Cost-Effectiveness of Lenvatinib Compared with Sorafenib for the First-Line Treatment of Advanced Hepatocellular Carcinoma in Australia.


Journal

Clinical drug investigation
ISSN: 1179-1918
Titre abrégé: Clin Drug Investig
Pays: New Zealand
ID NLM: 9504817

Informations de publication

Date de publication:
Dec 2020
Historique:
accepted: 24 10 2020
pubmed: 4 11 2020
medline: 27 1 2021
entrez: 3 11 2020
Statut: ppublish

Résumé

In the REFLECT trial, lenvatinib showed superior clinical benefits to sorafenib in terms of progression-free survival and was non-inferior for overall survival in the treatment of advanced hepatocellular carcinoma (HCC). We assessed the cost-effectiveness of lenvatinib compared with sorafenib for patients with advanced HCC in Australia. A partitioned-survival model was built to perform a cost-effectiveness analysis comparing lenvatinib and sorafenib from an Australian health-system perspective. Survival curves were obtained from the REFLECT trial and fitted with parametric survival functions for extrapolation purposes beyond the trial follow-up. Cost and quality-adjusted life-years (QALYs) were accrued over the 10-year time horizon of the model. Deterministic and probability sensitivity analysis (PSA) were carried out to verify the validity of the model. Lenvatinib incurred higher costs (A$96,325) and superior health outcomes (QALYs: 1.205), while sorafenib had lower costs (A$92,394) and inferior health outcomes (QALYs: 1.086). Thus, lenvatinib yielded an incremental cost-utility ratio of A$33,028/QALY gained. Further, the results of the PSA found that the probability of lenvatinib being cost-effective at a willingness-to-pay threshold of A$50,000/QALY was 64%. Our study found that, at current prices, lenvatinib is a cost-effective treatment option compared with sorafenib for the first-line treatment of patients with advanced HCC.

Sections du résumé

BACKGROUND AND OBJECTIVE OBJECTIVE
In the REFLECT trial, lenvatinib showed superior clinical benefits to sorafenib in terms of progression-free survival and was non-inferior for overall survival in the treatment of advanced hepatocellular carcinoma (HCC). We assessed the cost-effectiveness of lenvatinib compared with sorafenib for patients with advanced HCC in Australia.
METHOD METHODS
A partitioned-survival model was built to perform a cost-effectiveness analysis comparing lenvatinib and sorafenib from an Australian health-system perspective. Survival curves were obtained from the REFLECT trial and fitted with parametric survival functions for extrapolation purposes beyond the trial follow-up. Cost and quality-adjusted life-years (QALYs) were accrued over the 10-year time horizon of the model. Deterministic and probability sensitivity analysis (PSA) were carried out to verify the validity of the model.
RESULTS RESULTS
Lenvatinib incurred higher costs (A$96,325) and superior health outcomes (QALYs: 1.205), while sorafenib had lower costs (A$92,394) and inferior health outcomes (QALYs: 1.086). Thus, lenvatinib yielded an incremental cost-utility ratio of A$33,028/QALY gained. Further, the results of the PSA found that the probability of lenvatinib being cost-effective at a willingness-to-pay threshold of A$50,000/QALY was 64%.
CONCLUSION CONCLUSIONS
Our study found that, at current prices, lenvatinib is a cost-effective treatment option compared with sorafenib for the first-line treatment of patients with advanced HCC.

Identifiants

pubmed: 33140194
doi: 10.1007/s40261-020-00983-7
pii: 10.1007/s40261-020-00983-7
doi:

Substances chimiques

Antineoplastic Agents 0
Phenylurea Compounds 0
Quinolines 0
Sorafenib 9ZOQ3TZI87
lenvatinib EE083865G2

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

1167-1176

Références

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Auteurs

Masnoon Saiyed (M)

Centre for Applied Health Economics, Griffith University, Nathan, QLD, 4111, Australia. m.saiyed@griffith.edu.au.

Joshua Byrnes (J)

Centre for Applied Health Economics, Griffith University, Nathan, QLD, 4111, Australia.

Tushar Srivastava (T)

School of Health and Related Research (ScHARR), University of Sheffield, Sheffield, S1 4DA, UK.

Paul Scuffham (P)

Centre for Applied Health Economics, Griffith University, Nathan, QLD, 4111, Australia.
Menzies Health Institute Queensland, Griffith University, Nathan, QLD, 4111, Australia.

Martin Downes (M)

Centre for Applied Health Economics, Griffith University, Nathan, QLD, 4111, Australia.

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