Efficacy of phosphodiesterase type 5 inhibitors in univentricular congenital heart disease: the SV-INHIBITION study design.

Congenital heart defect Exercise capacity Pulmonary hypertension Pulmonary vasodilator Sildenafil Single ventricle

Journal

ESC heart failure
ISSN: 2055-5822
Titre abrégé: ESC Heart Fail
Pays: England
ID NLM: 101669191

Informations de publication

Date de publication:
04 2020
Historique:
received: 03 12 2019
revised: 04 01 2020
accepted: 12 01 2020
pubmed: 10 3 2020
medline: 22 6 2021
entrez: 10 3 2020
Statut: ppublish

Résumé

In univentricular hearts, selective lung vasodilators such as phosphodiesterase type 5 (PDE5) inhibitors would decrease pulmonary resistance and improve exercise tolerance. However, the level of evidence for the use of PDE5 inhibitors in patients with a single ventricle (SV) remains limited. We present the SV-INHIBITION study rationale, design, and methods. The SV-INHIBITION trial is a nationwide multicentre, randomized, double blind, placebo-controlled, Phase III study, aiming to evaluate the efficacy of sildenafil on the ventilatory efficiency during exercise, in teenagers and adult patients (>15 years old) with an SV. Patients with a mean pulmonary arterial pressure >15 mmHg and a trans-pulmonary gradient >5 mmHg, measured by cardiac catheterization, will be eligible. The primary outcome is the variation of the VE/VCO The SV-INHIBITION study aims to answer the question whether PDE5 inhibitors should be prescribed in patients with an SV. This trial has been built focusing on the three levels of research defined by the World Health Organization: disability (exercise tolerance), deficit (SV function), and handicap (quality of life).

Identifiants

pubmed: 32147955
doi: 10.1002/ehf2.12630
pmc: PMC7160497
doi:

Substances chimiques

Phosphodiesterase 5 Inhibitors 0

Banques de données

ClinicalTrials.gov
['NCT03997097']

Types de publication

Journal Article Multicenter Study Randomized Controlled Trial Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

747-756

Subventions

Organisme : French Department of Health
ID : DGOS-PHRC-N-2017
Pays : International

Informations de copyright

© 2020 The Authors. ESC Heart Failure published by John Wiley & Sons Ltd on behalf of European Society of Cardiology.

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Auteurs

Pascal Amedro (P)

Paediatric and Congenital Cardiology Department, M3C Regional Reference CHD Centre, CHU Montpellier, Montpellier, France.
PhyMedExp, CNRS, INSERM, University of Montpellier, CHU Montpellier, Montpellier, France.

Arthur Gavotto (A)

Paediatric and Congenital Cardiology Department, M3C Regional Reference CHD Centre, CHU Montpellier, Montpellier, France.

Hamouda Abassi (H)

Paediatric and Congenital Cardiology Department, M3C Regional Reference CHD Centre, CHU Montpellier, Montpellier, France.

Marie-Christine Picot (MC)

Department of Epidemiology and Biostatistics, CHU Montpellier, Montpellier, France.

Stefan Matecki (S)

Paediatric and Congenital Cardiology Department, M3C Regional Reference CHD Centre, CHU Montpellier, Montpellier, France.
PhyMedExp, CNRS, INSERM, University of Montpellier, CHU Montpellier, Montpellier, France.

Sophie Malekzadeh-Milani (S)

Paediatric Cardiology Department, AP-HP, Necker-Enfants malades, M3C National Reference Centre, Paris Descartes University, Sorbonne Paris Cite, Paris, France.

Marilyne Levy (M)

Paediatric Cardiology Department, AP-HP, Necker-Enfants malades, M3C National Reference Centre, Paris Descartes University, Sorbonne Paris Cite, Paris, France.

Magalie Ladouceur (M)

Adult Congenital Heart Disease Unit, Department of Cardiology, M3C National Reference Centre, European Hospital Georges Pompidou, Paris, France.

Caroline Ovaert (C)

Paediatric and Congenital Medico-Surgical Cardiology Department, M3C Regional Reference Centre, AP-HM, La Timone University Hospital, Marseille, France.
Laboratory of Medical Genetics, INSERM UMR 1251, Aix-Marseille University, Marseille, France.

Philippe Aldebert (P)

Paediatric and Congenital Medico-Surgical Cardiology Department, M3C Regional Reference Centre, AP-HM, La Timone University Hospital, Marseille, France.

Jean-Benoit Thambo (JB)

Paediatric and Adult Congenital Heart Disease Department, Hôpital Cardiologique du Haut-Lévêque, M3C National Reference Centre, CHU de Bordeaux, Bordeaux, France.

Alain Fraisse (A)

Pediatric Cardiology Service, Royal Brompton and Harefield Hospital Trust, London, UK.

Marc Humbert (M)

Department of Pulmonology, PH National Reference Centre, APHP, Kremlin-Bicetre, Paris, France.
Paris-Sud Faculty of Medicine, INSERM U999, Marie-Lannelongue Hospital, M3C National Reference Centre, Paris-Sud University, Paris-Saclay, Le Plessis-Robinson, Paris, France.

Sarah Cohen (S)

Paris-Sud Faculty of Medicine, INSERM U999, Marie-Lannelongue Hospital, M3C National Reference Centre, Paris-Sud University, Paris-Saclay, Le Plessis-Robinson, Paris, France.

Alban-Elouen Baruteau (AE)

Paediatric and Congenital Cardiology Department, M3C Regional Reference CHD Centre, CHU Nantes, Nantes, France.

Clement Karsenty (C)

Paediatric and Congenital Cardiology Department, M3C Regional Reference CHD Centre, CHU Toulouse, Toulouse, France.

Damien Bonnet (D)

Paediatric Cardiology Department, AP-HP, Necker-Enfants malades, M3C National Reference Centre, Paris Descartes University, Sorbonne Paris Cite, Paris, France.

Sebastien Hascoet (S)

Paris-Sud Faculty of Medicine, INSERM U999, Marie-Lannelongue Hospital, M3C National Reference Centre, Paris-Sud University, Paris-Saclay, Le Plessis-Robinson, Paris, France.

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