Romidepsin Plus Liposomal Doxorubicin Is Safe and Effective in Patients with Relapsed or Refractory T-Cell Lymphoma: Results of a Phase I Dose-Escalation Study.


Journal

Clinical cancer research : an official journal of the American Association for Cancer Research
ISSN: 1557-3265
Titre abrégé: Clin Cancer Res
Pays: United States
ID NLM: 9502500

Informations de publication

Date de publication:
01 03 2020
Historique:
received: 04 07 2019
revised: 08 10 2019
accepted: 20 11 2019
pubmed: 28 11 2019
medline: 5 1 2021
entrez: 28 11 2019
Statut: ppublish

Résumé

The histone deacetylase (HDAC) inhibitor romidepsin and the anthracycline liposomal doxorubicin (LD) have modest single-agent activity in cutaneous T-cell lymphoma (CTCL) and peripheral T-cell lymphoma (PTCL). We investigated the safety and efficacy of the combination of these two agents in CTCL and PTCL. Using CTCL cell lines and primary CTCL tumor cells, we demonstrated synergistic antitumor activity with romidepsin plus doxorubicin. We then conducted a phase I dose-escalation study of the romidepsin/LD combination in relapsed/refractory CTCL and PTCL. The primary objective was to determine the MTD of romidepsin in combination with LD at 20 mg/m Eleven patients with CTCL and 12 patients with PTCL were treated. The MTD of romidepsin was determined to be 12 mg/m Romidepsin plus LD demonstrated an acceptable safety profile and promising clinical efficacy with deep skin responses in relapsed/refractory CTCL. Thus, this combination could be considered as a bridge to skin-directed treatment or allogeneic hematopoietic cell transplantation in patients with aggressive CTCL.

Identifiants

pubmed: 31772119
pii: 1078-0432.CCR-19-2152
doi: 10.1158/1078-0432.CCR-19-2152
doi:

Substances chimiques

Depsipeptides 0
liposomal doxorubicin 0
Polyethylene Glycols 3WJQ0SDW1A
Doxorubicin 80168379AG
romidepsin CX3T89XQBK

Types de publication

Clinical Trial, Phase I Journal Article Multicenter Study Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

1000-1008

Informations de copyright

©2019 American Association for Cancer Research.

Auteurs

Khoan Vu (K)

Division of Hematology and Oncology, Department of Medicine, University of California, San Francisco, California.

Chi-Heng Wu (CH)

Division of Hematology and Oncology, Department of Medicine, University of California, San Francisco, California.

Chen-Yen Yang (CY)

Division of Hematology and Oncology, Department of Medicine, University of California, San Francisco, California.

Aaron Zhan (A)

Division of Hematology and Oncology, Department of Medicine, University of California, San Francisco, California.

Erika Cavallone (E)

Division of Hematology and Oncology, Department of Medicine, University of California, San Francisco, California.

Wade Berry (W)

Division of Hematology and Oncology, Department of Medicine, University of California, San Francisco, California.

Pamela Heeter (P)

Division of Hematology, Department of Internal Medicine, James Comprehensive Cancer Center, The Ohio State University, Columbus, Ohio.

Laura Pincus (L)

Division of Hematology and Oncology, Department of Medicine, University of California, San Francisco, California.

Matthew J Wieduwilt (MJ)

Moores Cancer Center, University of California, San Diego, California.

Basem M William (BM)

Division of Hematology, Department of Internal Medicine, James Comprehensive Cancer Center, The Ohio State University, Columbus, Ohio.

Charalambos Andreadis (C)

Division of Hematology and Oncology, Department of Medicine, University of California, San Francisco, California.

Lawrence K Kaplan (LK)

Division of Hematology and Oncology, Department of Medicine, University of California, San Francisco, California.

Frank McCormick (F)

Hellen Diller Family Cancer Center, University of California, San Francisco, California.

Pierluigi Porcu (P)

Division of Hematology, Department of Internal Medicine, James Comprehensive Cancer Center, The Ohio State University, Columbus, Ohio.

Jonathan E Brammer (JE)

Division of Hematology, Department of Internal Medicine, James Comprehensive Cancer Center, The Ohio State University, Columbus, Ohio.

Weiyun Z Ai (WZ)

Division of Hematology and Oncology, Department of Medicine, University of California, San Francisco, California. weiyun.ai@ucsf.edu.

Articles similaires

[Redispensing of expensive oral anticancer medicines: a practical application].

Lisanne N van Merendonk, Kübra Akgöl, Bastiaan Nuijen
1.00
Humans Antineoplastic Agents Administration, Oral Drug Costs Counterfeit Drugs

Smoking Cessation and Incident Cardiovascular Disease.

Jun Hwan Cho, Seung Yong Shin, Hoseob Kim et al.
1.00
Humans Male Smoking Cessation Cardiovascular Diseases Female
Humans United States Aged Cross-Sectional Studies Medicare Part C
1.00
Humans Yoga Low Back Pain Female Male

Classifications MeSH