Requirements for improving health and well-being of children with Prader-Willi syndrome and their families.


Journal

Journal of paediatrics and child health
ISSN: 1440-1754
Titre abrégé: J Paediatr Child Health
Pays: Australia
ID NLM: 9005421

Informations de publication

Date de publication:
Sep 2019
Historique:
received: 25 02 2019
revised: 15 05 2019
accepted: 02 06 2019
pubmed: 2 7 2019
medline: 7 2 2021
entrez: 2 7 2019
Statut: ppublish

Résumé

Prader-Willi syndrome (PWS) is a rare genetic condition with multi-system involvement. The literature was reviewed to describe neurodevelopment and the behavioural phenotype, endocrine and metabolic disorders and respiratory and sleep functioning. Implications for child and family quality of life were explored. Challenging behaviours contribute to poorer well-being and quality of life for both the child and caregiver. Recent evidence indicates healthy outcomes of weight and height can be achieved with growth hormone therapy and dietary restriction and should be the current target for all individuals with PWS. Gaps in the literature included therapies to manage challenging behaviours, as well as understanding the effects of growth hormone on respiratory and sleep function. New knowledge regarding the transition of children and families from schooling and paediatric health services to employment, accommodation and adult health services is also needed. Developing a national population-based registry could address these knowledge gaps and inform advocacy for support services that improve the well-being of individuals with PWS and their families.

Identifiants

pubmed: 31257692
doi: 10.1111/jpc.14546
pmc: PMC6852695
doi:

Types de publication

Journal Article Review

Langues

eng

Sous-ensembles de citation

IM

Pagination

1029-1037

Subventions

Organisme : Perth Children's Hospital Foundation
Organisme : Prader Willi Association USA

Informations de copyright

© 2019 The Authors. Journal of Paediatrics and Child Health published by John Wiley & Sons Australia, Ltd on behalf of Paediatrics and Child Health Division (The Royal Australasian College of Physicians).

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Auteurs

Jessica Mackay (J)

Telethon Kids Institute, Centre for Child Health Research, University of Western Australia, Perth, Western Australia, Australia.
School of Medicine, University of Western Australia, Perth, Western Australia, Australia.

Zoe McCallum (Z)

Department of Neurodevelopment and Disability, Royal Children's Hospital, Melbourne, Victoria, Australia.
Department of Gastroenterology and Clinical Nutrition, Royal Children's Hospital, Melbourne, Victoria, Australia.

Geoffrey R Ambler (GR)

Institute of Endocrinology and Diabetes, Children's Hospital at Westmead, Sydney, New South Wales, Australia.

Komal Vora (K)

Department of Paediatric Endocrinology and Diabetes, John Hunter Children's Hospital, Newcastle, New South Wales, Australia.

Gillian Nixon (G)

Melbourne Children's Sleep Centre, Monash Children's Hospital, Melbourne, Victoria, Australia.
The Ritchie Centre, Melbourne, Victoria, Australia.
Department of Paediatrics, Monash University, Melbourne, Victoria, Australia.

Philip Bergman (P)

Department of Paediatrics, Monash University, Melbourne, Victoria, Australia.
Department of Paediatric Endocrinology and Diabetes, Monash Children's Hospital, Melbourne, Victoria, Australia.

Nora Shields (N)

School of Allied Health, La Trobe University, Melbourne, Victoria, Australia.

Kate Milner (K)

Department of Neurodevelopment and Disability, Royal Children's Hospital, Melbourne, Victoria, Australia.
Centre for International Child Health, Murdoch Children's Research Institute, Melbourne, Victoria, Australia.

Nitin Kapur (N)

Respiratory and Sleep Medicine, Queensland Children's Hospital, Brisbane, Queensland, Australia.
School of Clinical Medicine, University of Queensland, Brisbane, Queensland, Australia.

Patricia Crock (P)

Department of Paediatric Endocrinology and Diabetes, John Hunter Children's Hospital, Newcastle, New South Wales, Australia.
Hunter Medical Research Institute, University of Newcastle, Newcastle, New South Wales, Australia.

Daan Caudri (D)

Telethon Kids Institute, Centre for Child Health Research, University of Western Australia, Perth, Western Australia, Australia.
Erasmus University Medical Center, Rotterdam, the Netherlands.

Jaqueline Curran (J)

Department of Endocrinology, Perth Children's Hospital, Perth, Western Australia, Australia.

Charles Verge (C)

Department of Endocrinology, Sydney Children's Hospital, Sydney, New South Wales, Australia.
School of Women's and Children's Health, University of New South Wales, Sydney, New South Wales, Australia.

Chris Seton (C)

Department of Sleep Medicine, Children's Hospital Westmead, Sydney, New South Wales, Australia.
Woolcock Institute of Medical Research, Sydney University, Sydney, New South Wales, Australia.

Andrew Tai (A)

Respiratory and Sleep Department, Women's and Children's Hospital, Adelaide, South Australia, Australia.

Elaine Tham (E)

Endrocrinology and Diabetes Department, Women's and Children's Hospital, Adelaide, South Australia, Australia.

Yassmin Musthaffa (Y)

Diamantina Institute, Faculty of Medicine, University of Queensland, Brisbane, Queensland, Australia.
Translational Research Institute, University of Queensland, Brisbane, Queensland, Australia.

Antony R Lafferty (AR)

Department of Endocrinology and Diabetes, Canberra Hospital, Canberra, Australian Capital Territory, Australia.
Medical School, Australian National University, Canberra, Australian Capital Territory, Australia.

Greg Blecher (G)

Department of Sleep Medicine, Sydney Children's Hospital, Sydney, New South Wales, Australia.

Jessica Harper (J)

Department of Endocrinology, Sydney Children's Hospital, Sydney, New South Wales, Australia.

Cara Schofield (C)

Telethon Kids Institute, Centre for Child Health Research, University of Western Australia, Perth, Western Australia, Australia.

Aleisha Nielsen (A)

Respiratory and Sleep Medicine, Perth Children's Hospital, Perth, Western Australia, Australia.

Andrew Wilson (A)

Telethon Kids Institute, Centre for Child Health Research, University of Western Australia, Perth, Western Australia, Australia.
Respiratory and Sleep Medicine, Perth Children's Hospital, Perth, Western Australia, Australia.

Helen Leonard (H)

Telethon Kids Institute, Centre for Child Health Research, University of Western Australia, Perth, Western Australia, Australia.

Catherine S Choong (CS)

Telethon Kids Institute, Centre for Child Health Research, University of Western Australia, Perth, Western Australia, Australia.
Department of Endocrinology, Perth Children's Hospital, Perth, Western Australia, Australia.

Jenny Downs (J)

Telethon Kids Institute, Centre for Child Health Research, University of Western Australia, Perth, Western Australia, Australia.
School of Physiotherapy and Exercise Science, Curtin University, Perth, Western Australia, Australia.

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