New Horizons: Novel Adrenal Regenerative Therapies.


Journal

The Journal of clinical endocrinology and metabolism
ISSN: 1945-7197
Titre abrégé: J Clin Endocrinol Metab
Pays: United States
ID NLM: 0375362

Informations de publication

Date de publication:
01 09 2020
Historique:
received: 27 05 2020
accepted: 02 07 2020
pubmed: 7 7 2020
medline: 24 2 2021
entrez: 7 7 2020
Statut: ppublish

Résumé

Adrenal insufficiency requires lifelong corticoid replacement therapies. However, current therapies are not able to replace the physiological circadian pattern of the adrenal cortex and are associated with many metabolic, vascular, neuroendocrine, and mental perturbations. Therefore, regenerative and more curative strategies would be desirable. In the current perspective, we describe emerging new regenerative therapies for the treatment of adrenal insufficiency. In particular, we discuss gene therapy and cell replacement strategies. Furthermore, we discuss how adrenal cells might be used as a source for regenerative therapies of nonadrenal neurodegenerative diseases such as Parkinson disease.

Identifiants

pubmed: 32629476
pii: 5868096
doi: 10.1210/clinem/dgaa438
pmc: PMC7398608
pii:
doi:

Substances chimiques

Glucocorticoids 0

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Informations de copyright

© Endocrine Society 2020.

Références

J Clin Endocrinol Metab. 2020 Apr 1;105(4):
pubmed: 31863094
World J Transplant. 2017 Jun 24;7(3):179-192
pubmed: 28698835
F1000Res. 2019 Apr 2;8:363
pubmed: 30984389
Proc Natl Acad Sci U S A. 2015 Feb 24;112(8):2527-32
pubmed: 25675525
Cell Stem Cell. 2019 Aug 1;25(2):290-296.e2
pubmed: 31104943
Front Endocrinol (Lausanne). 2015 May 06;6:70
pubmed: 25999916
Proc Natl Acad Sci U S A. 2018 Dec 18;115(51):12997-13002
pubmed: 30514817
Hum Gene Ther. 2018 Apr;29(4):403-412
pubmed: 29316814

Auteurs

Stefan R Bornstein (SR)

Department of Internal Medicine III, University Hospital Carl Gustav Carus, Technische Universität Dresden, Dresden, Germany.
Diabetes and Nutritional Sciences Division, King's College London, London, UK.

Maria Malyukov (M)

Department of Internal Medicine III, University Hospital Carl Gustav Carus, Technische Universität Dresden, Dresden, Germany.

Carolin Heller (C)

Department of Internal Medicine III, University Hospital Carl Gustav Carus, Technische Universität Dresden, Dresden, Germany.
Paul Langerhans Institute Dresden (PLID) of the Helmholtz Center Munich, University Hospital Carl Gustav Carus, Technische Universität Dresden, Dresden, Germany.
DFG-Center for Regenerative Therapies Dresden, Technische Universität Dresden, Dresden, Germany.

Christian G Ziegler (CG)

Department of Internal Medicine III, University Hospital Carl Gustav Carus, Technische Universität Dresden, Dresden, Germany.

Gerard Ruiz-Babot (G)

Department of Internal Medicine III, University Hospital Carl Gustav Carus, Technische Universität Dresden, Dresden, Germany.
Division of Endocrinology, Boston Children's Hospital, Boston, Massachusetts, USA.
Department of Pediatrics, Harvard Medical School, Boston, Massachusetts, USA.

Andreas Schedl (A)

Université Côte d'Azur, INSERM, CNRS, iBV, Nice, France.

Barbara Ludwig (B)

Department of Internal Medicine III, University Hospital Carl Gustav Carus, Technische Universität Dresden, Dresden, Germany.
Paul Langerhans Institute Dresden (PLID) of the Helmholtz Center Munich, University Hospital Carl Gustav Carus, Technische Universität Dresden, Dresden, Germany.
DFG-Center for Regenerative Therapies Dresden, Technische Universität Dresden, Dresden, Germany.
Department of Endocrinology and Diabetology, University Hospital Zurich, Zurich, Switzerland.

Charlotte Steenblock (C)

Department of Internal Medicine III, University Hospital Carl Gustav Carus, Technische Universität Dresden, Dresden, Germany.

Articles similaires

[Redispensing of expensive oral anticancer medicines: a practical application].

Lisanne N van Merendonk, Kübra Akgöl, Bastiaan Nuijen
1.00
Humans Antineoplastic Agents Administration, Oral Drug Costs Counterfeit Drugs

Smoking Cessation and Incident Cardiovascular Disease.

Jun Hwan Cho, Seung Yong Shin, Hoseob Kim et al.
1.00
Humans Male Smoking Cessation Cardiovascular Diseases Female
Humans United States Aged Cross-Sectional Studies Medicare Part C
1.00
Humans Yoga Low Back Pain Female Male

Classifications MeSH