Phase I Study of TAK-659, an Investigational, Dual SYK/FLT3 Inhibitor, in Patients with B-Cell Lymphoma.


Journal

Clinical cancer research : an official journal of the American Association for Cancer Research
ISSN: 1557-3265
Titre abrégé: Clin Cancer Res
Pays: United States
ID NLM: 9502500

Informations de publication

Date de publication:
15 07 2020
Historique:
received: 22 10 2019
revised: 11 03 2020
accepted: 17 04 2020
pubmed: 25 4 2020
medline: 3 11 2021
entrez: 25 4 2020
Statut: ppublish

Résumé

TAK-659 is an investigational, dual SYK/FLT3 inhibitor with preclinical activity in B-cell malignancy models. This first-in-human, dose-escalation/expansion study aimed to determine the safety, tolerability, MTD/recommended phase II dose (RP2D), and preliminary efficacy of TAK-659 in relapsed/refractory solid tumors and B-cell lymphomas. Patients received continuous, once-daily oral TAK-659, 60-120 mg in 28-day cycles, until disease progression or unacceptable toxicity. The study applied an accelerated dose-escalation design to determine the MTD and RP2D. In the expansion phase, patients with lymphoma were enrolled in five disease cohorts at the MTD. Overall, 105 patients were enrolled [dose escalation, TAK-659 has single-agent activity in patients with B-cell lymphoma. Further studies of the drug in combination, including an evaluation of the biologically optimal and safest long-term dose and schedule, are warranted.

Identifiants

pubmed: 32327472
pii: 1078-0432.CCR-19-3239
doi: 10.1158/1078-0432.CCR-19-3239
doi:

Substances chimiques

Drugs, Investigational 0
Protein Kinase Inhibitors 0
Pyrimidines 0
Pyrrolidinones 0
TAK-659 0
FLT3 protein, human EC 2.7.10.1
fms-Like Tyrosine Kinase 3 EC 2.7.10.1
SYK protein, human EC 2.7.10.2
Syk Kinase EC 2.7.10.2

Banques de données

ClinicalTrials.gov
['NCT02000934']

Types de publication

Clinical Trial, Phase I Journal Article Multicenter Study Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

3546-3556

Informations de copyright

©2020 American Association for Cancer Research.

Auteurs

Leo I Gordon (LI)

Northwestern University Feinberg School of Medicine and the Robert H. Lurie Comprehensive Cancer Center, Chicago, Illinois. l-gordon@northwestern.edu.

Jason B Kaplan (JB)

Northwestern University Feinberg School of Medicine and the Robert H. Lurie Comprehensive Cancer Center, Chicago, Illinois.

Rakesh Popat (R)

NIHR/UCLH Clinical Research Facility, University College London Hospitals NHS Foundation Trust, London, United Kingdom.

Howard A Burris (HA)

Sarah Cannon Research Institute/Tennessee Oncology, Nashville, Tennessee.

Silvia Ferrari (S)

Ospedale Papa Giovanni XXIII, Bergamo, Italy.

Sumit Madan (S)

Cancer Therapy and Research Center at University of Texas Health Science Center, San Antonio, Texas.

Manish R Patel (MR)

Florida Cancer Specialists/Sarah Cannon Research Institute, Sarasota, Florida.

Giuseppe Gritti (G)

Ospedale Papa Giovanni XXIII, Bergamo, Italy.

Dima El-Sharkawi (D)

NIHR/UCLH Clinical Research Facility, University College London Hospitals NHS Foundation Trust, London, United Kingdom.

Ian Chau (I)

Royal Marsden Hospital, Sutton, Surrey, United Kingdom.

John A Radford (JA)

The University of Manchester and the Christie NHS Foundation Trust, Manchester Academic Health Science Centre, Manchester, United Kingdom.

Jaime Pérez de Oteyza (J)

Hospital Universitario Madrid Sanchinarro, Universidad CEU San Pablo, Madrid, Spain.

Pier Luigi Zinzani (PL)

Institute of Hematology "Seragnoli," University of Bologna, Bologna, Italy.

Swaminathan Iyer (S)

Houston Methodist Cancer Center, Houston, Texas.

William Townsend (W)

NIHR/UCLH Clinical Research Facility, University College London Hospitals NHS Foundation Trust, London, United Kingdom.

Reem Karmali (R)

Northwestern University Feinberg School of Medicine and the Robert H. Lurie Comprehensive Cancer Center, Chicago, Illinois.

Harry Miao (H)

Millennium Pharmaceuticals, Inc., Cambridge, Massachusetts, a wholly owned subsidiary of Takeda Pharmaceutical Company Limited.

Igor Proscurshim (I)

Millennium Pharmaceuticals, Inc., Cambridge, Massachusetts, a wholly owned subsidiary of Takeda Pharmaceutical Company Limited.

Shining Wang (S)

Millennium Pharmaceuticals, Inc., Cambridge, Massachusetts, a wholly owned subsidiary of Takeda Pharmaceutical Company Limited.

Yujun Wu (Y)

Millennium Pharmaceuticals, Inc., Cambridge, Massachusetts, a wholly owned subsidiary of Takeda Pharmaceutical Company Limited.

Kate Stumpo (K)

Millennium Pharmaceuticals, Inc., Cambridge, Massachusetts, a wholly owned subsidiary of Takeda Pharmaceutical Company Limited.

Yaping Shou (Y)

Millennium Pharmaceuticals, Inc., Cambridge, Massachusetts, a wholly owned subsidiary of Takeda Pharmaceutical Company Limited.

Cecilia Carpio (C)

University Hospital Vall d'Hebron, Barcelona, Spain.

Francesc Bosch (F)

University Hospital Vall d'Hebron, Barcelona, Spain.

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Classifications MeSH