Androgenic Effects on Ventricular Repolarization: A Translational Study From the International Pharmacovigilance Database to iPSC-Cardiomyocytes.


Journal

Circulation
ISSN: 1524-4539
Titre abrégé: Circulation
Pays: United States
ID NLM: 0147763

Informations de publication

Date de publication:
24 09 2019
Historique:
pubmed: 6 8 2019
medline: 18 6 2020
entrez: 6 8 2019
Statut: ppublish

Résumé

Male hypogonadism, arising from a range of etiologies including androgen-deprivation therapies (ADTs), has been reported as a risk factor for acquired long-QT syndrome (aLQTS) and torsades de pointes (TdP). A full description of the clinical features of aLQTS associated with ADT and of underlying mechanisms is lacking. We searched the international pharmacovigilance database VigiBase for men (n=6 560 565 individual case safety reports) presenting with aLQTS, TdP, or sudden death associated with ADT. In cardiomyocytes derived from induced pluripotent stem cells from men, we studied electrophysiological effects of ADT and dihydrotestosterone. Among subjects receiving ADT in VigiBase, we identified 184 cases of aLQTS (n=168) and/or TdP (n=68; 11% fatal), and 99 with sudden death. Of the 10 ADT drugs examined, 7 had a disproportional association (reporting odds ratio=1.4-4.7; QT prolongation and TdP are a risk in men receiving enzalutamide and other ADTs. URL: https://www.clinicaltrials.gov. Unique identifier: NCT03193138.

Sections du résumé

BACKGROUND
Male hypogonadism, arising from a range of etiologies including androgen-deprivation therapies (ADTs), has been reported as a risk factor for acquired long-QT syndrome (aLQTS) and torsades de pointes (TdP). A full description of the clinical features of aLQTS associated with ADT and of underlying mechanisms is lacking.
METHODS
We searched the international pharmacovigilance database VigiBase for men (n=6 560 565 individual case safety reports) presenting with aLQTS, TdP, or sudden death associated with ADT. In cardiomyocytes derived from induced pluripotent stem cells from men, we studied electrophysiological effects of ADT and dihydrotestosterone.
RESULTS
Among subjects receiving ADT in VigiBase, we identified 184 cases of aLQTS (n=168) and/or TdP (n=68; 11% fatal), and 99 with sudden death. Of the 10 ADT drugs examined, 7 had a disproportional association (reporting odds ratio=1.4-4.7;
CONCLUSIONS
QT prolongation and TdP are a risk in men receiving enzalutamide and other ADTs.
CLINICAL TRIAL REGISTRATION
URL: https://www.clinicaltrials.gov. Unique identifier: NCT03193138.

Identifiants

pubmed: 31378084
doi: 10.1161/CIRCULATIONAHA.119.040162
pmc: PMC6756939
mid: NIHMS1532205
doi:

Substances chimiques

Androgens 0
Antineoplastic Agents 0
Benzamides 0
Nitriles 0
Phenylthiohydantoin 2010-15-3
enzalutamide 93T0T9GKNU

Banques de données

ClinicalTrials.gov
['NCT03193138']

Types de publication

Journal Article Research Support, N.I.H., Extramural Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

1070-1080

Subventions

Organisme : NIGMS NIH HHS
ID : P50 GM115305
Pays : United States
Organisme : NHLBI NIH HHS
ID : R35 HL144980
Pays : United States
Organisme : NHLBI NIH HHS
ID : R56 HL141466
Pays : United States

Commentaires et corrections

Type : CommentIn
Type : CommentIn

Références

J Cardiovasc Pharmacol. 2001 Nov;38(5):737-44
pubmed: 11602820
Circulation. 2003 Feb 18;107(6):838-44
pubmed: 12591753
N Engl J Med. 2004 Mar 4;350(10):1013-22
pubmed: 14999113
Eur Heart J. 2005 Mar;26(6):590-7
pubmed: 15637086
Am J Cardiol. 2009 Mar 15;103(6):887-90
pubmed: 19268751
Circulation. 2010 Feb 16;121(6):833-40
pubmed: 20124128
Clin Pharmacol Ther. 2010 Jul;88(1):88-94
pubmed: 20485337
Front Physiol. 2012 Apr 10;3:89
pubmed: 22514541
Sci Transl Med. 2012 Apr 25;4(131):131ra50
pubmed: 22539774
Pharmacoepidemiol Drug Saf. 2013 Oct;22(10):1119-29
pubmed: 23832706
N Engl J Med. 2014 Jul 31;371(5):424-33
pubmed: 24881730
Circulation. 2014 Jul 15;130(3):224-34
pubmed: 24895457
BJU Int. 2016 Feb;117(2):215-25
pubmed: 25818596
Clin Pharmacokinet. 2015 Oct;54(10):1043-55
pubmed: 25917876
J Clin Endocrinol Metab. 2016 Jul;101(7):2776-84
pubmed: 27167057
Pharmacol Ther. 2016 Nov;167:38-47
pubmed: 27452340
Eur Heart J. 2016 Sep 21;37(36):2768-2801
pubmed: 27567406
N Z Med J. 2016 Nov 18;129(1445):124-127
pubmed: 27857247
J Clin Endocrinol Metab. 2017 May 1;102(5):1478-1485
pubmed: 27992261
PLoS One. 2017 Aug 11;12(8):e0181875
pubmed: 28800628
Sci Rep. 2018 Jan 9;8(1):163
pubmed: 29317749
J Pharmacol Exp Ther. 2018 Jun;365(3):460-466
pubmed: 29563327
Pharmacol Ther. 2018 Sep;189:89-103
pubmed: 29698683
Heart. 2018 Nov;104(22):1859-1863
pubmed: 29720397
J Endocr Soc. 2018 Apr 20;2(5):485-496
pubmed: 29761176
N Engl J Med. 2018 Jun 28;378(26):2465-2474
pubmed: 29949494
Circulation. 2018 Jul 3;138(1):110-113
pubmed: 29967236
JAMA Cardiol. 2018 Sep 1;3(9):877-882
pubmed: 30073300
Int Heart J. 2019 Jan 25;60(1):193-198
pubmed: 30518719
Cardiovasc Res. 2019 Apr 15;115(5):878-894
pubmed: 30698686
Eur Heart J. 2019 Jun 14;40(23):1832-1836
pubmed: 30753398
N Engl J Med. 1994 Jan 13;330(2):120-5
pubmed: 7505051
J Am Coll Cardiol. 1994 Feb;23(2):296-301
pubmed: 7905012
JAMA. 1993 Dec 1;270(21):2590-7
pubmed: 8230644

Auteurs

Joe-Elie Salem (JE)

Assitance Publique Hopitaux de Paris, Pitié-Salpêtriére Hospital, Departments of Pharmacology and Cardiology, UNICO-GRECO Cardio-oncology Program, Centre d'investigation clinique-1421, Pharmacovigilance Unit (J-E.S., X.W., E.G., F.H-L., B.L-V., C.F-B.), INSERM, Sorbonne Université, Paris, France.
Department of Medicine (J-E.S., T.Y., J.J.M., B.C.K., A.M.G., D.M.R.), Vanderbilt University Medical Center, Nashville, TN.
Department of Pharmacology (J-E.S., T.Y., B.C.K., D.M.R.), Vanderbilt University Medical Center, Nashville, TN.

Tao Yang (T)

Department of Medicine (J-E.S., T.Y., J.J.M., B.C.K., A.M.G., D.M.R.), Vanderbilt University Medical Center, Nashville, TN.
Department of Pharmacology (J-E.S., T.Y., B.C.K., D.M.R.), Vanderbilt University Medical Center, Nashville, TN.

Javid J Moslehi (JJ)

Department of Medicine (J-E.S., T.Y., J.J.M., B.C.K., A.M.G., D.M.R.), Vanderbilt University Medical Center, Nashville, TN.

Xavier Waintraub (X)

Assitance Publique Hopitaux de Paris, Pitié-Salpêtriére Hospital, Departments of Pharmacology and Cardiology, UNICO-GRECO Cardio-oncology Program, Centre d'investigation clinique-1421, Pharmacovigilance Unit (J-E.S., X.W., E.G., F.H-L., B.L-V., C.F-B.), INSERM, Sorbonne Université, Paris, France.

Estelle Gandjbakhch (E)

Assitance Publique Hopitaux de Paris, Pitié-Salpêtriére Hospital, Departments of Pharmacology and Cardiology, UNICO-GRECO Cardio-oncology Program, Centre d'investigation clinique-1421, Pharmacovigilance Unit (J-E.S., X.W., E.G., F.H-L., B.L-V., C.F-B.), INSERM, Sorbonne Université, Paris, France.

Anne Bachelot (A)

IE3M, Department of Endocrinology and Reproductive Medicine, and Centre de Référence des Maladies Endocriniennes Rares de la croissance et Centre des Pathologies gynécologiques Rares (A.B.), INSERM, Sorbonne Université, Paris, France.

Francoise Hidden-Lucet (F)

Assitance Publique Hopitaux de Paris, Pitié-Salpêtriére Hospital, Departments of Pharmacology and Cardiology, UNICO-GRECO Cardio-oncology Program, Centre d'investigation clinique-1421, Pharmacovigilance Unit (J-E.S., X.W., E.G., F.H-L., B.L-V., C.F-B.), INSERM, Sorbonne Université, Paris, France.

Jean-Sebastien Hulot (JS)

Université Paris-Descartes, Sorbonne Paris Cité Paris Cardiovascular Research Center, Institut national de la santé et de la recherche médicale UMRS 970, Hôpital Européen Georges Pompidou, AP-HP, Paris, France (J-S-.H.).

Bjorn C Knollmann (BC)

Department of Medicine (J-E.S., T.Y., J.J.M., B.C.K., A.M.G., D.M.R.), Vanderbilt University Medical Center, Nashville, TN.
Department of Pharmacology (J-E.S., T.Y., B.C.K., D.M.R.), Vanderbilt University Medical Center, Nashville, TN.

Benedicte Lebrun-Vignes (B)

Assitance Publique Hopitaux de Paris, Pitié-Salpêtriére Hospital, Departments of Pharmacology and Cardiology, UNICO-GRECO Cardio-oncology Program, Centre d'investigation clinique-1421, Pharmacovigilance Unit (J-E.S., X.W., E.G., F.H-L., B.L-V., C.F-B.), INSERM, Sorbonne Université, Paris, France.

Christian Funck-Brentano (C)

Assitance Publique Hopitaux de Paris, Pitié-Salpêtriére Hospital, Departments of Pharmacology and Cardiology, UNICO-GRECO Cardio-oncology Program, Centre d'investigation clinique-1421, Pharmacovigilance Unit (J-E.S., X.W., E.G., F.H-L., B.L-V., C.F-B.), INSERM, Sorbonne Université, Paris, France.

Andrew M Glazer (AM)

Department of Medicine (J-E.S., T.Y., J.J.M., B.C.K., A.M.G., D.M.R.), Vanderbilt University Medical Center, Nashville, TN.

Dan M Roden (DM)

Department of Medicine (J-E.S., T.Y., J.J.M., B.C.K., A.M.G., D.M.R.), Vanderbilt University Medical Center, Nashville, TN.
Department of Pharmacology (J-E.S., T.Y., B.C.K., D.M.R.), Vanderbilt University Medical Center, Nashville, TN.
Department of Biomedical Informatics, Vanderbilt University Medical Center (D.M.R.), Vanderbilt University Medical Center, Nashville, TN.

Articles similaires

[Redispensing of expensive oral anticancer medicines: a practical application].

Lisanne N van Merendonk, Kübra Akgöl, Bastiaan Nuijen
1.00
Humans Antineoplastic Agents Administration, Oral Drug Costs Counterfeit Drugs

Smoking Cessation and Incident Cardiovascular Disease.

Jun Hwan Cho, Seung Yong Shin, Hoseob Kim et al.
1.00
Humans Male Smoking Cessation Cardiovascular Diseases Female
Humans United States Aged Cross-Sectional Studies Medicare Part C
1.00
Humans Yoga Low Back Pain Female Male

Classifications MeSH