Monozygotic Twins with Frontotemporal Dementia Due To Thr272fs GRN Mutation Discordant for Age At Onset.


Journal

Journal of Alzheimer's disease : JAD
ISSN: 1875-8908
Titre abrégé: J Alzheimers Dis
Pays: Netherlands
ID NLM: 9814863

Informations de publication

Date de publication:
2019
Historique:
pubmed: 29 1 2019
medline: 28 5 2020
entrez: 29 1 2019
Statut: ppublish

Résumé

We report the case of two monozygotic twins with Thr272fs mutation in progranulin gene. Both patients developed frontotemporal dementia with 5 years difference in age at onset (Twin 1:73 years, Twin 2:68 years), with early behavioral, language, dysexecutive, and memory problems. They had the same formal education (5 years), but while Twin 1 dedicated more to social and leisure activity, Twin 2 worked all her life. At neuroimaging (MRI for Twin 1 and CT for Twin 2), they both showed asymmetric atrophy with left predominance. The two were discordant for total tau levels in cerebrospinal fluid, neuropsychological testing, and smoking habits. The description of the twins can help identify environmental factors that influence the onset and phenotype of frontotemporal dementia.

Identifiants

pubmed: 30689572
pii: JAD180723
doi: 10.3233/JAD-180723
doi:

Substances chimiques

GRN protein, human 0
Progranulins 0

Types de publication

Case Reports Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

1173-1179

Auteurs

Giorgio Giulio Fumagalli (GG)

University of Milan, "Dino Ferrari" Center, Milan, Italy.
Foundation IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.
Department of Neurosciences, University of Florence, Psychology, Drug Research and Child Health (NEUROFARBA), Florence, Italy.

Luca Sacchi (L)

University of Milan, "Dino Ferrari" Center, Milan, Italy.
Foundation IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.

Paola Basilico (P)

University of Milan, "Dino Ferrari" Center, Milan, Italy.
Foundation IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.

Andrea Arighi (A)

University of Milan, "Dino Ferrari" Center, Milan, Italy.
Foundation IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.

Tiziana Carandini (T)

University of Milan, "Dino Ferrari" Center, Milan, Italy.
Foundation IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.

Marta Scarioni (M)

University of Milan, "Dino Ferrari" Center, Milan, Italy.
Foundation IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.

Annalisa Colombi (A)

University of Milan, "Dino Ferrari" Center, Milan, Italy.
Foundation IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.

Anna Pietroboni (A)

University of Milan, "Dino Ferrari" Center, Milan, Italy.
Foundation IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.

Laura Ghezzi (L)

University of Milan, "Dino Ferrari" Center, Milan, Italy.
Foundation IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.

Chiara Fenoglio (C)

University of Milan, "Dino Ferrari" Center, Milan, Italy.
Foundation IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.

Maria Serpente (M)

University of Milan, "Dino Ferrari" Center, Milan, Italy.
Foundation IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.

Marianna D'anca (M)

University of Milan, "Dino Ferrari" Center, Milan, Italy.
Foundation IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.

Marina Arcaro (M)

University of Milan, "Dino Ferrari" Center, Milan, Italy.
Foundation IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.

Matteo Mercurio (M)

University of Milan, "Dino Ferrari" Center, Milan, Italy.
Foundation IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.

Fabio Triulzi (F)

University of Milan, "Dino Ferrari" Center, Milan, Italy.
Foundation IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.

Elisa Scola (E)

University of Milan, "Dino Ferrari" Center, Milan, Italy.
Foundation IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.

Giorgio Marotta (G)

Foundation IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.

Elio Scarpini (E)

University of Milan, "Dino Ferrari" Center, Milan, Italy.
Foundation IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.

Daniela Galimberti (D)

University of Milan, "Dino Ferrari" Center, Milan, Italy.
Foundation IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.

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