Anakinra usage in febrile infection related epilepsy syndrome: an international cohort.


Journal

Annals of clinical and translational neurology
ISSN: 2328-9503
Titre abrégé: Ann Clin Transl Neurol
Pays: United States
ID NLM: 101623278

Informations de publication

Date de publication:
12 2020
Historique:
received: 28 07 2020
revised: 02 10 2020
accepted: 04 10 2020
entrez: 28 1 2021
pubmed: 29 1 2021
medline: 6 10 2021
Statut: ppublish

Résumé

Febrile-infection related epilepsy syndrome (FIRES) is a devastating neurological condition characterized by a febrile illness preceding new onset refractory status epilepticus (NORSE). Increasing evidence suggests innate immune dysfunction as a potential pathological mechanism. We report an international retrospective cohort of 25 children treated with anakinra, a recombinant interleukin-1 receptor antagonist, as an immunomodulator for FIRES. Anakinra was potentially safe with only one child discontinuing therapy due to infection. Earlier anakinra initiation was associated with shorter duration of mechanical ventilation, ICU and hospital length of stay. Our retrospective data lay the groundwork for prospective consensus-driven cohort studies of anakinra in FIRES.

Identifiants

pubmed: 33506622
doi: 10.1002/acn3.51229
pmc: PMC7732241
doi:

Substances chimiques

Interleukin 1 Receptor Antagonist Protein 0

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

2467-2474

Informations de copyright

© 2020 The Authors. Annals of Clinical and Translational Neurology published by Wiley Periodicals LLC on behalf of American Neurological Association.

Références

Ann Neurol. 2019 Apr;85(4):526-537
pubmed: 30779222
Epilepsia. 2018 Apr;59(4):745-752
pubmed: 29476535
Epilepsia. 2011 Nov;52(11):1956-65
pubmed: 21883180
Epilepsia. 2010 Jul;51(7):1323-8
pubmed: 20345937
Epilepsia. 2017 Jun;58(6):1102-1111
pubmed: 28448686
Eur J Paediatr Neurol. 2019 Sep;23(5):749-754
pubmed: 31446001
Rheumatology (Oxford). 2019 Nov 1;58(Suppl 6):vi9-vi22
pubmed: 31769856
Orphanet J Rare Dis. 2015 Feb 15;10:19
pubmed: 25758134
Epilepsia Open. 2019 Mar 27;4(2):344-350
pubmed: 31168503
J Neurosci. 1999 Jun 15;19(12):5054-65
pubmed: 10366638
Ann Neurol. 2016 Dec;80(6):939-945
pubmed: 27770579
Epilepsia. 2018 Sep;59(9):1753-1763
pubmed: 30132834
Proc Natl Acad Sci U S A. 2016 Sep 20;113(38):E5665-74
pubmed: 27601660
Epilepsia. 2018 Apr;59(4):739-744
pubmed: 29399791
J Neurosci. 2003 Sep 24;23(25):8692-700
pubmed: 14507968

Auteurs

Yi-Chen Lai (YC)

Baylor College of Medicine/Texas Children's Hospital, Houston, Texas, USA.

Eyal Muscal (E)

Baylor College of Medicine/Texas Children's Hospital, Houston, Texas, USA.

Elizabeth Wells (E)

Children's National Health System, Washington, District of Columbia, USA.

Nikita Shukla (N)

Baylor College of Medicine/Texas Children's Hospital, Houston, Texas, USA.

Krista Eschbach (K)

Department of Pediatrics, Section of Neurology, Children's Hospital Colorado, University of Colorado, Aurora, Colorado, USA.

Ki Hyeong Lee (K)

AdventHealth, Child Neurology and Comprehensive Epilepsy Center, Orlando, Florida, USA.

Marios Kaliakatsos (M)

Neurosciences Department, Great Ormond Street Hospital, London, UK.

Nevedita Desai (N)

Neurosciences Department, Great Ormond Street Hospital, London, UK.

Ronny Wickström (R)

Department of Women's and Children's Health, Karolinska University Hospital, Neuropediatric Unit, Stockholm, Sweden.

Maurizio Viri (M)

Childhood Neuropsychiatric Department, University Hospital Maggiore della Carità, Novara, Italy.

Elena Freri (E)

Department of Pediatric Neuroscience, FONDAZIONE IRCCS ISTITUTO NEUROLOGICO "CARLO BESTA", Milan, Italy.

Tiziana Granata (T)

Department of Pediatric Neuroscience, FONDAZIONE IRCCS ISTITUTO NEUROLOGICO "CARLO BESTA", Milan, Italy.

Srishti Nangia (S)

New York Presbyterian Hospital-Weill Cornell Medical College, NYC, New York, New York, USA.

Robertino Dilena (R)

Clinical Neurophysiology, Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.
Department of Neurosciences, Rehabilitation, Ophthalmology, Genetics, Maternal and Child Health, University of Genova, Genova, Italy.

Andreas Brunklaus (A)

Fraser of Allander Neurosciences Unit, Royal Hospital for Children, Glasgow, UK.

Mark S Wainwright (MS)

Department of Neurology, University of Washington, Seattle, Washington, USA.

Mark P Gorman (MP)

Department of Neurology, Pediatric Multiple Sclerosis and Related Disorders Program, Boston Children's Hospital, Harvard Medical School, Boston, Massachusetts, USA.

Coral M Stredny (CM)

Department of Neurology, Pediatric Multiple Sclerosis and Related Disorders Program, Boston Children's Hospital, Harvard Medical School, Boston, Massachusetts, USA.

Abdurhman Asiri (A)

Prince Sultan Medical Military City (PSMMC), Riyadh, Saudi Arabia.

Khalid Hundallah (K)

Prince Sultan Medical Military City (PSMMC), Riyadh, Saudi Arabia.

Asif Doja (A)

Division of Neurology, CHEO Research Institute, Faculty of Medicine, University of Ottawa, Ottawa, Canada.

Eric Payne (E)

Divisions of Neurology, Department of Pediatrics, Alberta Children's Hospital, Calgary, Alberta, Canada.

Elaine Wirrell (E)

Divisions of Child and Adolescent Neurology and Epilepsy, Department of Pediatric Neurology, Mayo Clinic, Rochester, Minnesota, USA.

Sookyong Koh (S)

Division of Neurology, Department of Pediatrics, Emory University School of Medicine, Atlanta, Georgia, USA.

Jessica L Carpenter (JL)

Children's National Health System, Washington, District of Columbia, USA.

James Riviello (J)

Baylor College of Medicine/Texas Children's Hospital, Houston, Texas, USA.

Articles similaires

[Redispensing of expensive oral anticancer medicines: a practical application].

Lisanne N van Merendonk, Kübra Akgöl, Bastiaan Nuijen
1.00
Humans Antineoplastic Agents Administration, Oral Drug Costs Counterfeit Drugs

Smoking Cessation and Incident Cardiovascular Disease.

Jun Hwan Cho, Seung Yong Shin, Hoseob Kim et al.
1.00
Humans Male Smoking Cessation Cardiovascular Diseases Female
Humans United States Aged Cross-Sectional Studies Medicare Part C
1.00
Humans Yoga Low Back Pain Female Male

Classifications MeSH