From Dysgammaglobulinemia to Autosomal-Dominant Activation-Induced Cytidine Deaminase Deficiency: Unraveling an Inherited Immunodeficiency after 50 Years.


Journal

The Journal of pediatrics
ISSN: 1097-6833
Titre abrégé: J Pediatr
Pays: United States
ID NLM: 0375410

Informations de publication

Date de publication:
08 2020
Historique:
received: 26 11 2019
revised: 17 02 2020
accepted: 12 03 2020
pubmed: 20 5 2020
medline: 2 12 2020
entrez: 20 5 2020
Statut: ppublish

Résumé

The genetic investigation of a family presenting with a dominant form of hyper IgM syndrome published in 1963 and 1975 revealed a R190X nonsense mutation in activation-induced cytidine deaminase. This report illustrates the progress made over 6 decades in the characterization of primary immunodeficiencies, from immunochemistry to whole-exome sequencing.

Identifiants

pubmed: 32423680
pii: S0022-3476(20)30353-X
doi: 10.1016/j.jpeds.2020.03.024
pii:
doi:

Substances chimiques

Cytidine Deaminase EC 3.5.4.5

Types de publication

Case Reports Research Support, N.I.H., Extramural Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

207-211.e1

Subventions

Organisme : NIAID NIH HHS
ID : P01 AI061093
Pays : United States

Informations de copyright

Copyright © 2020 Elsevier Inc. All rights reserved.

Auteurs

Jehane Fadlallah (J)

Department of Clinical Immunology, Saint-Louis Hospital, Assistance Publique-Hôpitaux de Paris, and Paris Diderot University, Paris, France. Electronic address: jehane.fadlallah@aphp.fr.

Loic Chentout (L)

Human Lymphohematopoiesis Laboratory, Institut Imagine, Inserm U1163, Paris Descartes Sorbonne, Paris Cite University, Paris, France.

Bertrand Boisson (B)

Laboratory of Human Genetics of Infectious Diseases, Necker Branch, Inserm U1163, Paris, France; St. Giles Laboratory of Human Genetics of Infectious Diseases, The Rockefeller University, New York, NY.

Aurore Pouliet (A)

Genomics Core Facility, Institut Imagine, Inserm U1163, Paris Descartes Sorbonne, Paris Cite University, Paris, France.

Cecile Masson (C)

Bioinformatics Facility, Institut Imagine, Inserm U1163, Paris Descartes Sorbonne, Paris Cite University, Paris, France.

Florence Morin (F)

Immunology and Histocompatibility Laboratory, Saint-Louis Hospital, Assistance Publique-Hôpitaux de Paris, Paris, France.

Anne Durandy (A)

Human Lymphohematopoiesis Laboratory, Institut Imagine, Inserm U1163, Paris Descartes Sorbonne, Paris Cite University, Paris, France.

Jean-Laurent Casanova (JL)

Laboratory of Human Genetics of Infectious Diseases, Necker Branch, Inserm U1163, Paris, France; St. Giles Laboratory of Human Genetics of Infectious Diseases, The Rockefeller University, New York, NY; Howard Hughes Medical Institute, New York, NY; Rockefeller University and Rockefeller University Hospital, New York, NY; Pediatric Immunology and Hematology Unit, Necker Hospital for Sick Children, Assistance Publique-Hôpitaux de Paris, Paris, France.

Eric Oksenhendler (E)

Department of Clinical Immunology, Saint-Louis Hospital, Assistance Publique-Hôpitaux de Paris, and Paris Diderot University, Paris, France.

Sven Kracker (S)

Human Lymphohematopoiesis Laboratory, Institut Imagine, Inserm U1163, Paris Descartes Sorbonne, Paris Cite University, Paris, France.

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Classifications MeSH