Dysregulation of myelin synthesis and actomyosin function underlies aberrant myelin in CMT4B1 neuropathy.


Journal

Proceedings of the National Academy of Sciences of the United States of America
ISSN: 1091-6490
Titre abrégé: Proc Natl Acad Sci U S A
Pays: United States
ID NLM: 7505876

Informations de publication

Date de publication:
09 03 2021
Historique:
entrez: 3 3 2021
pubmed: 4 3 2021
medline: 17 8 2021
Statut: ppublish

Résumé

Charcot-Marie-Tooth type 4B1 (CMT4B1) is a severe autosomal recessive demyelinating neuropathy with childhood onset, caused by loss-of-function mutations in the myotubularin-related 2 (

Identifiants

pubmed: 33653949
pii: 2009469118
doi: 10.1073/pnas.2009469118
pmc: PMC7958260
pii:
doi:

Substances chimiques

Phosphatidylinositol Phosphates 0
phosphatidylinositol 3,5-diphosphate 0
Mechanistic Target of Rapamycin Complex 1 EC 2.7.11.1
Mtmr2 protein, mouse EC 3.1.3.48
Protein Tyrosine Phosphatases, Non-Receptor EC 3.1.3.48
Myosin Type II EC 3.6.1.-
RhoA protein, mouse EC 3.6.5.2
rhoA GTP-Binding Protein EC 3.6.5.2

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Déclaration de conflit d'intérêts

The authors declare no competing interest.

Références

Proc Natl Acad Sci U S A. 2017 May 23;114(21):E4261-E4270
pubmed: 28484008
J Proteome Res. 2008 Dec;7(12):5295-313
pubmed: 19367725
Expert Rev Mol Med. 2007 Sep 20;9(25):1-16
pubmed: 17880751
Nature. 2006 Oct 12;443(7112):651-7
pubmed: 17035995
PLoS Genet. 2011 Oct;7(10):e1002319
pubmed: 22028665
Hum Mol Genet. 2006 Feb 15;15(4):569-79
pubmed: 16399794
Hum Mol Genet. 2002 Jun 15;11(13):1569-79
pubmed: 12045210
J Biol Chem. 2010 Dec 3;285(49):38362-73
pubmed: 20937815
Hum Mol Genet. 2005 Dec 1;14(23):3685-95
pubmed: 16249189
Cancer Res. 2011 May 1;71(9):3246-56
pubmed: 21430067
Trends Mol Med. 2012 Jun;18(6):317-27
pubmed: 22578719
Chem Biol. 2013 Jul 25;20(7):912-21
pubmed: 23890009
Proc Natl Acad Sci U S A. 2003 Oct 14;100(21):12177-82
pubmed: 14530412
Neuron. 2003 Oct 9;40(2):297-318
pubmed: 14556710
Cold Spring Harb Perspect Biol. 2015 Aug 03;7(8):a005959
pubmed: 26238352
Proc Natl Acad Sci U S A. 2008 Mar 25;105(12):4916-21
pubmed: 18349142
Mol Biol Cell. 2012 Aug;23(15):2955-62
pubmed: 22696681
Cell Struct Funct. 2017 May 3;42(1):49-60
pubmed: 28302928
J Peripher Nerv Syst. 2015 Mar;20(1):52-9
pubmed: 25676889
J Cell Biol. 2008 Sep 22;182(6):1171-84
pubmed: 18794332
J Biol Chem. 2011 Aug 26;286(34):29511-20
pubmed: 21719701
Brain. 2012 Dec;135(Pt 12):3567-83
pubmed: 23171661
Dev Cell. 2010 Dec 14;19(6):845-57
pubmed: 21145500
J Neurosci. 2016 Apr 20;36(16):4506-21
pubmed: 27098694
J Biol Chem. 2005 Sep 9;280(36):31699-707
pubmed: 15998640
Glia. 2018 Apr;66(4):693-707
pubmed: 29210103
Lancet Neurol. 2009 Jul;8(7):654-67
pubmed: 19539237
Elife. 2017 Sep 07;6:
pubmed: 28880149
EMBO J. 2016 Mar 15;35(6):561-79
pubmed: 26888746
Mol Cell Neurosci. 2007 May;35(1):120-9
pubmed: 17382558
Methods Mol Biol. 2004;273:201-12
pubmed: 15308803
Front Cell Neurosci. 2018 Jan 05;11:414
pubmed: 29354031
Dis Model Mech. 2015 Dec;8(12):1495-515
pubmed: 26542704
Dev Cell. 2015 Jul 27;34(2):152-67
pubmed: 26166300
Neurology. 2013 Jul 9;81(2):165-73
pubmed: 23749797
Methods Mol Biol. 2018;1791:115-129
pubmed: 30006705
J Cell Sci. 2015 Jan 15;128(2):207-17
pubmed: 25568150
Am J Hum Genet. 2003 May;72(5):1141-53
pubmed: 12687498
Oncogene. 2006 Nov 9;25(53):7029-40
pubmed: 16715128
Blood. 2017 Mar 30;129(13):1768-1778
pubmed: 28104689
J Neurosci. 2009 Jul 8;29(27):8858-70
pubmed: 19587293
Curr Opin Neurol. 2016 Oct;29(5):537-48
pubmed: 27584852
Dev Cell. 2015 Jul 27;34(2):139-151
pubmed: 26166299
Nat Genet. 2000 May;25(1):17-9
pubmed: 10802647
Nat Commun. 2020 Jun 5;11(1):2835
pubmed: 32503983
Hum Mol Genet. 2007 Dec 15;16(24):2991-3001
pubmed: 17855448
Biochimie. 2016 Jun;125:250-8
pubmed: 26391221
J Neurosci. 2013 Jul 3;33(27):10950-61
pubmed: 23825401
Ann Neurol. 2019 Jul;86(1):55-67
pubmed: 31070812
J Neurosci. 2005 Sep 14;25(37):8567-77
pubmed: 16162938
Adv Biol Regul. 2017 Jan;63:49-58
pubmed: 27666502
Glia. 2013 Nov;61(11):1906-21
pubmed: 24014231
J Cell Biol. 2011 Jan 24;192(2):243-50
pubmed: 21263026
J Cell Biol. 2002 Oct 28;159(2):361-72
pubmed: 12403818
J Neurosci. 2004 Apr 21;24(16):3953-63
pubmed: 15102911
EMBO Mol Med. 2012 Jun;4(6):486-99
pubmed: 22488882
J Cell Biol. 2009 Apr 6;185(1):147-61
pubmed: 19349584
J Cell Biol. 2004 Nov 22;167(4):711-21
pubmed: 15557122
J Neurosci. 1997 Jun 15;17(12):4662-71
pubmed: 9169527
Hum Mol Genet. 2003 Feb 1;12(3):349-56
pubmed: 12554688
Nature. 2018 Jun;558(7711):540-546
pubmed: 29899452
Curr Opin Neurol. 2015 Oct;28(5):462-7
pubmed: 26263471
Exp Cell Res. 2017 Sep 1;358(1):20-30
pubmed: 28363828
Proc Natl Acad Sci U S A. 2011 Oct 25;108(43):E952-61
pubmed: 21949390
Hum Mol Genet. 2017 Oct 1;26(19):3736-3748
pubmed: 28934386
Dev Growth Differ. 2017 Jun;59(5):340-350
pubmed: 28573735
Curr Biol. 2004 Jul 27;14(14):1296-302
pubmed: 15268862

Auteurs

Marta Guerrero-Valero (M)

Human Inherited Neuropathies Unit, Institute of Experimental Neurology (INSPE) and Division of Neuroscience, Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS) Ospedale San Raffaele, 20132 Milan, Italy.

Federica Grandi (F)

Human Inherited Neuropathies Unit, Institute of Experimental Neurology (INSPE) and Division of Neuroscience, Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS) Ospedale San Raffaele, 20132 Milan, Italy.

Silvia Cipriani (S)

Human Inherited Neuropathies Unit, Institute of Experimental Neurology (INSPE) and Division of Neuroscience, Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS) Ospedale San Raffaele, 20132 Milan, Italy.

Valeria Alberizzi (V)

Human Inherited Neuropathies Unit, Institute of Experimental Neurology (INSPE) and Division of Neuroscience, Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS) Ospedale San Raffaele, 20132 Milan, Italy.

Roberta Di Guardo (R)

Human Inherited Neuropathies Unit, Institute of Experimental Neurology (INSPE) and Division of Neuroscience, Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS) Ospedale San Raffaele, 20132 Milan, Italy.

Gaetan Chicanne (G)

Inserm UMR-1048, I2MC, Université Toulouse 3 Paul Sabatier, 31432 Toulouse, France.

Linda Sawade (L)

Department of Molecular Pharmacology and Cell Biology, Leibniz-Forschungsinstitut für Molekulare Pharmakologie, 13125 Berlin, Germany.

Francesca Bianchi (F)

Department of Neurology, IRCCS Ospedale San Raffaele, 20132 Milan, Italy.

Ubaldo Del Carro (U)

Department of Neurology, IRCCS Ospedale San Raffaele, 20132 Milan, Italy.

Ivan De Curtis (I)

Cell Adhesion Unit, Division of Neuroscience, IRCCS Ospedale San Raffaele, 20132 Milan, Italy.

Davide Pareyson (D)

Unit of Rare Neurodegenerative and Neurometabolic Diseases, Department of Clinical Neurosciences, Fondazione IRCCS Istituto Neurologico Carlo Besta, 20133 Milan, Italy.

Yesim Parman (Y)

Istanbul Faculty of Medicine, Neurology Department, Istanbul University, 34390 Istanbul, Turkey.

Angelo Schenone (A)

Department of Neurosciences, Rehabilitation, Ophthalmology, Genetic and Maternal Infantile Sciences, IRCCS Policlinico San Martino, University of Genoa, 16132 Genoa, Italy.

Volker Haucke (V)

Department of Molecular Pharmacology and Cell Biology, Leibniz-Forschungsinstitut für Molekulare Pharmakologie, 13125 Berlin, Germany.

Bernard Payrastre (B)

Inserm UMR-1048, I2MC, Université Toulouse 3 Paul Sabatier, 31432 Toulouse, France.

Alessandra Bolino (A)

Human Inherited Neuropathies Unit, Institute of Experimental Neurology (INSPE) and Division of Neuroscience, Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS) Ospedale San Raffaele, 20132 Milan, Italy; bolino.alessandra@hsr.it.

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