CCL3 predicts exceptional response to TGFβ inhibition in basal-like pancreatic cancer enriched in LIF-producing macrophages.


Journal

NPJ precision oncology
ISSN: 2397-768X
Titre abrégé: NPJ Precis Oncol
Pays: England
ID NLM: 101708166

Informations de publication

Date de publication:
30 Oct 2024
Historique:
received: 24 04 2024
accepted: 21 10 2024
medline: 31 10 2024
pubmed: 31 10 2024
entrez: 31 10 2024
Statut: epublish

Résumé

The TGFβ receptor inhibitor galunisertib showed promising efficacy in patients with pancreatic ductal adenocarcinoma (PDAC) in the phase 2 H9H-MC-JBAJ study. Identifying biomarkers for this treatment remains essential. Baseline plasma levels of chemokine CCL3 were integrated with clinical outcomes in PDAC patients treated with galunisertib plus gemcitabine (n = 104) or placebo plus gemcitabine (n = 52). High CCL3 was a poor prognostic factor in the placebo group (mOS 3.6 vs. 10.1 months; p < 0.01) but a positive predictor for galunisertib (mOS 9.2 vs. 3.6 months; p < 0.01). Mechanistically, tumor-derived CCL3 activates Tgfβ signaling in macrophages, inducing their M2 phenotype and Lif secretion, sustaining a mesenchymal/basal-like ecotype. TGFβ inhibition redirects macrophage polarization to M1, reducing Lif and shifting PDAC cells to a more epithelial/classical phenotype, improving gemcitabine sensitivity. This study supports exploring TGFβ-targeting agents in PDAC with a mesenchymal/basal-like ecotype driven by high CCL3 levels.

Identifiants

pubmed: 39478186
doi: 10.1038/s41698-024-00742-3
pii: 10.1038/s41698-024-00742-3
doi:

Types de publication

Journal Article

Langues

eng

Pagination

246

Subventions

Organisme : Associazione Italiana per la Ricerca sul Cancro (Italian Association for Cancer Research)
ID : 23719

Informations de copyright

© 2024. The Author(s).

Références

The Global Cancer Observatory. Pancreas, https://gco.iarc.fr/today/data/factsheets/cancers/13-Pancreas-fact-sheet.pdf (2020).
Siegel, R. L., Giaquinto, A. N. & Jemal, A. Cancer statistics, 2024. CA Cancer J. Clin. 74, 12–49 (2024).
doi: 10.3322/caac.21820 pubmed: 38230766
Rahib, L., Wehner, M. R., Matrisian, L. M. & Nead, K. T. Estimated projection of US cancer incidence and death to 2040. JAMA Netw. Open 4, e214708 (2021).
doi: 10.1001/jamanetworkopen.2021.4708 pubmed: 33825840 pmcid: 8027914
Tamburrino, A., Piro, G., Carbone, C., Tortora, G. & Melisi, D. Mechanisms of resistance to chemotherapeutic and anti-angiogenic drugs as novel targets for pancreatic cancer therapy. Front. Pharm. 4, 56 (2013).
doi: 10.3389/fphar.2013.00056
Collisson, E. A. et al. Subtypes of pancreatic ductal adenocarcinoma and their differing responses to therapy. Nat. Med. 17, 500–503 (2011).
doi: 10.1038/nm.2344 pubmed: 21460848 pmcid: 3755490
Moffitt, R. A. et al. Virtual microdissection identifies distinct tumor- and stroma-specific subtypes of pancreatic ductal adenocarcinoma. Nat. Genet. 47, 1168–1178 (2015).
doi: 10.1038/ng.3398 pubmed: 26343385 pmcid: 4912058
Bailey, P. et al. Genomic analyses identify molecular subtypes of pancreatic cancer. Nature 531, 47–52 (2016).
doi: 10.1038/nature16965 pubmed: 26909576
Zhou, X. et al. Clinical impact of molecular subtyping of pancreatic cancer. Front. Cell Dev. Biol. 9, 743908 (2021).
doi: 10.3389/fcell.2021.743908 pubmed: 34805152 pmcid: 8603393
Grunwald, B. T. et al. Spatially confined sub-tumor microenvironments in pancreatic cancer. Cell 184, 5577–5592.e5518 (2021).
doi: 10.1016/j.cell.2021.09.022 pubmed: 34644529
Gaianigo, N., Melisi, D. & Carbone, C. EMT and treatment resistance in pancreatic cancer. Cancers 9, https://doi.org/10.3390/cancers9090122 (2017).
Melisi, D. et al. Modulation of pancreatic cancer chemoresistance by inhibition of TAK1. J. Natl Cancer Inst. 103, 1190–1204 (2011).
doi: 10.1093/jnci/djr243 pubmed: 21743023 pmcid: 3149044
Melisi, D. et al. LY2109761, a novel transforming growth factor beta receptor type I and type II dual inhibitor, as a therapeutic approach to suppressing pancreatic cancer metastasis. Mol. Cancer Ther. 7, 829–840 (2008).
doi: 10.1158/1535-7163.MCT-07-0337 pubmed: 18413796 pmcid: 3088432
Melisi, D. et al. Galunisertib plus gemcitabine vs. gemcitabine for first-line treatment of patients with unresectable pancreatic cancer. Br. J. Cancer 119, 1208–1214 (2018).
doi: 10.1038/s41416-018-0246-z pubmed: 30318515 pmcid: 6251034
Melisi, D. et al. TGFbeta receptor inhibitor galunisertib is linked to inflammation- and remodeling-related proteins in patients with pancreatic cancer. Cancer Chemother. Pharmacol. 83, 975–991 (2019).
doi: 10.1007/s00280-019-03807-4 pubmed: 30887178
Gueorguieva, I. et al. Population pharmacokinetics and exposure-overall survival analysis of the transforming growth factor-beta inhibitor galunisertib in patients with pancreatic cancer. Cancer Chemother. Pharmacol. https://doi.org/10.1007/s00280-019-03931-1 (2019).
Yap, T. A. et al. First-in-human phase I study of a next-generation, oral, TGFbeta Receptor 1 inhibitor, LY3200882, in patients with advanced cancer. Clin. Cancer Res. https://doi.org/10.1158/1078-0432.CCR-21-1504 (2021).
Melisi, D. et al. Safety and activity of the TGFbeta receptor I kinase inhibitor galunisertib plus the anti-PD-L1 antibody durvalumab in metastatic pancreatic cancer. J Immunother. Cancer 9, https://doi.org/10.1136/jitc-2020-002068 (2021).
Mantovani, A., Marchesi, F., Malesci, A., Laghi, L. & Allavena, P. Tumour-associated macrophages as treatment targets in oncology. Nat. Rev. Clin. Oncol. 14, 399–416 (2017).
doi: 10.1038/nrclinonc.2016.217 pubmed: 28117416 pmcid: 5480600
Vayrynen, S. A. et al. Composition, spatial characteristics, and prognostic significance of myeloid cell infiltration in pancreatic cancer. Clin. Cancer Res. 27, 1069–1081 (2021).
doi: 10.1158/1078-0432.CCR-20-3141 pubmed: 33262135
Zucchetto, A. et al. Monocytes/macrophages but not T lymphocytes are the major targets of the CCL3/CCL4 chemokines produced by CD38(+)CD49d(+) chronic lymphocytic leukaemia cells. Br. J. Haematol. 150, 111–113 (2010).
doi: 10.1111/j.1365-2141.2010.08152.x pubmed: 20346010
Menten, P., Wuyts, A. & Van Damme, J. Macrophage inflammatory protein-1. Cytokine Growth Factor Rev. 13, 455–481 (2002).
doi: 10.1016/S1359-6101(02)00045-X pubmed: 12401480
Qin, R. et al. Role of chemokines in the crosstalk between tumor and tumor-associated macrophages. Clin. Exp. Med. https://doi.org/10.1007/s10238-022-00888-z (2022).
Carbone, C. et al. Homeobox B9 mediates resistance to anti-VEGF therapy in colorectal cancer patients. Clin. Cancer Res. 23, 4312–4322 (2017).
doi: 10.1158/1078-0432.CCR-16-3153 pubmed: 28298545
Wang, C. et al. Targeting a positive regulatory loop in the tumor-macrophage interaction impairs the progression of clear cell renal cell carcinoma. Cell Death Differ. 28, 932–951 (2021).
doi: 10.1038/s41418-020-00626-6 pubmed: 33009518
Melisi, D. et al. Secreted interleukin-1alpha induces a metastatic phenotype in pancreatic cancer by sustaining a constitutive activation of nuclear factor-kappaB. Mol. Cancer Res. 7, 624–633 (2009).
doi: 10.1158/1541-7786.MCR-08-0201 pubmed: 19435817 pmcid: 2856954
Shi, Y. et al. Targeting LIF-mediated paracrine interaction for pancreatic cancer therapy and monitoring. Nature 569, 131–135 (2019).
doi: 10.1038/s41586-019-1130-6 pubmed: 30996350 pmcid: 6565370
Pittet, M. J., Michielin, O. & Migliorini, D. Clinical relevance of tumour-associated macrophages. Nat. Rev. Clin. Oncol. 19, 402–421 (2022).
doi: 10.1038/s41571-022-00620-6 pubmed: 35354979
Storrs, E. P. et al. High-dimensional deconstruction of pancreatic cancer identifies tumor microenvironmental and developmental stemness features that predict survival. NPJ Precis Oncol. 7, 105 (2023).
doi: 10.1038/s41698-023-00455-z pubmed: 37857854 pmcid: 10587349
Batlle, E. & Massague, J. Transforming growth factor-beta signaling in immunity and cancer. Immunity 50, 924–940 (2019).
doi: 10.1016/j.immuni.2019.03.024 pubmed: 30995507 pmcid: 7507121
Sabbadini, F. et al. The multifaceted role of TGF-beta in gastrointestinal tumors. Cancers 13, https://doi.org/10.3390/cancers13163960 (2021).
Hou, P. et al. Tumor microenvironment remodeling enables bypass of oncogenic KRAS dependency in pancreatic cancer. Cancer Discov. 10, 1058–1077 (2020).
doi: 10.1158/2159-8290.CD-19-0597 pubmed: 32341020 pmcid: 7334087
Viswanadhapalli, S., Dileep, K. V., Zhang, K. Y. J., Nair, H. B. & Vadlamudi, R. K. Targeting LIF/LIFR signaling in cancer. Genes Dis. 9, 973–980 (2022).
doi: 10.1016/j.gendis.2021.04.003 pubmed: 35685476
Pascual-Garcia, M. et al. LIF regulates CXCL9 in tumor-associated macrophages and prevents CD8(+) T cell tumor-infiltration impairing anti-PD1 therapy. Nat. Commun. 10, 2416 (2019).
doi: 10.1038/s41467-019-10369-9 pubmed: 31186412 pmcid: 6559950
Hallett, R. M. et al. Therapeutic targeting of LIF overcomes macrophage-mediated immunosuppression of the local tumor microenvironment. Clin. Cancer Res. 29, 791–804 (2023).
doi: 10.1158/1078-0432.CCR-21-1888 pubmed: 36441800
Penuelas, S. et al. TGF-beta increases glioma-initiating cell self-renewal through the induction of LIF in human glioblastoma. Cancer Cell 15, 315–327 (2009).
doi: 10.1016/j.ccr.2009.02.011 pubmed: 19345330
Halama, N. et al. Tumoral immune cell exploitation in colorectal cancer metastases can be targeted effectively by anti-CCR5 therapy in cancer patients. Cancer Cell 29, 587–601 (2016).
doi: 10.1016/j.ccell.2016.03.005 pubmed: 27070705
Haag, G. M. et al. Pembrolizumab and maraviroc in refractory mismatch repair proficient/microsatellite-stable metastatic colorectal cancer - the PICCASSO phase I trial. Eur. J. Cancer 167, 112–122 (2022).
doi: 10.1016/j.ejca.2022.03.017 pubmed: 35427833
Borazanci, E. et al. Phase I, first-in-human study of MSC-1 (AZD0171), a humanized anti-leukemia inhibitory factor monoclonal antibody, for advanced solid tumors. ESMO Open 7, 100530 (2022).
doi: 10.1016/j.esmoop.2022.100530 pubmed: 35921760 pmcid: 9434412
Pietrobono, S. et al. Autotaxin secretion is a stromal mechanism of adaptive resistance to TGFbeta inhibition in pancreatic ductal adenocarcinoma. Cancer Res. https://doi.org/10.1158/0008-5472.CAN-23-0104 (2023).
Gameiro, S. R., Strauss, J., Gulley, J. L. & Schlom, J. Preclinical and clinical studies of bintrafusp alfa, a novel bifunctional anti-PD-L1/TGFbetaRII agent: current status. Exp. Biol. Med. 247, 1124–1134 (2022).
doi: 10.1177/15353702221089910
Greco, R. et al. Pan-TGFbeta inhibition by SAR439459 relieves immunosuppression and improves antitumor efficacy of PD-1 blockade. Oncoimmunology 9, 1811605 (2020).
doi: 10.1080/2162402X.2020.1811605 pubmed: 33224628 pmcid: 7657645
Bauer, T. M. et al. Phase I/Ib, open-label, multicenter, dose-escalation study of the anti-TGF-beta monoclonal antibody, NIS793, in combination with spartalizumab in adult patients with advanced tumors. J. Immunother. Cancer 11, https://doi.org/10.1136/jitc-2023-007353 (2023).

Auteurs

Silvia Pietrobono (S)

Department of Medicine, Digestive Molecular Clinical Oncology Research Unit, University of Verona, Verona, Italy.

Monica Bertolini (M)

Department of Medicine, Digestive Molecular Clinical Oncology Research Unit, University of Verona, Verona, Italy.

Veronica De Vita (V)

Department of Medicine, Digestive Molecular Clinical Oncology Research Unit, University of Verona, Verona, Italy.

Fabio Sabbadini (F)

Department of Medicine, Digestive Molecular Clinical Oncology Research Unit, University of Verona, Verona, Italy.

Federica Fazzini (F)

Investigational Cancer Therapeutics Clinical Unit, Azienda Ospedaliera Universitaria Integrata, Verona, Italy.

Cristina Frusteri (C)

Department of Engineering for Innovation Medicine, University of Verona, Verona, Italy.

Enza Scarlato (E)

Department of Medicine, Digestive Molecular Clinical Oncology Research Unit, University of Verona, Verona, Italy.

Domenico Mangiameli (D)

Department of Medicine, Digestive Molecular Clinical Oncology Research Unit, University of Verona, Verona, Italy.

Alberto Quinzii (A)

Department of Medicine, Digestive Molecular Clinical Oncology Research Unit, University of Verona, Verona, Italy.

Simona Casalino (S)

Department of Medicine, Digestive Molecular Clinical Oncology Research Unit, University of Verona, Verona, Italy.

Camilla Zecchetto (C)

Department of Medicine, Digestive Molecular Clinical Oncology Research Unit, University of Verona, Verona, Italy.

Valeria Merz (V)

Department of Medicine, Digestive Molecular Clinical Oncology Research Unit, University of Verona, Verona, Italy.

Davide Melisi (D)

Department of Medicine, Digestive Molecular Clinical Oncology Research Unit, University of Verona, Verona, Italy. davide.melisi@univr.it.
Investigational Cancer Therapeutics Clinical Unit, Azienda Ospedaliera Universitaria Integrata, Verona, Italy. davide.melisi@univr.it.

Classifications MeSH