Successful donor engraftment and repair of the blood-brain barrier in cerebral adrenoleukodystrophy.
ATP Binding Cassette Transporter, Subfamily D, Member 1
/ genetics
Adolescent
Adrenoleukodystrophy
/ genetics
Adult
Biological Transport
Blood-Brain Barrier
/ physiology
Child
Child, Preschool
Disease Progression
Follow-Up Studies
Gadolinium
/ metabolism
Graft Rejection
/ prevention & control
Graft Survival
Hematopoietic Stem Cell Transplantation
Humans
Male
Middle Aged
Mutation
Prognosis
Tissue Donors
Young Adult
Journal
Blood
ISSN: 1528-0020
Titre abrégé: Blood
Pays: United States
ID NLM: 7603509
Informations de publication
Date de publication:
21 03 2019
21 03 2019
Historique:
received:
26
11
2018
accepted:
06
01
2019
pubmed:
13
1
2019
medline:
9
11
2019
entrez:
13
1
2019
Statut:
ppublish
Résumé
Adrenoleukodystrophy (ALD) is caused by mutations within the X-linked
Identifiants
pubmed: 30635285
pii: S0006-4971(20)42693-X
doi: 10.1182/blood-2018-11-887240
pmc: PMC6440119
doi:
Substances chimiques
ABCD1 protein, human
0
ATP Binding Cassette Transporter, Subfamily D, Member 1
0
Gadolinium
AU0V1LM3JT
Types de publication
Journal Article
Langues
eng
Sous-ensembles de citation
IM
Pagination
1378-1381Subventions
Organisme : NCI NIH HHS
ID : P30 CA077598
Pays : United States
Commentaires et corrections
Type : CommentIn
Informations de copyright
© 2019 by The American Society of Hematology.
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