Alleviation of Huntington pathology in mice by oral administration of food additive glyceryl tribenzoate.


Journal

Neurobiology of disease
ISSN: 1095-953X
Titre abrégé: Neurobiol Dis
Pays: United States
ID NLM: 9500169

Informations de publication

Date de publication:
06 2021
Historique:
received: 12 11 2020
revised: 05 02 2021
accepted: 22 02 2021
pubmed: 27 2 2021
medline: 29 1 2022
entrez: 26 2 2021
Statut: ppublish

Résumé

Huntington's disease (HD) is a neurodegenerative disorder characterized by accumulation of mutant huntingtin protein and significant loss of neurons in striatum and cortex. Along with motor difficulties, the HD patients also manifest anxiety and loss of cognition. Unfortunately, the clinically approved drugs only offer symptomatic relief and are not free from side effects. This study underlines the importance of glyceryl tribenzoate (GTB), an FDA-approved food flavoring ingredient, in alleviating HD pathology in transgenic N171-82Q mouse model. Oral administration of GTB significantly reduced mutant huntingtin level in striatum, motor cortex as well as hippocampus and increased the integrity of viable neurons. Furthermore, we found the presence of sodium benzoate (NaB), a FDA-approved drug for urea cycle disorders and glycine encephalopathy, in the brain of GTB-fed HD mice. Accordingly, NaB administration also markedly decreased huntingtin level in striatum and cortex. Glial activation is found to coincide with neuronal death in affected regions of HD brains. Interestingly, both GTB and NaB treatment suppressed activation of glial cells and inflammation in the brain. Finally, neuroprotective effect of GTB and NaB resulted in improved motor performance of HD mice. Collectively, these results suggest that GTB and NaB may be repurposed for HD.

Identifiants

pubmed: 33636386
pii: S0969-9961(21)00067-X
doi: 10.1016/j.nbd.2021.105318
pmc: PMC8026693
mid: NIHMS1677088
pii:
doi:

Substances chimiques

Benzoates 0
Flavoring Agents 0
Food Preservatives 0
HTT protein, human 0
Huntingtin Protein 0
glyceryl tribenzoate 0
Benzoic Acid 8SKN0B0MIM
Sodium Benzoate OJ245FE5EU

Types de publication

Journal Article Research Support, N.I.H., Extramural Research Support, Non-U.S. Gov't Research Support, U.S. Gov't, Non-P.H.S.

Langues

eng

Sous-ensembles de citation

IM

Pagination

105318

Subventions

Organisme : BLRD VA
ID : IK6 BX004982
Pays : United States
Organisme : NIA NIH HHS
ID : R01 AG050431
Pays : United States
Organisme : NCCIH NIH HHS
ID : R01 AT010980
Pays : United States
Organisme : NINDS NIH HHS
ID : R21 NS108025
Pays : United States

Informations de copyright

Copyright © 2021 The Author(s). Published by Elsevier Inc. All rights reserved.

Références

Nat Rev Immunol. 2008 Nov;8(11):837-48
pubmed: 18927578
J Neuroimmune Pharmacol. 2013 Jun;8(3):739-55
pubmed: 23475543
J Clin Cell Immunol. 2017 Feb;8(1):
pubmed: 28367355
CNS Neurosci Ther. 2014 Jan;20(1):10-9
pubmed: 24188794
Arch Neurol. 2005 Jan;62(1):46-51
pubmed: 15642849
J Neuropathol Exp Neurol. 2001 Feb;60(2):161-72
pubmed: 11273004
J Neuroimmune Pharmacol. 2020 Sep 5;:
pubmed: 32889602
Biomed Rep. 2013 Mar;1(2):193-196
pubmed: 24648917
J Clin Invest. 1997 Dec 1;100(11):2671-9
pubmed: 9389730
J Neurosci. 2006 May 3;26(18):4930-9
pubmed: 16672668
Fundam Appl Toxicol. 1984 Jun;4(3 Pt 1):494-6
pubmed: 6745539
Nat Rev Dis Primers. 2015 Apr 23;1:15005
pubmed: 27188817
Biochem Biophys Res Commun. 2006 Mar 31;342(1):184-90
pubmed: 16472774
S Afr Med J. 1981 Feb 21;59(8):250
pubmed: 6451036
J Biol Chem. 2010 Mar 19;285(12):8808-23
pubmed: 20086007
Cancer Res Treat. 2013 Dec;45(4):313-24
pubmed: 24454004
J Immunol. 2009 Nov 1;183(9):5917-27
pubmed: 19812204
Trends Immunol. 2015 Jun;36(6):364-73
pubmed: 26001312
J Neuroimmune Pharmacol. 2014 Sep;9(4):569-81
pubmed: 24946862
J Biol Chem. 2006 May 26;281(21):14971-80
pubmed: 16551637
Neurobiol Dis. 2019 Dec;132:104575
pubmed: 31445159
J Neurosci. 2004 Sep 15;24(37):7999-8008
pubmed: 15371500
Biochem J. 1970 Jun;118(1):47-51
pubmed: 4990586
J Neuropathol Exp Neurol. 2019 Feb 1;78(2):123-129
pubmed: 30605553
CNS Neurol Disord Drug Targets. 2013 Sep;12(6):726-40
pubmed: 24070095
J Immunol. 2007 Jul 1;179(1):275-83
pubmed: 17579047
Orphanet J Rare Dis. 2010 Dec 20;5:40
pubmed: 21171977
Antioxid Redox Signal. 2006 May-Jun;8(5-6):929-47
pubmed: 16771683
Brain. 2007 Jul;130(Pt 7):1759-66
pubmed: 17400599
J Med Genet. 1999 Apr;36(4):265-70
pubmed: 10227391
Int J Mol Sci. 2020 May 20;21(10):
pubmed: 32443829
Neurodegener Dis Manag. 2016 Aug;6(4):331-43
pubmed: 27507223
Neuroimage. 2012 May 1;60(4):2086-95
pubmed: 22342677
Cells. 2016 Mar 18;5(1):
pubmed: 26999213
Eur J Neurosci. 2008 Jun;27(11):2803-20
pubmed: 18588526
Mol Neurobiol. 2018 Jan;55(1):804-821
pubmed: 28062948
J Neuroimmunol. 2020 Nov 15;348:577380
pubmed: 32896821
Neurobiol Dis. 2008 Jun;30(3):293-302
pubmed: 18395459
Brain Res. 2000 Mar 10;858(2):356-62
pubmed: 10708687
Int Immunopharmacol. 2014 Feb;18(2):325-32
pubmed: 24378401
Front Aging Neurosci. 2020 Sep 03;12:571185
pubmed: 33101007
PLoS One. 2015 Jun 23;10(6):e0130398
pubmed: 26102198
Cell. 1993 Mar 26;72(6):971-83
pubmed: 8458085
Mol Neurobiol. 2015 Feb;51(1):406-23
pubmed: 24788684
Bio Protoc. 2017 Apr 20;7(8):
pubmed: 28713848
J Exp Med. 2008 Aug 4;205(8):1869-77
pubmed: 18625748
J Neurochem. 2008 Jan;104(2):420-34
pubmed: 17953654
Neurochem Int. 2009 Nov;55(6):431-7
pubmed: 19410615

Auteurs

Debashis Dutta (D)

Department of Neurological Sciences, Rush University Medical Center, Chicago, USA.

Moumita Majumder (M)

Department of Neurological Sciences, Rush University Medical Center, Chicago, USA.

Ramesh Kumar Paidi (RK)

Department of Neurological Sciences, Rush University Medical Center, Chicago, USA.

Kalipada Pahan (K)

Department of Neurological Sciences, Rush University Medical Center, Chicago, USA; Division of Research and Development, Jesse Brown Veterans Affairs Medical Center, Chicago, USA. Electronic address: Kalipada_Pahan@rush.edu.

Articles similaires

[Redispensing of expensive oral anticancer medicines: a practical application].

Lisanne N van Merendonk, Kübra Akgöl, Bastiaan Nuijen
1.00
Humans Antineoplastic Agents Administration, Oral Drug Costs Counterfeit Drugs

Smoking Cessation and Incident Cardiovascular Disease.

Jun Hwan Cho, Seung Yong Shin, Hoseob Kim et al.
1.00
Humans Male Smoking Cessation Cardiovascular Diseases Female
Humans United States Aged Cross-Sectional Studies Medicare Part C
1.00
Humans Yoga Low Back Pain Female Male

Classifications MeSH