A New Genetic Risk Score to Predict the Outcome of Locally Advanced or Metastatic Breast Cancer Patients Treated With First-Line Exemestane: Results From a Prospective Study.


Journal

Clinical breast cancer
ISSN: 1938-0666
Titre abrégé: Clin Breast Cancer
Pays: United States
ID NLM: 100898731

Informations de publication

Date de publication:
04 2019
Historique:
received: 01 10 2018
accepted: 18 11 2018
pubmed: 26 12 2018
medline: 15 4 2020
entrez: 26 12 2018
Statut: ppublish

Résumé

Approximately 50% of locally advanced or metastatic breast cancer (MBC) patients treated with first-line exemestane do not show objective response and currently there are no reliable biomarkers to predict the outcome of patients using this therapy. The constitutive genetic background might be responsible for differences in the outcome of exemestane-treated patients. We designed a prospective study to investigate the role of germ line polymorphisms as biomarkers of survival. Three hundred two locally advanced or MBC patients treated with first-line exemestane were genotyped for 74 germ line polymorphisms in 39 candidate genes involved in drug activity, hormone balance, DNA replication and repair, and cell signaling pathways. Associations with progression-free survival (PFS) and overall survival (OS) were tested with multivariate Cox regression. Bootstrap resampling was used as an internal assessment of results reproducibility. Cytochrome P450 19A1-rs10046TC/CC, solute carrier organic anion transporter 1B1-rs4149056TT, adenosine triphosphate binding cassette subfamily G member 2-rs2046134GG, fibroblast growth factor receptor-4-rs351855TT, and X-ray repair cross complementing 3-rs861539TT were significantly associated with PFS and then combined into a risk score (0-1, 2, 3, or 4-6 risk points). Patients with the highest risk score (4-6 risk points) compared with ones with the lowest score (0-1 risk points) had a median PFS of 10 months versus 26.3 months (adjusted hazard ratio [AdjHR], 3.12 [95% confidence interval (CI), 2.18-4.48]; P < .001) and a median OS of 38.9 months versus 63.0 months (AdjHR, 2.41 [95% CI, 1.22-4.79], P = .012), respectively. In this study we defined a score including 5 polymorphisms to stratify patients for PFS and OS. This score, if validated, might be translated to personalize locally advanced or MBC patient treatment and management.

Identifiants

pubmed: 30584056
pii: S1526-8209(18)30679-7
doi: 10.1016/j.clbc.2018.11.009
pii:
doi:

Substances chimiques

Androstadienes 0
Antineoplastic Agents, Hormonal 0
Aromatase Inhibitors 0
Biomarkers, Tumor 0
Receptors, Estrogen 0
exemestane NY22HMQ4BX

Types de publication

Journal Article Multicenter Study Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

137-145.e4

Informations de copyright

Copyright © 2018 The Authors. Published by Elsevier Inc. All rights reserved.

Auteurs

Sara Gagno (S)

Experimental and Clinical Pharmacology Unit, Centro di Riferimento Oncologico di Aviano, IRCCS, Aviano, Italy.

Mario Rosario D'Andrea (MR)

Department of Oncology, San Filippo Neri Hospital, Rome, Italy.

Mauro Mansutti (M)

Department of Oncology, University Hospital of Udine, Udine, Italy.

Chiara Zanusso (C)

Experimental and Clinical Pharmacology Unit, Centro di Riferimento Oncologico di Aviano, IRCCS, Aviano, Italy.

Fabio Puglisi (F)

Medical Oncology and Cancer Prevention Unit, Centro di Riferimento Oncologico di Aviano, IRCCS, Aviano, Italy; Medical Oncology, Department of Medicine, University of Udine, Udine, Italy.

Eva Dreussi (E)

Experimental and Clinical Pharmacology Unit, Centro di Riferimento Oncologico di Aviano, IRCCS, Aviano, Italy.

Marcella Montico (M)

Scientific Directorate, Centro di Riferimento Oncologico di Aviano, IRCCS, Aviano, Italy.

Paola Biason (P)

Experimental and Clinical Pharmacology Unit, Centro di Riferimento Oncologico di Aviano, IRCCS, Aviano, Italy; Medical Oncology Unit 1, Istituto Oncologico Veneto IOV IRCCS, Padova, Italy.

Erika Cecchin (E)

Experimental and Clinical Pharmacology Unit, Centro di Riferimento Oncologico di Aviano, IRCCS, Aviano, Italy.

Donatella Iacono (D)

Department of Oncology, University Hospital of Udine, Udine, Italy.

Stefania Russo (S)

Department of Oncology, University Hospital of Udine, Udine, Italy.

Marika Cinausero (M)

Department of Oncology, University Hospital of Udine, Udine, Italy.

Silvana Saracchini (S)

Medical Oncology Unit, Santa Maria degli Angeli Hospital, Pordenone, Italy.

Giampietro Gasparini (G)

Department of Oncology, San Filippo Neri Hospital, Rome, Italy.

Donata Sartori (D)

Medical Oncology Department, General Hospital, Mirano, Italy.

Mario Bari (M)

Medical Oncology Department, General Hospital, Mirano, Italy.

Elena Collovà (E)

Oncology Operative Unit, ASST Ovest Milanese, Ospedale di Legnano, Legnano, Italy.

Rosa Meo (R)

Medical Oncology Unit, Presidio Ospedaliero Sant'Alfonso Maria dei Liguori, Cerreto Sannita, Italy.

Ghassan Merkabaoui (G)

Medical Oncology Unit, Azienda Ospedaliera Universitaria Federico II di Napoli, Napoli, Italy.

Ilaria Spagnoletti (I)

Medical Oncology Unit, Ospedale Sacro Cuore di Gesù, Fatebenefratelli, Benevento, Italy.

Arianna Pellegrino (A)

Medical Oncology Unit, Ospedale San Pietro Fatebenefratelli, Rome, Italy.

Lorenzo Gianni (L)

Department of Oncology, Infermi Hospital, Rimini, Italy.

Paolo Sandri (P)

Medical Oncology Unit, San Vito al Tagliamento Hospital, Pordenone, Italy.

Elisabetta Cretella (E)

Medical Oncology, Azienda Sanitaria dell'Alto Adige, Bolzano, Italy.

Emanuela Vattemi (E)

Medical Oncology, Azienda Sanitaria dell'Alto Adige, Bolzano, Italy.

Andrea Rocca (A)

Department of Medical Oncology, Istituto Scientifico Romagnolo per lo Studio e la Cura dei Tumori (IRST), IRCCS, Meldola, Italy.

Patrizia Serra (P)

Department of Medical Oncology, Istituto Scientifico Romagnolo per lo Studio e la Cura dei Tumori (IRST), IRCCS, Meldola, Italy.

Maria Agnese Fabbri (MA)

Division of Oncology, Complesso Ospedaliero Belcolle, AUSL Viterbo, Viterbo, Italy.

Giovanni Benedetti (G)

Oncology Unit, Civitanova Marche Hospital, Macerata, Italy.

Laura Foghini (L)

Oncology Unit, Macerata Hospital, Macerata, Italy.

Michele Medici (M)

Department of Medical Oncology, Azienda ULSS 3 Serenissima, Mestre, Italy.

Umberto Basso (U)

Medical Oncology Unit 1, Istituto Oncologico Veneto IOV IRCCS, Padova, Italy.

Vito Amoroso (V)

Medical Oncology Unit, Spedali Civili Hospital, Brescia, Italy.

Ferdinando Riccardi (F)

Medical Oncology Unit, Ospedale Cardarelli, Napoli, Italy.

Anna Maria Baldelli (AM)

Medical Oncology Unit, Azienda Ospedaliera Ospedali Riuniti Marche Nord, San Salvatore Hospital, Pesaro, Italy.

Mario Clerico (M)

Department of Oncology, Ospedale degli Infermi, Biella, Italy.

Salvatore Bonura (S)

Department of Oncology, Latisana Hospital, Latisana, Italy.

Chiara Saggia (C)

Azienda Ospedaliero-Universitaria Maggiore della Carità, Novara, Italy.

Federico Innocenti (F)

University of North Carolina, Chapel Hill, NC.

Giuseppe Toffoli (G)

Experimental and Clinical Pharmacology Unit, Centro di Riferimento Oncologico di Aviano, IRCCS, Aviano, Italy. Electronic address: gtoffoli@cro.it.

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Classifications MeSH