Treatment Patterns and Use of Resources in Patients With Tuberous Sclerosis Complex: Insights From the TOSCA Registry.
TOSCA
TSC
management
rare diseases
registry
resource use
Journal
Frontiers in neurology
ISSN: 1664-2295
Titre abrégé: Front Neurol
Pays: Switzerland
ID NLM: 101546899
Informations de publication
Date de publication:
2019
2019
Historique:
received:
21
08
2019
accepted:
14
10
2019
entrez:
12
11
2019
pubmed:
12
11
2019
medline:
12
11
2019
Statut:
epublish
Résumé
Tuberous Sclerosis Complex (TSC) is a rare autosomal-dominant disorder caused by mutations in the
Identifiants
pubmed: 31708865
doi: 10.3389/fneur.2019.01144
pmc: PMC6823684
doi:
Types de publication
Journal Article
Langues
eng
Pagination
1144Informations de copyright
Copyright © 2019 Marques, Belousova, Benedik, Carter, Cottin, Curatolo, Dahlin, D'Amato, Beaure d'Augères, de Vries, Ferreira, Feucht, Fladrowski, Hertzberg, Jozwiak, Lawson, Macaya, Nabbout, O'Callaghan, Qin, Sander, Sauter, Shah, Takahashi, Touraine, Youroukos, Zonnenberg, Kingswood and Jansen.
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