Targeting multiple G-quadruplex-forming DNA sequences: Design, biophysical and biological evaluations of indolo-naphthyridine scaffold derivatives.


Journal

European journal of medicinal chemistry
ISSN: 1768-3254
Titre abrégé: Eur J Med Chem
Pays: France
ID NLM: 0420510

Informations de publication

Date de publication:
15 Nov 2019
Historique:
received: 24 06 2019
revised: 02 08 2019
accepted: 14 08 2019
pubmed: 26 8 2019
medline: 3 1 2020
entrez: 26 8 2019
Statut: ppublish

Résumé

It is well recognized that the non-canonical DNA structures known as G-quadruplexes (G4s) have a potential anticancer significance and several compounds have been discovered and evaluated as promising G4 binders with anticancer activity. Here, starting from a promising hit with an indolo-naphthyridine scaffold, a small series of five indolo-naphthyridine based derivatives have been designed and evaluated as G4-targeting compounds. FRET biophysical studies were performed on multiple DNA G4 structures, leading to the identification of a multi-target G4 stabilizer with a slight preference for the c-KIT1 and a good G4 over duplex selectivity. The good affinity of this compound against c-KIT1 G4 was also confirmed by SPR and MST experiments, while biological assays revealed its cytotoxic activity on tumour cells. Finally, Molecular Dynamics simulations helped to elucidate the stabilization effect of the selected compound against the c-KIT1 G4.

Identifiants

pubmed: 31446246
pii: S0223-5234(19)30761-5
doi: 10.1016/j.ejmech.2019.111627
pii:
doi:

Substances chimiques

Antineoplastic Agents 0
DNA, Neoplasm 0
Indoles 0
Ligands 0
Naphthyridines 0

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

111627

Informations de copyright

Copyright © 2019 Elsevier Masson SAS. All rights reserved.

Auteurs

Raffaella Catalano (R)

Dipartimento di Scienze della Salute, Università "Magna Græcia", Campus Salvatore Venuta, Viale Europa, 88100, Catanzaro, Italy; Net4Science srl, Università "Magna Græcia", Campus Salvatore Venuta, Viale Europa, 88100, Catanzaro, Italy.

Federica Moraca (F)

Dipartimento di Scienze della Salute, Università "Magna Græcia", Campus Salvatore Venuta, Viale Europa, 88100, Catanzaro, Italy; Net4Science srl, Università "Magna Græcia", Campus Salvatore Venuta, Viale Europa, 88100, Catanzaro, Italy; Department of Pharmacy, University "Federico II" of Naples, Via D. Montesano 49, 80131, Naples, Italy. Electronic address: federica.moraca@unina.it.

Jussara Amato (J)

Department of Pharmacy, University "Federico II" of Naples, Via D. Montesano 49, 80131, Naples, Italy. Electronic address: jussara.amato@unina.it.

Camilla Cristofari (C)

Department of Pharmaceutical and Pharmacological Sciences, University of Padova, 35131, Padova, Italy.

Riccardo Rigo (R)

Department of Pharmaceutical and Pharmacological Sciences, University of Padova, 35131, Padova, Italy.

Lisa Dalla Via (LD)

Department of Pharmaceutical and Pharmacological Sciences, University of Padova, 35131, Padova, Italy.

Roberta Rocca (R)

Dipartimento di Scienze della Salute, Università "Magna Græcia", Campus Salvatore Venuta, Viale Europa, 88100, Catanzaro, Italy; Net4Science srl, Università "Magna Græcia", Campus Salvatore Venuta, Viale Europa, 88100, Catanzaro, Italy.

Antonio Lupia (A)

Dipartimento di Scienze della Salute, Università "Magna Græcia", Campus Salvatore Venuta, Viale Europa, 88100, Catanzaro, Italy; Net4Science srl, Università "Magna Græcia", Campus Salvatore Venuta, Viale Europa, 88100, Catanzaro, Italy.

Annalisa Maruca (A)

Dipartimento di Scienze della Salute, Università "Magna Græcia", Campus Salvatore Venuta, Viale Europa, 88100, Catanzaro, Italy; Net4Science srl, Università "Magna Græcia", Campus Salvatore Venuta, Viale Europa, 88100, Catanzaro, Italy.

Giosuè Costa (G)

Dipartimento di Scienze della Salute, Università "Magna Græcia", Campus Salvatore Venuta, Viale Europa, 88100, Catanzaro, Italy; Net4Science srl, Università "Magna Græcia", Campus Salvatore Venuta, Viale Europa, 88100, Catanzaro, Italy.

Bruno Catalanotti (B)

Department of Pharmacy, University "Federico II" of Naples, Via D. Montesano 49, 80131, Naples, Italy.

Anna Artese (A)

Dipartimento di Scienze della Salute, Università "Magna Græcia", Campus Salvatore Venuta, Viale Europa, 88100, Catanzaro, Italy; Net4Science srl, Università "Magna Græcia", Campus Salvatore Venuta, Viale Europa, 88100, Catanzaro, Italy.

Bruno Pagano (B)

Department of Pharmacy, University "Federico II" of Naples, Via D. Montesano 49, 80131, Naples, Italy.

Antonio Randazzo (A)

Department of Pharmacy, University "Federico II" of Naples, Via D. Montesano 49, 80131, Naples, Italy.

Claudia Sissi (C)

Department of Pharmaceutical and Pharmacological Sciences, University of Padova, 35131, Padova, Italy.

Ettore Novellino (E)

Department of Pharmacy, University "Federico II" of Naples, Via D. Montesano 49, 80131, Naples, Italy.

Stefano Alcaro (S)

Dipartimento di Scienze della Salute, Università "Magna Græcia", Campus Salvatore Venuta, Viale Europa, 88100, Catanzaro, Italy; Net4Science srl, Università "Magna Græcia", Campus Salvatore Venuta, Viale Europa, 88100, Catanzaro, Italy.

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Classifications MeSH