Characterization of Recessive Parkinson Disease in a Large Multicenter Study.


Journal

Annals of neurology
ISSN: 1531-8249
Titre abrégé: Ann Neurol
Pays: United States
ID NLM: 7707449

Informations de publication

Date de publication:
10 2020
Historique:
received: 15 10 2019
revised: 17 05 2020
accepted: 18 05 2020
entrez: 13 10 2020
pubmed: 14 10 2020
medline: 15 12 2020
Statut: ppublish

Résumé

Studies of the phenotype and population distribution of rare genetic forms of parkinsonism are required, now that gene-targeting approaches for Parkinson disease have reached the clinical trial stage. We evaluated the frequencies of PRKN, PINK1, and DJ-1 mutations in a cohort of 1,587 cases. Mutations were found in 14.1% of patients; 27.6% were familial and 8% were isolated. PRKN was the gene most frequently mutated in Caucasians, whereas PINK1 mutations predominated in Arab-Berber individuals. Patients with PRKN mutations had an earlier age at onset, and less asymmetry, levodopa-induced motor complications, dysautonomia, and dementia than those without mutations. ANN NEUROL 2020;88:843-850.

Identifiants

pubmed: 33045815
doi: 10.1002/ana.25787
pmc: PMC8944279
mid: NIHMS1789404
doi:

Substances chimiques

Ubiquitin-Protein Ligases EC 2.3.2.27
parkin protein EC 2.3.2.27
Protein Kinases EC 2.7.-
PTEN-induced putative kinase EC 2.7.11.1
PARK7 protein, human EC 3.1.2.-
Protein Deglycase DJ-1 EC 3.1.2.-

Types de publication

Journal Article Multicenter Study Research Support, N.I.H., Intramural Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

843-850

Subventions

Organisme : Intramural NIH HHS
ID : Z01 AG000949
Pays : United States
Organisme : Intramural NIH HHS
ID : Z01 AG000958
Pays : United States
Organisme : Intramural Research Program of the National Institute on Aging, National Institutes of Health, Department of Health and Human Services
ID : ZO1 AG000949
Pays : International

Investigateurs

Suzanne Lesage (S)
Ariane Lunati (A)
Marion Houot (M)
Sawssan Ben Romdhan (S)
Fabienne Clot (F)
Christelle Tesson (C)
Graziella Mangone (G)
Benjamin Le Toullec (B)
Thomas Courtin (T)
Kathy Larcher (K)
Mustapha Benmahdjoub (M)
Mohammed Arezki (M)
Ahmed Bouhouche (A)
Mathieu Anheim (M)
Emmanuel Roze (E)
François Viallet (F)
François Tison (F)
Emmanuel Broussolle (E)
Murat Emre (M)
Hasmet Hanagasi (H)
Basar Bilgic (B)
Mouna Ben Djebara (M)
Riadh Gouider (R)
Meriem Tazir (M)
Christine Tranchant (C)
Marie Vidailhet (M)
Eric Le Guern (E)
Olga Corti (O)
Chokri Mhiri (C)
Ebba Lohmann (E)
Andy Singleton (A)
Jean-Christophe Corvol (JC)
Alexis Brice (A)

Informations de copyright

© 2020 American Neurological Association.

Références

Am J Hum Genet. 2016 Mar 3;98(3):500-513
pubmed: 26942284
Arch Neurol. 2010 Jun;67(6):731-8
pubmed: 20558392
Arch Neurol. 2006 Sep;63(9):1257-61
pubmed: 16966503
Mov Disord Clin Pract. 2017 May 23;4(4):499-508
pubmed: 30363439
Mov Disord. 2018 May;33(5):730-741
pubmed: 29644727
Rev Neurol (Paris). 2018 Nov;174(9):628-643
pubmed: 30245141
JAMA Neurol. 2014 Jan;71(1):62-7
pubmed: 24190026
Ann Neurol. 2019 Aug;86(2):153-157
pubmed: 31155756
Eur J Neurol. 2012 May;19(5):769-75
pubmed: 22233331
Front Neurol. 2018 Aug 23;9:701
pubmed: 30190701
Front Neurol. 2017 Oct 31;8:567
pubmed: 29163333
Brain. 2006 Mar;129(Pt 3):686-94
pubmed: 16401616
Parkinsonism Relat Disord. 2019 Jul;64:8-19
pubmed: 30121162
Mov Disord Clin Pract. 2016 Sep-Oct;3(5):465-471
pubmed: 27709117
Hum Mutat. 2007 Jan;28(1):27-32
pubmed: 17068781
J Neurol Neurosurg Psychiatry. 1992 Mar;55(3):181-4
pubmed: 1564476
Mov Disord. 2012 Oct;27(12):1522-9
pubmed: 22956510
Brain. 2003 Jun;126(Pt 6):1279-92
pubmed: 12764051
Mov Disord. 2019 Apr;34(4):506-515
pubmed: 30788857
Ann Neurol. 2003 Aug;54(2):176-85
pubmed: 12891670

Auteurs

Suzanne Lesage (S)

Research Unit UMR 1127, Sorbonne University, Paris, France.
Research Unit U1127, National Institute of Health and Medical Research, Paris, France.
Research Unit UMR 7225, the French National Center for Scientific Research, Paris, France.
Institute for Brain and Spinal Cord, Paris, France.

Ariane Lunati (A)

Research Unit UMR 1127, Sorbonne University, Paris, France.
Research Unit U1127, National Institute of Health and Medical Research, Paris, France.
Research Unit UMR 7225, the French National Center for Scientific Research, Paris, France.
Institute for Brain and Spinal Cord, Paris, France.

Marion Houot (M)

Institute of Memory and Alzheimer's Disease, Center of Excellence for Neurodegenerative Diseases, Public Hospital Network of Paris, Department of Neurology, Pitié-Salpêtrière Hospital, University of Paris 6, Paris, France.
Clinical Investigation Center, Pitié Neurosciences CIC-1422, Paris, France.

Sawssan Ben Romdhan (SB)

Research Unit UMR 1127, Sorbonne University, Paris, France.
Research Unit U1127, National Institute of Health and Medical Research, Paris, France.
Research Unit UMR 7225, the French National Center for Scientific Research, Paris, France.
Institute for Brain and Spinal Cord, Paris, France.
Research Unit in Neurogenetics, Clinical Investigation Center, Habib Bourguiba University Hospital Center, Sfax, Tunisia.

Fabienne Clot (F)

Functional Unit of Molecular and Cellular Neurogenetics, Department of Genetics, Public Hospital Network of Paris, University Hospitals of La Pitié Salpêtrière-Charles Foix, Paris, France.

Christelle Tesson (C)

Research Unit UMR 1127, Sorbonne University, Paris, France.
Research Unit U1127, National Institute of Health and Medical Research, Paris, France.
Research Unit UMR 7225, the French National Center for Scientific Research, Paris, France.
Institute for Brain and Spinal Cord, Paris, France.

Graziella Mangone (G)

Clinical Investigation Center, Pitié Neurosciences CIC-1422, Paris, France.

Benjamin Le Toullec (BL)

Clinical Investigation Center, Pitié Neurosciences CIC-1422, Paris, France.

Thomas Courtin (T)

Research Unit UMR 1127, Sorbonne University, Paris, France.
Research Unit U1127, National Institute of Health and Medical Research, Paris, France.
Research Unit UMR 7225, the French National Center for Scientific Research, Paris, France.
Institute for Brain and Spinal Cord, Paris, France.

Kathy Larcher (K)

Functional Unit of Molecular and Cellular Neurogenetics, Department of Genetics, Public Hospital Network of Paris, University Hospitals of La Pitié Salpêtrière-Charles Foix, Paris, France.

Mustapha Benmahdjoub (M)

Frantz Fanon Hospital, University Hospital Center of Blida, Blida, Algeria.

Mohamed Arezki (M)

Frantz Fanon Hospital, University Hospital Center of Blida, Blida, Algeria.

Ahmed Bouhouche (A)

Research Unit in Neurology and Neurogenetics, Department of Neurology B and Neurogenetics, Faculty of Medicine and Pharmacy, Specialty Hospital ONO, Mohammed V University, Rabat, Morocco.

Mathieu Anheim (M)

Department of Neurology, University Hospitals of Strasbourg, Strasbourg, France.
Institute of Genetics and Molecular and Cellular Biology, Illkirch, France.
Federation of Translational Medicine of Strasbourg, University of Strasbourg, Strasbourg, France.

Emmanuel Roze (E)

Research Unit UMR 1127, Sorbonne University, Paris, France.
Research Unit U1127, National Institute of Health and Medical Research, Paris, France.
Research Unit UMR 7225, the French National Center for Scientific Research, Paris, France.
Institute for Brain and Spinal Cord, Paris, France.
Department of Neurology, Pitié-Salpêtrière Hospital, Paris, France.

François Viallet (F)

Department of Neurology, Intercommunal Hospital Center of Aix-Pertuis, Aix-en-Provence, France.
Department of Speech and Language, Research Unit UMR 7309, French National Center for Scientific Research and University of Aix-Marseille, Aix-en-Provence, France.

François Tison (F)

Department of Neurology, Pellegrin Hospital, University Hospital Center of Bordeaux, Bordeaux, France.
Institute of Neurodegenerative Diseases, University of Bordeaux, Bordeaux, France.
Research Unit UMR 5293, French National Center for Scientific Research, Bordeaux, France.

Emmanuel Broussolle (E)

Research Unit UMR 5229, Marc-Jeannerod Institute of Cognitive Science, French National Center for Scientific Research, University of Lyon, Bron, France.
Department of Neurology C, Civil Hospices of Lyon, Pierre-Wertheimer Neurological Hospital, Bron, France.
Faculty of Medicine Lyon-Sud Charles-Mérieux, University of Lyon, Oullins, France.

Murat Emre (M)

Behavioral Neurology and Movement Disorders Unit, Department of Neurology, Istanbul Faculty of Medicine, Istanbul University, Istanbul, Turkey.

Hasmet Hanagasi (H)

Behavioral Neurology and Movement Disorders Unit, Department of Neurology, Istanbul Faculty of Medicine, Istanbul University, Istanbul, Turkey.

Basar Bilgic (B)

Behavioral Neurology and Movement Disorders Unit, Department of Neurology, Istanbul Faculty of Medicine, Istanbul University, Istanbul, Turkey.

Meriem Tazir (M)

Department of Neurology, Mustapha Bacha University Hospital, Algiers, Algeria.

Mouna Ben Djebara (MB)

Department of Neurology, Faculty of Medicine of Tunis, Clinical Investigation Center, Razi University Hospital, Tunis, Tunisia.

Riadh Gouider (R)

Department of Neurology, Faculty of Medicine of Tunis, Clinical Investigation Center, Razi University Hospital, Tunis, Tunisia.

Christine Tranchant (C)

Department of Neurology, University Hospitals of Strasbourg, Strasbourg, France.
Institute of Genetics and Molecular and Cellular Biology, Illkirch, France.
Federation of Translational Medicine of Strasbourg, University of Strasbourg, Strasbourg, France.

Marie Vidailhet (M)

Research Unit UMR 1127, Sorbonne University, Paris, France.
Research Unit U1127, National Institute of Health and Medical Research, Paris, France.
Research Unit UMR 7225, the French National Center for Scientific Research, Paris, France.
Institute for Brain and Spinal Cord, Paris, France.
Department of Neurology, Pitié-Salpêtrière Hospital, Paris, France.

Eric Le Guern (E)

Research Unit UMR 1127, Sorbonne University, Paris, France.
Research Unit U1127, National Institute of Health and Medical Research, Paris, France.
Research Unit UMR 7225, the French National Center for Scientific Research, Paris, France.
Institute for Brain and Spinal Cord, Paris, France.
Functional Unit of Molecular and Cellular Neurogenetics, Department of Genetics, Public Hospital Network of Paris, University Hospitals of La Pitié Salpêtrière-Charles Foix, Paris, France.

Olga Corti (O)

Research Unit UMR 1127, Sorbonne University, Paris, France.
Research Unit U1127, National Institute of Health and Medical Research, Paris, France.
Research Unit UMR 7225, the French National Center for Scientific Research, Paris, France.
Institute for Brain and Spinal Cord, Paris, France.

Chokri Mhiri (C)

Research Unit in Neurogenetics, Clinical Investigation Center, Habib Bourguiba University Hospital Center, Sfax, Tunisia.

Ebba Lohmann (E)

Behavioral Neurology and Movement Disorders Unit, Department of Neurology, Istanbul Faculty of Medicine, Istanbul University, Istanbul, Turkey.
Department of Neurodegenerative Diseases, Hertie Institute for Clinical Brain Research, University of Tübingen, Tübingen, Germany.

Andrew Singleton (A)

Laboratory of Neurogenetics, National Institute on Aging, National Institutes of Health, Bethesda, Maryland.

Jean-Christophe Corvol (JC)

Research Unit UMR 1127, Sorbonne University, Paris, France.
Research Unit U1127, National Institute of Health and Medical Research, Paris, France.
Research Unit UMR 7225, the French National Center for Scientific Research, Paris, France.
Institute for Brain and Spinal Cord, Paris, France.
Clinical Investigation Center, Pitié Neurosciences CIC-1422, Paris, France.

Alexis Brice (A)

Research Unit UMR 1127, Sorbonne University, Paris, France.
Research Unit U1127, National Institute of Health and Medical Research, Paris, France.
Research Unit UMR 7225, the French National Center for Scientific Research, Paris, France.
Institute for Brain and Spinal Cord, Paris, France.

Articles similaires

[Redispensing of expensive oral anticancer medicines: a practical application].

Lisanne N van Merendonk, Kübra Akgöl, Bastiaan Nuijen
1.00
Humans Antineoplastic Agents Administration, Oral Drug Costs Counterfeit Drugs

Smoking Cessation and Incident Cardiovascular Disease.

Jun Hwan Cho, Seung Yong Shin, Hoseob Kim et al.
1.00
Humans Male Smoking Cessation Cardiovascular Diseases Female
Humans United States Aged Cross-Sectional Studies Medicare Part C
1.00
Humans Yoga Low Back Pain Female Male

Classifications MeSH