori", 47014 Meldola, Italy.

Alessandra Boccaccino (A)

Medical Oncology, Santa Maria delle Croci hospital, Ravenna AUSL, 48121 Romagna, Italy.

Vera Himmelsbach (V)

Medical Clinic 1, Department of Gastroenterology, University Hospital Frankfurt, 60596 Frankfurt am Main, Germany.

Matteo Landriscina (M)

Unit of Medical Oncology and Biomolecular Therapy, Policlinico Riuniti, 71122 Foggia, Italy.
Department of Medical and Surgical Sciences, University of Foggia, 71122 Foggia, Italy.

Selma Ahcene Djaballah (S)

Department of Oncology, Veneto Institute of Oncology IOV - IRCCS, 35128 Padua, Italy.

Valentina Zanuso (V)

Medical Oncology and Hematology Unit, Humanitas Cancer Center, IRCCS Humanitas Research Hospital, Rozzano, 20089 Milan, Italy.
Department of Biomedical Sciences, Humanitas University, 20072 Pieve Emanuele (Milan), Italy.

Gianluca Masi (G)

Unit of Medical Oncology 2, Azienda Ospedaliero-Universitaria Pisana, 56126 Pisa, Italy.
Department of Translational Research and New Technologies in Medicine and Surgery, University of Pisa, 56126 Pisa, Italy.

Sara Lonardi (S)

Department of Oncology, Veneto Institute of Oncology IOV - IRCCS, 35128 Padua, Italy.

Lorenza Rimassa (L)

Medical Oncology and Hematology Unit, Humanitas Cancer Center, IRCCS Humanitas Research Hospital, Rozzano, 20089 Milan, Italy.
Department of Biomedical Sciences, Humanitas University, 20072 Pieve Emanuele (Milan), Italy.

Andrea Casadei-Gardini (A)

Department of Oncology, Vita-Salute San Raffaele University, IRCCS San Raffaele Scientific Institute Hospital, 20132 Milan, Italy.

Classifications MeSH