A Peptidyl Inhibitor that Blocks Calcineurin-NFAT Interaction and Prevents Acute Lung Injury.


Journal

Journal of medicinal chemistry
ISSN: 1520-4804
Titre abrégé: J Med Chem
Pays: United States
ID NLM: 9716531

Informations de publication

Date de publication:
12 11 2020
Historique:
pubmed: 20 10 2020
medline: 19 12 2020
entrez: 19 10 2020
Statut: ppublish

Résumé

Acute respiratory distress syndrome (ARDS) is an inflammatory lung disease with a high morbidity and mortality rate, for which no pharmacologic treatment is currently available. Our previous studies discovered that a pivotal step in the disease process is the activation of the nuclear factor of activated T cells (NFAT) c3 in lung macrophages, suggesting that inhibitors against the upstream protein phosphatase calcineurin should be effective for prevention/treatment of ARDS. Herein, we report the development of a highly potent, cell-permeable, and metabolically stable peptidyl inhibitor, CNI103, which selectively blocks the interaction between calcineurin and NFATc3, through computational and medicinal chemistry. CNI103 specifically inhibited calcineurin signaling

Identifiants

pubmed: 33073986
doi: 10.1021/acs.jmedchem.0c01236
pmc: PMC8011862
mid: NIHMS1682094
doi:

Substances chimiques

Calcineurin Inhibitors 0
Lipopolysaccharides 0
NFATC Transcription Factors 0
Peptides 0
transcription factor NF-AT c3 0
Calcineurin EC 3.1.3.16

Types de publication

Journal Article Research Support, N.I.H., Extramural Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

12853-12872

Subventions

Organisme : NIGMS NIH HHS
ID : R01 GM110406
Pays : United States
Organisme : NHLBI NIH HHS
ID : R01 HL137224
Pays : United States
Organisme : NIGMS NIH HHS
ID : R35 GM122459
Pays : United States

Références

Sci Signal. 2015 Jun 23;8(382):ra63
pubmed: 26106221
Ann Am Thorac Soc. 2016 Oct;13(10):1742-1751
pubmed: 27403914
Chest. 2007 Feb;131(2):554-62
pubmed: 17296661
Cell Commun Signal. 2009 Oct 27;7:25
pubmed: 19860902
Rheumatol Int. 2020 Jul;40(7):1177-1179
pubmed: 32415310
J Vis Exp. 2014 Dec 05;(94):
pubmed: 25549242
J Med Chem. 2014 Sep 25;57(18):7792-7
pubmed: 25162754
Arterioscler Thromb Vasc Biol. 2006 Jul;26(7):1531-7
pubmed: 16675727
Mol Ther Methods Clin Dev. 2019 Oct 23;16:32-41
pubmed: 31737742
Adv Drug Deliv Rev. 2015 Jun 29;87:46-51
pubmed: 25666165
Angew Chem Int Ed Engl. 2017 Aug 21;56(35):10294-10323
pubmed: 28186380
Cardiovasc Drug Rev. 2007 Summer;25(2):175-87
pubmed: 17614939
Proc Natl Acad Sci U S A. 2004 May 18;101(20):7554-9
pubmed: 15131267
Am J Respir Crit Care Med. 2014 Mar 15;189(6):674-83
pubmed: 24392848
J Comput Chem. 2004 Oct;25(13):1605-12
pubmed: 15264254
Lancet. 1967 Aug 12;2(7511):319-23
pubmed: 4143721
J Biol Chem. 2005 Nov 11;280(45):37698-706
pubmed: 16148011
N Engl J Med. 2019 May 23;380(21):1997-2008
pubmed: 31112383
J Med Chem. 2006 Oct 19;49(21):6177-96
pubmed: 17034125
Biochemistry. 2005 Nov 15;44(45):14932-47
pubmed: 16274240
Nat Med. 2004 Mar;10(3):305-9
pubmed: 14770176
Blood. 2013 May 9;121(19):3879-88, S1-8
pubmed: 23460614
J Am Soc Mass Spectrom. 2018 Mar;29(3):516-526
pubmed: 29209911
J Innate Immun. 2014;6(6):754-64
pubmed: 24970700
Oncotarget. 2018 Jan 25;9(12):10606-10620
pubmed: 29535830
J Med Chem. 2019 Nov 27;62(22):10098-10107
pubmed: 31657556
Chem Commun (Camb). 2015 Feb 7;51(11):2162-5
pubmed: 25554998
PLoS One. 2014 Apr 02;9(4):e93362
pubmed: 24695324
J Med Chem. 2016 Sep 8;59(17):8061-7
pubmed: 27509198
Int J Mol Sci. 2019 May 14;20(10):
pubmed: 31091705
J Org Chem. 2020 Feb 7;85(3):1416-1424
pubmed: 31609620
Respir Care. 2014 Feb;59(2):288-96
pubmed: 23777655
Chem Rev. 1997 Apr 1;97(2):411-448
pubmed: 11848877
PLoS One. 2012;7(3):e34172
pubmed: 22479554
J Intensive Care. 2014 May 07;2(1):32
pubmed: 25520844
ACS Chem Biol. 2020 Sep 18;15(9):2485-2492
pubmed: 32786250
Chest. 1996 Dec;110(6 Suppl):273S-277S
pubmed: 8989164
Chem Asian J. 2012 Jun;7(6):1221-30
pubmed: 22488808
J Neurosci. 2012 Feb 29;32(9):3176-92
pubmed: 22378890
Biochemistry. 2014 Jun 24;53(24):4034-46
pubmed: 24896852
Cell. 1999 Mar 5;96(5):611-4
pubmed: 10089876
Circ Res. 2012 Jan 20;110(2):200-10
pubmed: 22116820
N Engl J Med. 2019 Dec 26;381(26):2529-2540
pubmed: 31826336
Lancet Respir Med. 2019 Feb;7(2):154-162
pubmed: 30455077
Methods. 2007 Jul;42(3):207-19
pubmed: 17532507
Annu Rev Med. 1986;37:215-24
pubmed: 2939791
Crit Rev Immunol. 2011;31(5):379-446
pubmed: 22142165
Immunol Lett. 2012 Apr 30;143(2):170-6
pubmed: 22342853
Br J Surg. 1993 Jan;80(1):10-7
pubmed: 8428262
Science. 1999 Sep 24;285(5436):2129-33
pubmed: 10497131
Chem Biol Drug Des. 2006 Mar;67(3):238-43
pubmed: 16611217
Curr Opin Chem Biol. 2017 Jun;38:80-86
pubmed: 28388463
Cell. 1991 Aug 23;66(4):807-15
pubmed: 1715244
J Med Chem. 2004 Mar 25;47(7):1750-9
pubmed: 15027866
Biochemistry. 2016 May 10;55(18):2601-12
pubmed: 27089101
Proc Natl Acad Sci U S A. 2007 Jul 3;104(27):11418-23
pubmed: 17596340
N Engl J Med. 2014 Oct 30;371(18):1695-703
pubmed: 25268516
J Biol Chem. 2010 Jan 15;285(3):1888-98
pubmed: 19923214

Auteurs

Patrick G Dougherty (PG)

Department of Chemistry and Biochemistry, The Ohio State University, 484 West 12th Ave., Columbus, Ohio 43210, United States.
Entrada Therapeutics, 50 Northern Avenue, Boston, Massachusetts 02210, United States.

Manjula Karpurapu (M)

Department of Medicine, Division of Pulmonary, Critical Care and Sleep Medicine, Ohio State University Wexner Medical Center, Davis Heart and Lung Research Institute, Columbus, Ohio 43210, United States.

Amritendu Koley (A)

Department of Chemistry and Biochemistry, The Ohio State University, 484 West 12th Ave., Columbus, Ohio 43210, United States.

Jessica K Lukowski (JK)

Department of Chemistry and Biochemistry, University of Notre Dame, Notre Dame, Indiana 46556, United States.

Ziqing Qian (Z)

Department of Chemistry and Biochemistry, The Ohio State University, 484 West 12th Ave., Columbus, Ohio 43210, United States.
Entrada Therapeutics, 50 Northern Avenue, Boston, Massachusetts 02210, United States.

Teja Srinivas Nirujogi (T)

Department of Medicine, Division of Pulmonary, Critical Care and Sleep Medicine, Ohio State University Wexner Medical Center, Davis Heart and Lung Research Institute, Columbus, Ohio 43210, United States.
East Liverpool City Hospital, 425 W 5th Street, East Liverpool, Ohio 43920, United States.

Luiza Rusu (L)

Department of Medicine, Division of Pulmonary, Critical Care and Sleep Medicine, Ohio State University Wexner Medical Center, Davis Heart and Lung Research Institute, Columbus, Ohio 43210, United States.

Sangwoon Chung (S)

Department of Medicine, Division of Pulmonary, Critical Care and Sleep Medicine, Ohio State University Wexner Medical Center, Davis Heart and Lung Research Institute, Columbus, Ohio 43210, United States.

Amanda B Hummon (AB)

Department of Chemistry and Biochemistry, The Ohio State University, 484 West 12th Ave., Columbus, Ohio 43210, United States.
Comprehensive Cancer Center, The Ohio State University, Columbus Ohio, 43210, United States.

Hao W Li (HW)

Columbia Center for Translational Immunology, Columbia University, 650 W. 168th Street, New York, New York 10032, United States.

John W Christman (JW)

Department of Medicine, Division of Pulmonary, Critical Care and Sleep Medicine, Ohio State University Wexner Medical Center, Davis Heart and Lung Research Institute, Columbus, Ohio 43210, United States.

Dehua Pei (D)

Department of Chemistry and Biochemistry, The Ohio State University, 484 West 12th Ave., Columbus, Ohio 43210, United States.

Articles similaires

[Redispensing of expensive oral anticancer medicines: a practical application].

Lisanne N van Merendonk, Kübra Akgöl, Bastiaan Nuijen
1.00
Humans Antineoplastic Agents Administration, Oral Drug Costs Counterfeit Drugs

Smoking Cessation and Incident Cardiovascular Disease.

Jun Hwan Cho, Seung Yong Shin, Hoseob Kim et al.
1.00
Humans Male Smoking Cessation Cardiovascular Diseases Female
Humans United States Aged Cross-Sectional Studies Medicare Part C
1.00
Humans Yoga Low Back Pain Female Male

Classifications MeSH