Conducting clinical trials in sub-Saharan Africa: challenges and lessons learned from the Malawi Cryptosporidium study.


Journal

Trials
ISSN: 1745-6215
Titre abrégé: Trials
Pays: England
ID NLM: 101263253

Informations de publication

Date de publication:
25 Jul 2020
Historique:
received: 05 03 2020
accepted: 16 07 2020
entrez: 27 7 2020
pubmed: 28 7 2020
medline: 15 5 2021
Statut: epublish

Résumé

An effective drug to treat cryptosporidial diarrhea in HIV-infected individuals is a global health priority. Promising drugs need to be evaluated in endemic areas which may be challenged by both lack of resources and experience to conduct International Committee of Harmonisation-Good Clinical Practice (ICH-GCP)-compliant clinical trials. We present the challenges and lessons learned in implementing a phase 2A, randomized, double-blind, placebo-controlled trial of clofazimine, in treatment of cryptosporidiosis among HIV-infected adults at a single site in Malawi. Primary challenges are grouped under study initiation, study population, study implementation, and cultural issues. The lessons learned primarily deal with regulatory system and operational barriers, and recommendations can be applied to other human experimental trials in low- and middle-income countries, specifically in sub-Saharan Africa. This study demonstrated that initiating and implementing human experimental trials in sub-Saharan Africa can be challenging. However, solutions exist and successful execution requires careful planning, ongoing evaluation, responsiveness to new developments, and oversight of all trial operations.

Sections du résumé

BACKGROUND BACKGROUND
An effective drug to treat cryptosporidial diarrhea in HIV-infected individuals is a global health priority. Promising drugs need to be evaluated in endemic areas which may be challenged by both lack of resources and experience to conduct International Committee of Harmonisation-Good Clinical Practice (ICH-GCP)-compliant clinical trials.
METHODS METHODS
We present the challenges and lessons learned in implementing a phase 2A, randomized, double-blind, placebo-controlled trial of clofazimine, in treatment of cryptosporidiosis among HIV-infected adults at a single site in Malawi.
RESULTS RESULTS
Primary challenges are grouped under study initiation, study population, study implementation, and cultural issues. The lessons learned primarily deal with regulatory system and operational barriers, and recommendations can be applied to other human experimental trials in low- and middle-income countries, specifically in sub-Saharan Africa.
CONCLUSION CONCLUSIONS
This study demonstrated that initiating and implementing human experimental trials in sub-Saharan Africa can be challenging. However, solutions exist and successful execution requires careful planning, ongoing evaluation, responsiveness to new developments, and oversight of all trial operations.

Identifiants

pubmed: 32711568
doi: 10.1186/s13063-020-04620-8
pii: 10.1186/s13063-020-04620-8
pmc: PMC7382797
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

680

Subventions

Organisme : Bill and Melinda Gates Foundation
ID : OPP1172544

Références

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pubmed: 28158186
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pubmed: 32277809
Lancet Glob Health. 2018 Jul;6(7):e758-e768
pubmed: 29903377
Int J Equity Health. 2018 Mar 22;17(1):37
pubmed: 29566721
BMJ Open. 2013 Nov 27;3(11):e003616
pubmed: 24285629
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pubmed: 28199646
Am J Trop Med Hyg. 2014 Aug;91(2):213-215
pubmed: 24821846
Trials. 2018 Aug 23;19(1):456
pubmed: 30139372

Auteurs

Neema Toto (N)

Malawi-Liverpool Wellcome Trust Clinical Research Programme, Blantyre, Malawi.
Liverpool School of Tropical Medicine, Liverpool, UK.

Elaine Douglas (E)

Center for Emerging and Re-emerging Infectious Diseases (CERID), University of Washington, Seattle, WA, USA.

Markus Gmeiner (M)

Malawi-Liverpool Wellcome Trust Clinical Research Programme, Blantyre, Malawi.
Liverpool School of Tropical Medicine, Liverpool, UK.

Lynn K Barrett (LK)

Center for Emerging and Re-emerging Infectious Diseases (CERID), University of Washington, Seattle, WA, USA.

Robert Lindblad (R)

Emmes, Rockville, MD, USA.

Lumbani Makhaza (L)

Malawi-Liverpool Wellcome Trust Clinical Research Programme, Blantyre, Malawi.

Wilfred Nedi (W)

Malawi-Liverpool Wellcome Trust Clinical Research Programme, Blantyre, Malawi.

Jacob Phulusa (J)

Malawi-Liverpool Wellcome Trust Clinical Research Programme, Blantyre, Malawi.

Gerald V Quinnan (GV)

Emmes, Rockville, MD, USA.

Leigh A Sawyer (LA)

Emmes, Rockville, MD, USA.

Herbert Thole (H)

Malawi-Liverpool Wellcome Trust Clinical Research Programme, Blantyre, Malawi.

Wesley C Van Voorhis (WC)

Center for Emerging and Re-emerging Infectious Diseases (CERID), University of Washington, Seattle, WA, USA.

Pui-Ying Iroh Tam (PY)

Malawi-Liverpool Wellcome Trust Clinical Research Programme, Blantyre, Malawi. irohtam@mlw.mw.
Liverpool School of Tropical Medicine, Liverpool, UK. irohtam@mlw.mw.

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