How is the Pharmaceutical Industry Structured to Optimize Pediatric Drug Development? Existing Pediatric Structure Models and Proposed Recommendations for Structural Enhancement.

Child Drug development Expert group Medicines for children Pediatric medicines Pediatric structures

Journal

Therapeutic innovation & regulatory science
ISSN: 2168-4804
Titre abrégé: Ther Innov Regul Sci
Pays: Switzerland
ID NLM: 101597411

Informations de publication

Date de publication:
09 2020
Historique:
received: 30 05 2019
accepted: 26 11 2019
pubmed: 8 2 2020
medline: 3 6 2021
entrez: 8 2 2020
Statut: ppublish

Résumé

Pediatric regulations enacted in both Europe and the USA have disrupted the pharmaceutical industry, challenging business and drug development processes, and organizational structures. Over the last decade, with science and innovation evolving, industry has moved from a reactive to a proactive mode, investing in building appropriate structures and capabilities as part of their business strategy to better tackle the challenges and opportunities of pediatric drug development. The EFGCP Children's Medicines Working Party and the IQ Pediatric working group have joined their efforts to survey their member company representatives to understand how pharmaceutical companies are organized to fulfill their regulatory obligations and optimize their pediatric drug development programs. Key success factors and recommendations for a fit-for-purpose Pediatric Expert Group (PEG) were identified. Pediatric structures and expert groups were shown to be important to support optimization of the development of pediatric medicines.

Sections du résumé

BACKGROUND
Pediatric regulations enacted in both Europe and the USA have disrupted the pharmaceutical industry, challenging business and drug development processes, and organizational structures. Over the last decade, with science and innovation evolving, industry has moved from a reactive to a proactive mode, investing in building appropriate structures and capabilities as part of their business strategy to better tackle the challenges and opportunities of pediatric drug development.
METHODS
The EFGCP Children's Medicines Working Party and the IQ Pediatric working group have joined their efforts to survey their member company representatives to understand how pharmaceutical companies are organized to fulfill their regulatory obligations and optimize their pediatric drug development programs.
RESULTS
Key success factors and recommendations for a fit-for-purpose Pediatric Expert Group (PEG) were identified.
CONCLUSION
Pediatric structures and expert groups were shown to be important to support optimization of the development of pediatric medicines.

Identifiants

pubmed: 32030690
doi: 10.1007/s43441-020-00116-4
pii: 10.1007/s43441-020-00116-4
pmc: PMC7458895
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

1076-1084

Commentaires et corrections

Type : ErratumIn

Références

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Auteurs

Thomas Severin (T)

Global Drug Development, Novartis Pharma AG, Novartis Campus, 4002, Basel, Switzerland. thomas.severin@novartis.com.

Solange Corriol-Rohou (S)

Global Regulatory Excellence, AstraZeneca, Paris, France.

Christina Bucci-Rechtweg (C)

Global Health Policy, Regulatory Affairs, Novartis Pharmaceuticals Corporation, East Hanover, NJ, USA.

Kristina An Haack (K)

R&D/Clinical Development Rare Diseases, Sanofi/Genzyme, Chilly-Mazarin, France.

Sabine Fuerst-Recktenwald (S)

Product Development Neurology, F. Hoffmann-La Roche Ltd., Basel, Switzerland.

Pirkko Lepola (P)

Department of Children and Adolescents, Helsinki University Hospital, Helsinki, Finland.

Ensio Norjavaara (E)

Global Medicines Development, AstraZeneca, Mölndal, Sweden.

Martine Dehlinger-Kremer (M)

Pediatric Development, Synteract, & EUCROF, Munich, Germany.

Sebastian Haertter (S)

Translational Medicine & Clinical Pharmacology, Boehringer-Ingelheim, Ingelheim, Germany.

S Y Amy Cheung (SYA)

Certara, Princeton, NJ, USA.

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Classifications MeSH