De novo duplication on Chromosome 19 observed in nuclear family displaying neurodevelopmental disorders.


Journal

Cold Spring Harbor molecular case studies
ISSN: 2373-2873
Titre abrégé: Cold Spring Harb Mol Case Stud
Pays: United States
ID NLM: 101660017

Informations de publication

Date de publication:
06 2020
Historique:
received: 19 08 2019
accepted: 06 04 2020
pubmed: 24 4 2020
medline: 29 5 2021
entrez: 24 4 2020
Statut: epublish

Résumé

Pleiotropy and variable expressivity have been cited to explain the seemingly distinct neurodevelopmental disorders due to a common genetic etiology within the same family. Here we present a family with a de novo 1-Mb duplication involving 18 genes on Chromosome 19. Within the family there are multiple cases of neurodevelopmental disorders including autism spectrum disorder, attention deficit/hyperactivity disorder, intellectual disability, and psychiatric disease in individuals carrying this copy-number variant (CNV). Quantitative polymerase chain reaction (PCR) confirmed the CNV was de novo in the mother and inherited by both sons. Whole-exome sequencing did not uncover further genetic risk factors segregating within the family. Transcriptome analysis of peripheral blood demonstrated a ∼1.5-fold increase in RNA transcript abundance in 12 of the 15 detected genes within the CNV region for individuals carrying the CNV compared with their noncarrier relatives. Examination of transcript abundance across the rest of the transcriptome identified 407 differentially expressed genes (

Identifiants

pubmed: 32321736
pii: mcs.a004721
doi: 10.1101/mcs.a004721
pmc: PMC7304355
pii:
doi:

Substances chimiques

RNA, Messenger 0

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Informations de copyright

© 2020 Sjaarda et al.; Published by Cold Spring Harbor Laboratory Press.

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Auteurs

Calvin P Sjaarda (CP)

Queen's Genomics Laboratory at Ongwanada (QGLO), Ongwanada Resource Center, Kingston, Ontario K7M 8A6, Canada.
Department of Psychiatry, Queen's University, Kingston, Ontario K7L 3N6, Canada.

Beatrice Kaiser (B)

Queen's Genomics Laboratory at Ongwanada (QGLO), Ongwanada Resource Center, Kingston, Ontario K7M 8A6, Canada.
Department of Psychiatry, Queen's University, Kingston, Ontario K7L 3N6, Canada.

Amy J M McNaughton (AJM)

Queen's Genomics Laboratory at Ongwanada (QGLO), Ongwanada Resource Center, Kingston, Ontario K7M 8A6, Canada.
Department of Psychiatry, Queen's University, Kingston, Ontario K7L 3N6, Canada.

Melissa L Hudson (ML)

Queen's Genomics Laboratory at Ongwanada (QGLO), Ongwanada Resource Center, Kingston, Ontario K7M 8A6, Canada.
Department of Psychiatry, Queen's University, Kingston, Ontario K7L 3N6, Canada.

Liam Harris-Lowe (L)

Queen's Genomics Laboratory at Ongwanada (QGLO), Ongwanada Resource Center, Kingston, Ontario K7M 8A6, Canada.
School of Applied Science and Computing, St. Lawrence College, Kingston, Ontario K7L 5A6, Canada.

Kyle Lou (K)

Queen's Genomics Laboratory at Ongwanada (QGLO), Ongwanada Resource Center, Kingston, Ontario K7M 8A6, Canada.
Department of Psychiatry, Queen's University, Kingston, Ontario K7L 3N6, Canada.

Andrea Guerin (A)

Division of Medical Genetics, Department of Pediatrics, Queen's University, Kingston, Ontario K7L 3N6, Canada.

Muhammad Ayub (M)

Department of Psychiatry, Queen's University, Kingston, Ontario K7L 3N6, Canada.

Xudong Liu (X)

Queen's Genomics Laboratory at Ongwanada (QGLO), Ongwanada Resource Center, Kingston, Ontario K7M 8A6, Canada.
Department of Psychiatry, Queen's University, Kingston, Ontario K7L 3N6, Canada.

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