Long-term lineage commitment in hematopoietic stem cell gene therapy.

Journal

Nature
ISSN: 1476-4687
Titre abrégé: Nature
Pays: England
ID NLM: 0410462

Informations de publication

Date de publication:
23 Oct 2024
Historique:
received: 16 09 2022
accepted: 18 10 2024
medline: 24 10 2024
pubmed: 24 10 2024
entrez: 23 10 2024
Statut: aheadofprint

Résumé

Hematopoietic Stem Cell (HSC) gene therapy (GT) may provide lifelong reconstitution of the hematopoietic system with gene-corrected cells

Identifiants

DOI: 10.1038/s41586-024-08250-x PMID: 39442556
pubmed: 39442556
doi: 10.1038/s41586-024-08250-x
pii: 10.1038/s41586-024-08250-x
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Informations de copyright

© 2024. The Author(s), under exclusive licence to Springer Nature Limited.

Auteurs

Andrea Calabria (A)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy. calabria.andrea@hsr.it.
ORCID: 0000-0003-3515-3384

Giulio Spinozzi (G)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.
ORCID: 0000-0002-4220-2474

Daniela Cesana (D)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.
ORCID: 0000-0001-6366-4224

Elena Buscaroli (E)

Department of Mathematics, Informatics and Geosciences, University of Trieste, Triste, Italy.

Fabrizio Benedicenti (F)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.

Giulia Pais (G)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.
ORCID: 0009-0005-5621-4803

Francesco Gazzo (F)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.
Department of Electronics, Information and Bioengineering, Politecnico di Milano, Milan, Italy.
ORCID: 0009-0000-4626-1386

Serena Scala (S)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.

Maria Rosa Lidonnici (MR)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.
ORCID: 0000-0003-3413-8414

Samantha Scaramuzza (S)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.

Alessandra Albertini (A)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.

Simona Esposito (S)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.
ORCID: 0000-0003-1594-5835

Francesca Tucci (F)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.
Pediatric Immunohematology and BMT, San Raffaele Hospital, Milan, Italy.

Daniele Canarutto (D)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.
Pediatric Immunohematology and BMT, San Raffaele Hospital, Milan, Italy.
Vita Salute San Raffaele University, Milan, Italy.

Maryam Omrani (M)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.

Fabiola De Mattia (F)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.

Francesca Dionisio (F)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.

Stefania Giannelli (S)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.

Sarah Marktel (S)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.
Pediatric Immunohematology and BMT, San Raffaele Hospital, Milan, Italy.

Francesca Fumagalli (F)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.
Pediatric Immunohematology and BMT, San Raffaele Hospital, Milan, Italy.
ORCID: 0000-0001-7476-4087

Valeria Calbi (V)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.
Pediatric Immunohematology and BMT, San Raffaele Hospital, Milan, Italy.
ORCID: 0000-0003-3514-666X

Sabina Cenciarelli (S)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.
Pediatric Immunohematology and BMT, San Raffaele Hospital, Milan, Italy.
ORCID: 0000-0002-1413-4371

Francesca Ferrua (F)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.
Pediatric Immunohematology and BMT, San Raffaele Hospital, Milan, Italy.

Bernhard Gentner (B)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.
ORCID: 0000-0001-6024-4718

Giulio Caravagna (G)

Department of Mathematics, Informatics and Geosciences, University of Trieste, Triste, Italy.
ORCID: 0000-0003-4240-3265

Fabio Ciceri (F)

Pediatric Immunohematology and BMT, San Raffaele Hospital, Milan, Italy.
ORCID: 0000-0003-0873-0123

Luigi Naldini (L)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.
Vita Salute San Raffaele University, Milan, Italy.
ORCID: 0000-0002-7835-527X

Giuliana Ferrari (G)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.
Vita Salute San Raffaele University, Milan, Italy.

Alessandro Aiuti (A)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.
Pediatric Immunohematology and BMT, San Raffaele Hospital, Milan, Italy.
Vita Salute San Raffaele University, Milan, Italy.
ORCID: 0000-0002-5398-1717

Eugenio Montini (E)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy. montini.eugenio@hsr.it.
ORCID: 0000-0003-1771-6067

Classifications MeSH