Cerebrospinal Fluid Penetration and Combination Therapy of Entrectinib for Disseminated
CSF penetrance
NTRK fusion
ROS1 fusion
abemaciclib
entrectinib
radiotherapy
targeted therapies
trametinib
Journal
Journal of personalized medicine
ISSN: 2075-4426
Titre abrégé: J Pers Med
Pays: Switzerland
ID NLM: 101602269
Informations de publication
Date de publication:
18 Dec 2020
18 Dec 2020
Historique:
received:
18
11
2020
revised:
15
12
2020
accepted:
16
12
2020
entrez:
23
12
2020
pubmed:
24
12
2020
medline:
24
12
2020
Statut:
epublish
Résumé
Targeting oncogenic fusion-genes in pediatric high-grade gliomas (pHGG) with entrectinib has emerged as a highly promising therapeutic approach. Despite ongoing clinical studies, to date, no reports on the treatment of cerebrospinal fluid (CSF) disseminated fusion-positive pHGG exist. Moreover, clinically important information of combination with other treatment modalities such as intrathecal therapy, radiotherapy and other targeted agents is missing. We report on our clinical experience of entrectinib therapy in two CSF disseminated
Identifiants
pubmed: 33353026
pii: jpm10040290
doi: 10.3390/jpm10040290
pmc: PMC7766483
pii:
doi:
Types de publication
Journal Article
Langues
eng
Subventions
Organisme : Medical-scientific fund of the Mayor of the federal capital Vienna
ID : 19086
Organisme : Austrian Science Fund
ID : T 906-B28
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