Fratricide-resistant CD1a-specific CAR T cells for the treatment of cortical T-cell acute lymphoblastic leukemia.


Journal

Blood
ISSN: 1528-0020
Titre abrégé: Blood
Pays: United States
ID NLM: 7603509

Informations de publication

Date de publication:
23 05 2019
Historique:
received: 29 10 2018
accepted: 18 02 2019
pubmed: 24 2 2019
medline: 24 12 2019
entrez: 24 2 2019
Statut: ppublish

Résumé

Relapsed/refractory T-cell acute lymphoblastic leukemia (T-ALL) has a dismal outcome, and no effective targeted immunotherapies for T-ALL exist. The extension of chimeric antigen receptor (CAR) T cells (CARTs) to T-ALL remains challenging because the shared expression of target antigens between CARTs and T-ALL blasts leads to CART fratricide. CD1a is exclusively expressed in cortical T-ALL (coT-ALL), a major subset of T-ALL, and retained at relapse. This article reports that the expression of CD1a is mainly restricted to developing cortical thymocytes, and neither CD34

Identifiants

pubmed: 30796021
pii: S0006-4971(20)42537-6
doi: 10.1182/blood-2018-10-882944
pmc: PMC6554538
doi:

Substances chimiques

Antigens, CD1 0
CD1a antigen 0
Receptors, Chimeric Antigen 0

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

2291-2304

Subventions

Organisme : Medical Research Council
ID : MR/R006237/1
Pays : United Kingdom

Commentaires et corrections

Type : CommentIn

Informations de copyright

© 2019 by The American Society of Hematology.

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Auteurs

Diego Sánchez-Martínez (D)

Josep Carreras Leukemia Research Institute, Department of Biomedicine, School of Medicine, University of Barcelona, Barcelona, Spain.

Matteo L Baroni (ML)

Josep Carreras Leukemia Research Institute, Department of Biomedicine, School of Medicine, University of Barcelona, Barcelona, Spain.

Francisco Gutierrez-Agüera (F)

Josep Carreras Leukemia Research Institute, Department of Biomedicine, School of Medicine, University of Barcelona, Barcelona, Spain.

Heleia Roca-Ho (H)

Josep Carreras Leukemia Research Institute, Department of Biomedicine, School of Medicine, University of Barcelona, Barcelona, Spain.

Oscar Blanch-Lombarte (O)

AIDS Research Institute IrsiCaixa, Institut d'Investigació en Ciències de la Salut Germans Trias i Pujol, Universitat Autònoma de Barcelona, Barcelona, Spain.

Sara González-García (S)

Centro de Biología Molecular Severo Ochoa CSIC-UAM, Madrid, Spain.

Montserrat Torrebadell (M)

Haematology Laboratory, Institut de Recerca, Hospital Sant Joan de Déu, Barcelona, Spain.
Centro de Investigación Biomédica en Red de Enfermedades Raras, Instituto de Salud Carlos III, Madrid, Spain.

Jordi Junca (J)

Institut Catala d'Oncologia-Hospital Germans Trias i Pujol, Josep Carreras Leukaemia Research Institute, Universitat Autònoma de Barcelona, Badalona, Spain.

Manuel Ramírez-Orellana (M)

Department of Pediatric Hematology and Oncology, Hospital Infantil Universitario Niño Jesús, Universidad Autónoma de Madrid, Madrid, Spain.

Talía Velasco-Hernández (T)

Josep Carreras Leukemia Research Institute, Department of Biomedicine, School of Medicine, University of Barcelona, Barcelona, Spain.

Clara Bueno (C)

Josep Carreras Leukemia Research Institute, Department of Biomedicine, School of Medicine, University of Barcelona, Barcelona, Spain.

José Luís Fuster (JL)

Sección de Oncohematología Pediátrica, Hospital Clínico Universitario Virgen de la Arrixaca, Murcia, Spain.
Instituto Murciano de Investigación Biosanitaria, Murcia, Spain.

Julia G Prado (JG)

AIDS Research Institute IrsiCaixa, Institut d'Investigació en Ciències de la Salut Germans Trias i Pujol, Universitat Autònoma de Barcelona, Barcelona, Spain.

Julien Calvo (J)

Univerité Paris Diderot and Université Paris-Sud, Unité Mixte de Recherche 967, INSERM, U967, Fontenay-aux-Roses, France.

Benjamin Uzan (B)

Univerité Paris Diderot and Université Paris-Sud, Unité Mixte de Recherche 967, INSERM, U967, Fontenay-aux-Roses, France.

Jan Cools (J)

KU Center for Human Genetics and VIB Center for Cancer Biology, Leuven, Belgium.

Mireia Camos (M)

Haematology Laboratory, Institut de Recerca, Hospital Sant Joan de Déu, Barcelona, Spain.
Centro de Investigación Biomédica en Red de Enfermedades Raras, Instituto de Salud Carlos III, Madrid, Spain.

Françoise Pflumio (F)

Univerité Paris Diderot and Université Paris-Sud, Unité Mixte de Recherche 967, INSERM, U967, Fontenay-aux-Roses, France.

María Luisa Toribio (ML)

Centro de Biología Molecular Severo Ochoa CSIC-UAM, Madrid, Spain.

Pablo Menéndez (P)

Josep Carreras Leukemia Research Institute, Department of Biomedicine, School of Medicine, University of Barcelona, Barcelona, Spain.
Centro de Investigación Biomedica en Red-Oncología, Instituto de Salud Carlos III, Barcelona, Spain; and.
Instituciò Catalana de Recerca i Estudis Avançats, Barcelona, Spain.

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Classifications MeSH