Mineralocorticoid receptor antagonism limits experimental choroidal neovascularization and structural changes associated with neovascular age-related macular degeneration.


Journal

Nature communications
ISSN: 2041-1723
Titre abrégé: Nat Commun
Pays: England
ID NLM: 101528555

Informations de publication

Date de publication:
21 01 2019
Historique:
received: 30 03 2018
accepted: 11 12 2018
entrez: 22 1 2019
pubmed: 22 1 2019
medline: 6 2 2019
Statut: epublish

Résumé

Choroidal neovascularization (CNV) is a major cause of visual impairment in patients suffering from wet age-related macular degeneration (AMD), particularly when refractory to intraocular anti-VEGF injections. Here we report that treatment with the oral mineralocorticoid receptor (MR) antagonist spironolactone reduces signs of CNV in patients refractory to anti-VEGF treatment. In animal models of wet AMD, pharmacological inhibition of the MR pathway or endothelial-specific deletion of MR inhibits CNV through VEGF-independent mechanisms, in part through upregulation of the extracellular matrix protein decorin. Intravitreal injections of spironolactone-loaded microspheres and systemic delivery lead to similar reductions in CNV. Together, our work suggests MR inhibition as a novel therapeutic option for wet AMD patients unresponsive to anti-VEGF drugs.

Identifiants

pubmed: 30664640
doi: 10.1038/s41467-018-08125-6
pii: 10.1038/s41467-018-08125-6
pmc: PMC6341116
doi:

Substances chimiques

Angiogenesis Inhibitors 0
Mineralocorticoid Receptor Antagonists 0
Receptors, Mineralocorticoid 0
Recombinant Fusion Proteins 0
VEGFA protein, human 0
Vascular Endothelial Growth Factor A 0
aflibercept 15C2VL427D
Spironolactone 27O7W4T232
Receptors, Vascular Endothelial Growth Factor EC 2.7.10.1
Ranibizumab ZL1R02VT79

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

369

Subventions

Organisme : NCCIH NIH HHS
ID : F05 AT002013
Pays : United States

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Auteurs

Min Zhao (M)

Inserm UMR_S 1138, Team 17, Centre de Recherche des Cordeliers, 75006, Paris, France.
Sorbonne University, University of Pierre et Marie Curie, UMR_S 1138, Centre de Recherche des Cordeliers, 75006, Paris, France.
Paris Descartes University, Sorbonne Paris Cité, UMR_S 1138, Centre de Recherche des Cordeliers, 75006, Paris, France.

Irmela Mantel (I)

Department of Ophthalmology, University of Lausanne, Jules Gonin Eye Hospital, Fondation Asile des Aveugles, 1004, Lausanne, Switzerland.

Emmanuelle Gelize (E)

Inserm UMR_S 1138, Team 17, Centre de Recherche des Cordeliers, 75006, Paris, France.
Sorbonne University, University of Pierre et Marie Curie, UMR_S 1138, Centre de Recherche des Cordeliers, 75006, Paris, France.
Paris Descartes University, Sorbonne Paris Cité, UMR_S 1138, Centre de Recherche des Cordeliers, 75006, Paris, France.

Xinxin Li (X)

Inserm UMR_S 1138, Team 17, Centre de Recherche des Cordeliers, 75006, Paris, France.
Sorbonne University, University of Pierre et Marie Curie, UMR_S 1138, Centre de Recherche des Cordeliers, 75006, Paris, France.
Paris Descartes University, Sorbonne Paris Cité, UMR_S 1138, Centre de Recherche des Cordeliers, 75006, Paris, France.

Xiaoyue Xie (X)

Inserm UMR_S 1138, Team 17, Centre de Recherche des Cordeliers, 75006, Paris, France.
Sorbonne University, University of Pierre et Marie Curie, UMR_S 1138, Centre de Recherche des Cordeliers, 75006, Paris, France.
Paris Descartes University, Sorbonne Paris Cité, UMR_S 1138, Centre de Recherche des Cordeliers, 75006, Paris, France.

Alejandro Arboleda (A)

Inserm UMR_S 1138, Team 17, Centre de Recherche des Cordeliers, 75006, Paris, France.
Sorbonne University, University of Pierre et Marie Curie, UMR_S 1138, Centre de Recherche des Cordeliers, 75006, Paris, France.
Paris Descartes University, Sorbonne Paris Cité, UMR_S 1138, Centre de Recherche des Cordeliers, 75006, Paris, France.
Ophthalmic Biophysics Center, Department of Ophthalmology, Bascom Palmer Eye Institute, University of Miami Miller School of Medicine, Miami, FL, 33136, USA.

Marie Seminel (M)

Inserm UMR_S 1138, Team 17, Centre de Recherche des Cordeliers, 75006, Paris, France.
Sorbonne University, University of Pierre et Marie Curie, UMR_S 1138, Centre de Recherche des Cordeliers, 75006, Paris, France.
Paris Descartes University, Sorbonne Paris Cité, UMR_S 1138, Centre de Recherche des Cordeliers, 75006, Paris, France.

Rinath Levy-Boukris (R)

Inserm UMR_S 1138, Team 17, Centre de Recherche des Cordeliers, 75006, Paris, France.
Sorbonne University, University of Pierre et Marie Curie, UMR_S 1138, Centre de Recherche des Cordeliers, 75006, Paris, France.
Paris Descartes University, Sorbonne Paris Cité, UMR_S 1138, Centre de Recherche des Cordeliers, 75006, Paris, France.

Marilyn Dernigoghossian (M)

Inserm UMR_S 1138, Team 17, Centre de Recherche des Cordeliers, 75006, Paris, France.
Sorbonne University, University of Pierre et Marie Curie, UMR_S 1138, Centre de Recherche des Cordeliers, 75006, Paris, France.
Paris Descartes University, Sorbonne Paris Cité, UMR_S 1138, Centre de Recherche des Cordeliers, 75006, Paris, France.

Andrea Prunotto (A)

Department of Computational Biology, Unit of Medical Genetics, University of Lausanne, 1011, Lausanne, Switzerland.

Charlotte Andrieu-Soler (C)

IGMM, CNRS, Univ. Montpellier, 34293, Montpellier Cedex 5, France.

Carlo Rivolta (C)

Department of Computational Biology, Unit of Medical Genetics, University of Lausanne, 1011, Lausanne, Switzerland.
Department of Genetics and Genome Biology, University of Leicester, Leicester, LE1 7RH, UK.

Jérémie Canonica (J)

Department of Ophthalmology, University of Lausanne, Jules Gonin Eye Hospital, Fondation Asile des Aveugles, 1004, Lausanne, Switzerland.

Marie-Christine Naud (MC)

Inserm UMR_S 1138, Team 17, Centre de Recherche des Cordeliers, 75006, Paris, France.
Sorbonne University, University of Pierre et Marie Curie, UMR_S 1138, Centre de Recherche des Cordeliers, 75006, Paris, France.
Paris Descartes University, Sorbonne Paris Cité, UMR_S 1138, Centre de Recherche des Cordeliers, 75006, Paris, France.

Sebastian Lechner (S)

Sorbonne University, University of Pierre et Marie Curie, UMR_S 1138, Centre de Recherche des Cordeliers, 75006, Paris, France.
Paris Descartes University, Sorbonne Paris Cité, UMR_S 1138, Centre de Recherche des Cordeliers, 75006, Paris, France.
Inserm UMR_S 1138, Team 1, Centre de Recherche des Cordeliers, 75006, Paris, France.

Nicolette Farman (N)

Sorbonne University, University of Pierre et Marie Curie, UMR_S 1138, Centre de Recherche des Cordeliers, 75006, Paris, France.
Paris Descartes University, Sorbonne Paris Cité, UMR_S 1138, Centre de Recherche des Cordeliers, 75006, Paris, France.
Inserm UMR_S 1138, Team 1, Centre de Recherche des Cordeliers, 75006, Paris, France.

Irene Bravo-Osuna (I)

Department of Pharmacy and Pharmaceutical Technology, Universidad Complutense de Madrid, 28040, Madrid, Spain.
Instituto Universitario de Farmacia Industrial, Faculty of Pharmacy, Universidad Complutense de Madrid, 28040, Madrid, Spain.
Fundación para la Investigación-HCSC, Instituto de Investigación Sanitaria San Carlos (IdISSC), 28040, Madrid, Spain.

Rocio Herrero-Vanrell (R)

Department of Pharmacy and Pharmaceutical Technology, Universidad Complutense de Madrid, 28040, Madrid, Spain.
Instituto Universitario de Farmacia Industrial, Faculty of Pharmacy, Universidad Complutense de Madrid, 28040, Madrid, Spain.
Fundación para la Investigación-HCSC, Instituto de Investigación Sanitaria San Carlos (IdISSC), 28040, Madrid, Spain.

Frederic Jaisser (F)

Sorbonne University, University of Pierre et Marie Curie, UMR_S 1138, Centre de Recherche des Cordeliers, 75006, Paris, France.
Paris Descartes University, Sorbonne Paris Cité, UMR_S 1138, Centre de Recherche des Cordeliers, 75006, Paris, France.
Inserm UMR_S 1138, Team 1, Centre de Recherche des Cordeliers, 75006, Paris, France.

Francine Behar-Cohen (F)

Inserm UMR_S 1138, Team 17, Centre de Recherche des Cordeliers, 75006, Paris, France. francine.behar@gmail.com.
Sorbonne University, University of Pierre et Marie Curie, UMR_S 1138, Centre de Recherche des Cordeliers, 75006, Paris, France. francine.behar@gmail.com.
Paris Descartes University, Sorbonne Paris Cité, UMR_S 1138, Centre de Recherche des Cordeliers, 75006, Paris, France. francine.behar@gmail.com.
Assistance Publique - Hôpitaux de Paris, Hôtel-Dieu de Paris, 75004, Paris, France. francine.behar@gmail.com.

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