Chemically Programmable and Switchable CAR-T Therapy.


Journal

Angewandte Chemie (International ed. in English)
ISSN: 1521-3773
Titre abrégé: Angew Chem Int Ed Engl
Pays: Germany
ID NLM: 0370543

Informations de publication

Date de publication:
13 07 2020
Historique:
received: 14 04 2020
pubmed: 25 4 2020
medline: 26 3 2021
entrez: 25 4 2020
Statut: ppublish

Résumé

Although macromolecules on cell surfaces are predominantly targeted and drugged with antibodies, they harbor pockets that are only accessible to small molecules and constitutes a rich subset of binding sites with immense potential diagnostic and therapeutic utility. Compared to antibodies, however, small molecules are disadvantaged by a less confined biodistribution, shorter circulatory half-life, and inability to communicate with the immune system. Presented herein is a method that endows small molecules with the ability to recruit and activate chimeric antigen receptor T cells (CAR-Ts). It is based on a CAR-T platform that uses a chemically programmed antibody fragment (cp-Fab) as on/off switch. In proof-of-concept studies, this cp-Fab/CAR-T system targeting folate binding proteins on the cell surface mediated potent and specific eradication of folate-receptor-expressing cancer cells in vitro and in vivo.

Identifiants

pubmed: 32329959
doi: 10.1002/anie.202005432
pmc: PMC7429910
mid: NIHMS1617513
doi:

Substances chimiques

Antigens, Neoplasm 0
Folate Receptor 2 0
Receptors, Antigen, T-Cell 0
Receptors, Cell Surface 0
Receptors, Chimeric Antigen 0

Types de publication

Journal Article Research Support, N.I.H., Extramural Research Support, N.I.H., Intramural

Langues

eng

Sous-ensembles de citation

IM

Pagination

12178-12185

Subventions

Organisme : NCI NIH HHS
ID : R01 CA204484
Pays : United States
Organisme : NCI NIH HHS
ID : R01 CA174844
Pays : United States
Organisme : NIH HHS
ID : Intramural Research Program
Pays : United States
Organisme : NCI NIH HHS
ID : R01 CA181258
Pays : United States

Informations de copyright

© 2020 Wiley-VCH Verlag GmbH & Co. KGaA, Weinheim.

Références

Cancer Res. 2011 Jul 1;71(13):4617-27
pubmed: 21546571
J Biol Chem. 2016 Sep 9;291(37):19661-73
pubmed: 27445334
Science. 2018 Mar 23;359(6382):1361-1365
pubmed: 29567707
Proc Natl Acad Sci U S A. 1998 Dec 22;95(26):15351-5
pubmed: 9860972
J Med Chem. 2010 Oct 14;53(19):6811-24
pubmed: 20666486
Nat Rev Drug Discov. 2018 May;17(5):333-352
pubmed: 29651105
MAbs. 2019 May/Jun;11(4):621-631
pubmed: 30892136
Drug Discov Today. 2019 Nov;24(11):2111-2115
pubmed: 31278990
PLoS One. 2015 Apr 20;10(3):e0121314
pubmed: 25894527
Blood. 2011 Aug 4;118(5):1255-63
pubmed: 21653320
Nature. 2015 Feb 5;518(7537):38-9
pubmed: 25652990
Proc Natl Acad Sci U S A. 2018 Nov 13;115(46):E10988-E10997
pubmed: 30373828
Nat Rev Drug Discov. 2019 Sep;18(10):733-736
pubmed: 31570852
J Biol Chem. 2004 Apr 30;279(18):18870-7
pubmed: 14754898
J Mol Biol. 2003 Sep 26;332(4):889-99
pubmed: 12972259
Proc Natl Acad Sci U S A. 2003 Apr 29;100(9):5396-400
pubmed: 12702756
Clin Cancer Res. 2019 Mar 15;25(6):1702-1708
pubmed: 30413526
Bioconjug Chem. 2019 Nov 20;30(11):2889-2896
pubmed: 31675216
J Pharmacol Exp Ther. 2008 Dec;327(3):918-25
pubmed: 18791065
J Biol Chem. 2012 Aug 17;287(34):28206-14
pubmed: 22761439
Angew Chem Int Ed Engl. 2016 Jun 20;55(26):7520-4
pubmed: 27145250
Blood. 2018 Aug 23;132(8):777-781
pubmed: 29914976
Proc Natl Acad Sci U S A. 1989 Dec;86(24):10024-8
pubmed: 2513569
J Am Chem Soc. 2015 Mar 4;137(8):2832-5
pubmed: 25692571
Science. 1997 Dec 19;278(5346):2085-92
pubmed: 9405338
Cancer Discov. 2018 Aug;8(8):924-934
pubmed: 30012854
Proc Natl Acad Sci U S A. 2018 Nov 13;115(46):E10898-E10906
pubmed: 30373813
Cancer Immunol Res. 2015 Feb;3(2):125-35
pubmed: 25212991
Nat Commun. 2019 Jun 18;10(1):2681
pubmed: 31213606
Nat Rev Drug Discov. 2017 Feb;16(2):131-147
pubmed: 27932801
Oncotarget. 2016 May 31;7(22):32144-55
pubmed: 27014973
Proc Natl Acad Sci U S A. 2016 Jan 26;113(4):E450-8
pubmed: 26759368
Chem Sci. 2017 Dec 18;9(4):790-810
pubmed: 29675145
Proc Natl Acad Sci U S A. 2016 Jan 26;113(4):E459-68
pubmed: 26759369
Trends Biotechnol. 2014 Apr;32(4):186-97
pubmed: 24630478
Bioorg Med Chem Lett. 2009 Mar 1;19(5):1421-4
pubmed: 19181522
Cell. 2017 Jan 26;168(3):527-541.e29
pubmed: 28111073
Nature. 2017 May 24;545(7655):423-431
pubmed: 28541315
Clin Cancer Res. 2019 Feb 15;25(4):1142-1146
pubmed: 30309857
Front Immunol. 2019 Aug 21;10:1994
pubmed: 31497024
Cancer Res. 2019 Jan 15;79(2):387-396
pubmed: 30482775
Hum Gene Ther. 2018 May;29(5):559-568
pubmed: 29620951
Cancer Cell. 2017 Mar 13;31(3):311-325
pubmed: 28292435

Auteurs

Junpeng Qi (J)

Department of Immunology and Microbiology, The Scripps Research Institute, 130 Scripps Way, Jupiter, FL, 33458, USA.

Kohei Tsuji (K)

Chemical Biology Laboratory, Center for Cancer Research, National Cancer Institute, National Institutes of Health, Building 376 Boyles Street, Frederick, MD, 21702, USA.
Department of Medicinal Chemistry, Institute of Biomaterials and Bioengineering, Tokyo Medical and Dental University, 2-3-10 Kandasurugadai, Chiyoda-ku, Tokyo, 101-0062, Japan.

David Hymel (D)

Chemical Biology Laboratory, Center for Cancer Research, National Cancer Institute, National Institutes of Health, Building 376 Boyles Street, Frederick, MD, 21702, USA.

Terrence R Burke (TR)

Chemical Biology Laboratory, Center for Cancer Research, National Cancer Institute, National Institutes of Health, Building 376 Boyles Street, Frederick, MD, 21702, USA.

Michael Hudecek (M)

Medizinische Klinik und Poliklinik II, Universitätsklinikum Würzburg, Oberdürrbacherstrasse 6, 97080, Würzburg, Germany.

Christoph Rader (C)

Department of Immunology and Microbiology, The Scripps Research Institute, 130 Scripps Way, Jupiter, FL, 33458, USA.

Haiyong Peng (H)

Department of Immunology and Microbiology, The Scripps Research Institute, 130 Scripps Way, Jupiter, FL, 33458, USA.

Articles similaires

[Redispensing of expensive oral anticancer medicines: a practical application].

Lisanne N van Merendonk, Kübra Akgöl, Bastiaan Nuijen
1.00
Humans Antineoplastic Agents Administration, Oral Drug Costs Counterfeit Drugs

Smoking Cessation and Incident Cardiovascular Disease.

Jun Hwan Cho, Seung Yong Shin, Hoseob Kim et al.
1.00
Humans Male Smoking Cessation Cardiovascular Diseases Female
Humans United States Aged Cross-Sectional Studies Medicare Part C
1.00
Humans Yoga Low Back Pain Female Male

Classifications MeSH