Ferrous sulfate oral solution in young children with iron deficiency anemia: An open-label trial of efficacy, safety, and acceptability.


Journal

Pediatrics international : official journal of the Japan Pediatric Society
ISSN: 1442-200X
Titre abrégé: Pediatr Int
Pays: Australia
ID NLM: 100886002

Informations de publication

Date de publication:
Jul 2020
Historique:
received: 07 08 2019
revised: 03 03 2020
accepted: 16 03 2020
pubmed: 20 3 2020
medline: 17 3 2021
entrez: 20 3 2020
Statut: ppublish

Résumé

This study evaluated the efficacy, safety, and acceptability of a new ferrous sulfate oral solution (Tardyferon® 20 mg/mL) in young children with mild or moderate iron deficiency anemia (IDA). This was a multicenter, national, single-arm, open-label study. Children aged 6-53 months presenting with mild or moderate IDA (i.e., blood hemoglobin (Hb) ranging from 7.0 to 10.9 g/dL and serum ferritin <12 ng/mL) were eligible for inclusion. The ferrous sulfate heptahydrate solution (2 mg/kg/day) was administered orally for 3 months. If normalization of either Hb or ferritin was not achieved at month 3 the treatment was continued for another 3 months. Of the 100 children screened, 21 aged 6-17 months were included and received the study treatment, and 19 were analyzed for hematologic outcomes at month 3. Only one patient continued treatment for the additional 3 months. At month 3, mean ± SD Hb and ferritin levels were 12.0 ± 0.7 g/dL and 31.5 ± 19.4 ng/mL, respectively. Hemoglobin and ferritin levels were normalized in 95% (18/19) and 84% (16/19) of the patients, respectively. Treatment compliance and levels of satisfaction of both the parents and the investigators were high. Overall, 33.3% of patients (7/21) experienced at least one adverse event. Only one patient (4.8%) experienced a drug-related adverse event (upper abdominal pain). A 2 mg/kg daily dose of the new oral ferrous sulfate heptahydrate solution provides substantial therapeutic benefit with high levels of tolerability in young children who have mild or moderate IDA.

Sections du résumé

BACKGROUND BACKGROUND
This study evaluated the efficacy, safety, and acceptability of a new ferrous sulfate oral solution (Tardyferon® 20 mg/mL) in young children with mild or moderate iron deficiency anemia (IDA).
METHODS METHODS
This was a multicenter, national, single-arm, open-label study. Children aged 6-53 months presenting with mild or moderate IDA (i.e., blood hemoglobin (Hb) ranging from 7.0 to 10.9 g/dL and serum ferritin <12 ng/mL) were eligible for inclusion. The ferrous sulfate heptahydrate solution (2 mg/kg/day) was administered orally for 3 months. If normalization of either Hb or ferritin was not achieved at month 3 the treatment was continued for another 3 months.
RESULTS RESULTS
Of the 100 children screened, 21 aged 6-17 months were included and received the study treatment, and 19 were analyzed for hematologic outcomes at month 3. Only one patient continued treatment for the additional 3 months. At month 3, mean ± SD Hb and ferritin levels were 12.0 ± 0.7 g/dL and 31.5 ± 19.4 ng/mL, respectively. Hemoglobin and ferritin levels were normalized in 95% (18/19) and 84% (16/19) of the patients, respectively. Treatment compliance and levels of satisfaction of both the parents and the investigators were high. Overall, 33.3% of patients (7/21) experienced at least one adverse event. Only one patient (4.8%) experienced a drug-related adverse event (upper abdominal pain).
CONCLUSIONS CONCLUSIONS
A 2 mg/kg daily dose of the new oral ferrous sulfate heptahydrate solution provides substantial therapeutic benefit with high levels of tolerability in young children who have mild or moderate IDA.

Identifiants

pubmed: 32191814
doi: 10.1111/ped.14237
pmc: PMC7496601
doi:

Substances chimiques

Drug Combinations 0
Ferrous Compounds 0
Hemoglobins 0
Mucins 0
ferrous sulfate, mucin drug combination 75285-30-2
Ferritins 9007-73-2

Types de publication

Clinical Trial, Phase III Journal Article Multicenter Study

Langues

eng

Sous-ensembles de citation

IM

Pagination

820-827

Subventions

Organisme : Pierre Fabre Médicament

Informations de copyright

© 2020 The Authors. Pediatrics International published by John Wiley & Sons Australia, Ltd on behalf of Japan Pediatric Society.

Références

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pubmed: 17542112
Pediatrics. 2001 Sep;108(3):613-6
pubmed: 11533326
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pubmed: 8237843
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pubmed: 22392603
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pubmed: 19274317
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pubmed: 21643774
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pubmed: 28090490
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pubmed: 15473523
J Pediatr Gastroenterol Nutr. 2007 Apr;44(4):468-86
pubmed: 17414146

Auteurs

Lidia Pachuta Węgier (L)

Lidia Pachuta Węgier Medical Services, Lublin, Poland.

Maciej Kubiak (M)

Tolek Clinic for Children, Lesznowola, Poland.

Agata Liebert (A)

Tolek Clinic for Children, Lesznowola, Poland.

Thierry Clavel (T)

TCC Consulting, Revel, France.

Agnès Montagne (A)

Clinical Development Department, Institut de Recherche Pierre Fabre, CRDPF, Toulouse, France.

Aline Stennevin (A)

Clinical Development Department, Institut de Recherche Pierre Fabre, CRDPF, Toulouse, France.

Sandrine Roye (S)

Clinical Development Department, Institut de Recherche Pierre Fabre, CRDPF, Toulouse, France.

Asmaa Boudribila (A)

Clinical Development Department, Institut de Recherche Pierre Fabre, CRDPF, Toulouse, France.

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Classifications MeSH