D Pangonis

Affiliations

National Tay-Sachs and Allied Disease Foundation, 2001 Beacon Street, Suite 204, Boston, MA, 02135, USA.

Publications (2)

A master protocol to investigate a novel therapy acetyl-L-leucine for three ultra-rare neurodegenerative diseases: Niemann-Pick type C, the GM2 gangliosidoses, and ataxia telangiectasia.

Trials

Avec: T Fields , M Patterson , T Bremova-Ertl , G Belcher , I Billington , G C Churchill , W Davis , W Evans , S Flint , A Galione , U Granzer , J Greenfield , R Karl , R Kay , D Lewi , T Mathieson , T Meyer , D Pangonis , F M Platt , L Tsang , C Verburg , M Factor , M Strupp

GM1-gangliosidosis: The caregivers' assessments of symptom impact and most important symptoms to treat.

American journal of medical genetics. Part A

Avec: Amanda Bingaman , Christine Waggoner , Sara M Andrews , Diana Pangonis , Marie Trad , Roberto Giugliani , Ruben Giorgino , Jeanine Jarnes , Rojan Vakili , Victoria Ballard , Holly L Peay

Réseau de co-auteurs

T Fields 1 collaboration

M Patterson 1 collaboration

T Bremova-Ertl 1 collaboration

G Belcher 1 collaboration

I Billington 1 collaboration

G C Churchill 1 collaboration

W Davis 1 collaboration

W Evans 1 collaboration

S Flint 1 collaboration

A Galione 1 collaboration

U Granzer 1 collaboration

J Greenfield 1 collaboration

R Karl 1 collaboration

R Kay 1 collaboration

D Lewi 1 collaboration

T Mathieson 1 collaboration

T Meyer 1 collaboration

F M Platt 1 collaboration

L Tsang 1 collaboration

C Verburg 1 collaboration

M Factor 1 collaboration

M Strupp 1 collaboration

Amanda Bingaman 1 collaboration

Christine Waggoner 1 collaboration

Sara M Andrews 1 collaboration

Diana Pangonis 1 collaboration

Marie Trad 1 collaboration

Roberto Giugliani 1 collaboration

Ruben Giorgino 1 collaboration

Jeanine Jarnes 1 collaboration

Rojan Vakili 1 collaboration

Victoria Ballard 1 collaboration

Holly L Peay 1 collaboration