Leigh Syndrome in a Pedigree Harboring the m.1555A>G Mutation in the Mitochondrial 12S rRNA.


Journal

Genes
ISSN: 2073-4425
Titre abrégé: Genes (Basel)
Pays: Switzerland
ID NLM: 101551097

Informations de publication

Date de publication:
27 08 2020
Historique:
received: 09 07 2020
revised: 28 07 2020
accepted: 24 08 2020
entrez: 2 9 2020
pubmed: 2 9 2020
medline: 1 4 2021
Statut: epublish

Résumé

Leigh syndrome (LS) is a serious genetic disease that can be caused by mutations in dozens of different genes. Clinical study of a deafness pedigree in which some members developed LS. Cellular, biochemical and molecular genetic analyses of patients' tissues and cybrid cell lines were performed. mitochondrial DNA (mtDNA) m.1555A>G/ The m.1555A>G pathological mutation, accompanied with an unknown nuclear DNA (nDNA) factor, could be the cause of the phenotypic manifestations in this pedigree.

Sections du résumé

BACKGROUND
Leigh syndrome (LS) is a serious genetic disease that can be caused by mutations in dozens of different genes.
METHODS
Clinical study of a deafness pedigree in which some members developed LS. Cellular, biochemical and molecular genetic analyses of patients' tissues and cybrid cell lines were performed.
RESULTS
mitochondrial DNA (mtDNA) m.1555A>G/
CONCLUSION
The m.1555A>G pathological mutation, accompanied with an unknown nuclear DNA (nDNA) factor, could be the cause of the phenotypic manifestations in this pedigree.

Identifiants

pubmed: 32867169
pii: genes11091007
doi: 10.3390/genes11091007
pmc: PMC7565518
pii:
doi:

Substances chimiques

RNA, Mitochondrial 0
RNA, Ribosomal 0
RNA, ribosomal, 12S 0

Types de publication

Case Reports Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

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Auteurs

Mouna Habbane (M)

Departamento de Bioquímica, Biología Molecular y Celular, Universidad de Zaragoza, 50013 Zaragoza, Spain.
Laboratoire Biologie et Santé, Faculté des Sciences Ben M'Sik, Université Hassan II, 20670 Casablanca, Morocco.

Laura Llobet (L)

Departamento de Bioquímica, Biología Molecular y Celular, Universidad de Zaragoza, 50013 Zaragoza, Spain.

M Pilar Bayona-Bafaluy (MP)

Departamento de Bioquímica, Biología Molecular y Celular, Universidad de Zaragoza, 50013 Zaragoza, Spain.
Instituto de Investigación Sanitaria (IIS) de Aragón, 50009 Zaragoza, Spain.
Centro de Investigaciones Biomédicas en Red de Enfermedades Raras (CIBERER), 28029 Madrid, Spain.

José E Bárcena (JE)

Servicio de Neurología, Hospital Universitario Cruces, 48903 Baracaldo, Vizcaya, Spain.

Leticia Ceberio (L)

Servicio de Medicina Interna, Hospital Universitario Cruces, 48903 Baracaldo, Vizcaya, Spain.

Covadonga Gómez-Díaz (C)

Servicio de Otorrinolaringología, Hospital Universitario Miguel Servet, 50009 Zaragoza, Spain.

Laura Gort (L)

Centro de Investigaciones Biomédicas en Red de Enfermedades Raras (CIBERER), 28029 Madrid, Spain.
Errors Congènits del Metabolisme, Servicio de Bioquímica i Genètica Molecular, CDB, Hospital Clínic, IDIBAPS, 08036 Barcelona, Spain.

Rafael Artuch (R)

Centro de Investigaciones Biomédicas en Red de Enfermedades Raras (CIBERER), 28029 Madrid, Spain.
Servicio de Bioquímica Clínica, Institut de Recerca Sant Joan de Déu, 08950 Barcelona, Spain.

Julio Montoya (J)

Departamento de Bioquímica, Biología Molecular y Celular, Universidad de Zaragoza, 50013 Zaragoza, Spain.
Instituto de Investigación Sanitaria (IIS) de Aragón, 50009 Zaragoza, Spain.
Centro de Investigaciones Biomédicas en Red de Enfermedades Raras (CIBERER), 28029 Madrid, Spain.

Eduardo Ruiz-Pesini (E)

Departamento de Bioquímica, Biología Molecular y Celular, Universidad de Zaragoza, 50013 Zaragoza, Spain.
Instituto de Investigación Sanitaria (IIS) de Aragón, 50009 Zaragoza, Spain.
Centro de Investigaciones Biomédicas en Red de Enfermedades Raras (CIBERER), 28029 Madrid, Spain.
Fundación Araid, 50018 Zaragoza, Spain.

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Classifications MeSH