Tocilizumab in COVID-19 interstitial pneumonia.


Journal

Journal of internal medicine
ISSN: 1365-2796
Titre abrégé: J Intern Med
Pays: England
ID NLM: 8904841

Informations de publication

Date de publication:
05 2021
Historique:
revised: 25 11 2020
received: 23 09 2020
accepted: 14 12 2020
pubmed: 30 1 2021
medline: 5 5 2021
entrez: 29 1 2021
Statut: ppublish

Résumé

Published reports on tocilizumab in COVID-19 pneumonitis show conflicting results due to weak designs or heterogeneity in critical methodological issues. This open-label trial, structured according to Simon's optimal design, aims to identify factors predicting which patients could benefit from anti-IL6 strategies and to enhance the design of unequivocal and reliable future randomized trials. A total of 46 patients with COVID-19 pneumonia needing of oxygen therapy to maintain SO2 > 93% and with recent worsening of lung function received a single infusion of tocilizumab. Clinical and biological markers were measured to test their predictive values. Primary end point was early and sustained clinical response. Twenty-one patients fulfilled pre-defined response criteria. Lower levels of IL-6 at 24 h after tocilizumab infusion (P = 0.049) and higher baseline values of PaO2/FiO2 (P = 0.008) predicted a favourable response. Objective clinical response rate overcame the pre-defined threshold of 30%. Efficacy of tocilizumab to improve respiratory function in patients selected according to our inclusion criteria warrants investigations in randomized trials.

Sections du résumé

BACKGROUND
Published reports on tocilizumab in COVID-19 pneumonitis show conflicting results due to weak designs or heterogeneity in critical methodological issues.
METHODS
This open-label trial, structured according to Simon's optimal design, aims to identify factors predicting which patients could benefit from anti-IL6 strategies and to enhance the design of unequivocal and reliable future randomized trials. A total of 46 patients with COVID-19 pneumonia needing of oxygen therapy to maintain SO2 > 93% and with recent worsening of lung function received a single infusion of tocilizumab. Clinical and biological markers were measured to test their predictive values. Primary end point was early and sustained clinical response.
RESULTS
Twenty-one patients fulfilled pre-defined response criteria. Lower levels of IL-6 at 24 h after tocilizumab infusion (P = 0.049) and higher baseline values of PaO2/FiO2 (P = 0.008) predicted a favourable response.
CONCLUSIONS
Objective clinical response rate overcame the pre-defined threshold of 30%. Efficacy of tocilizumab to improve respiratory function in patients selected according to our inclusion criteria warrants investigations in randomized trials.

Identifiants

pubmed: 33511686
doi: 10.1111/joim.13231
pmc: PMC8013903
doi:

Substances chimiques

Antibodies, Monoclonal, Humanized 0
Biomarkers, Pharmacological 0
Immunologic Factors 0
Interleukin-6 0
tocilizumab I031V2H011

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

738-746

Subventions

Organisme : Azienda Ospedaliera Universitaria Ospedali Riuniti, Ancona, Italy

Informations de copyright

© 2020 The Association for the Publication of the Journal of Internal Medicine.

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Auteurs

G Pomponio (G)

From the, Clinica Medica, Ospedali Riuniti di Ancona, Ancona, Italy.

A Ferrarini (A)

From the, Clinica Medica, Ospedali Riuniti di Ancona, Ancona, Italy.

M Bonifazi (M)

Pneumologia, Ospedali Riuniti di Ancona, Ancona, Italy.

M Moretti (M)

SOD Medicina di Laboratorio Ospedali Riuniti di Ancona, Ancona, Italy.

A Salvi (A)

Medicina Interna e Sub Intensiva, Ospedali Riuniti di Ancona, Ancona, Italy.

A Giacometti (A)

Clinica di Malattie Infettive, Ospedali Riuniti di Ancona, Ancona, Italy.

M Tavio (M)

Malattie Infettive, Ospedali Riuniti di Ancona, Ancona, Italy.

G Titolo (G)

Medicina di Urgenza, Ospedali Riuniti Marche Nord, Pesaro/Fano, Italy.

L Morbidoni (L)

Medicina Interna, Ospedale di Senigallia, Senigallia, Italy.

G Frausini (G)

Medicina Interna, Ospedali Riuniti Marche Nord, Pesaro/Fano, Italy.

M Onesta (M)

Medicina Interna, Ospedale di Fabriano, Fabriano, Italy.

D Amico (D)

Pneumologia, Ospedali Riuniti Marche Nord, Pesaro/Fano, Italy.

M L B Rocchi (MLB)

Statistica Medica, Dipartimento di Scienze Biomolecolari, Università di Urbino, Urbino, Italy.

S Menzo (S)

Virologia, Ospedali Riuniti di Ancona, Ancona, Italy.

L Zuccatosta (L)

Pneumologia, Ospedali Riuniti di Ancona, Ancona, Italy.

F Mei (F)

Pneumologia, Ospedali Riuniti di Ancona, Ancona, Italy.

V Menditto (V)

Medicina Interna e Sub Intensiva, Ospedali Riuniti di Ancona, Ancona, Italy.

S Svegliati (S)

Clinica Medica, DISCLIMO, Università Politecnica delle Marche, Ancona, Italy.

A Donati (A)

Clinica di Rianimazione, Ospedali Riuniti di Ancona, Ancona, Italy.

M M D'Errico (MM)

Dip. Scienze biomediche e sanità pubblica, Università Politecnica delle Marche, Ancona, Italy.

M Pavani (M)

Laboratorio di Patologia Sperimentale, DISCLIMO, Università Politecnica delle Marche, Ancona, Italy.

A Gabrielli (A)

From the, Clinica Medica, Ospedali Riuniti di Ancona, Ancona, Italy.
Clinica Medica, DISCLIMO, Università Politecnica delle Marche, Ancona, Italy.

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