Discovery of CYR715: A novel carboxylic acid-containing soluble guanylate cyclase stimulator.


Journal

Bioorganic & medicinal chemistry letters
ISSN: 1464-3405
Titre abrégé: Bioorg Med Chem Lett
Pays: England
ID NLM: 9107377

Informations de publication

Date de publication:
15 05 2021
Historique:
received: 10 09 2020
revised: 09 02 2021
accepted: 10 02 2021
pubmed: 5 3 2021
medline: 16 9 2021
entrez: 4 3 2021
Statut: ppublish

Résumé

Soluble guanylate cyclase (sGC) is a clinically validated therapeutic target in the treatment of pulmonary hypertension. Modulators of sGC have the potential to treat diseases that are affected by dysregulation of the NO-sGC-cGMP signal transduction pathway. This letter describes the SAR efforts that led to the discovery of CYR715, a novel carboxylic acid-containing sGC stimulator, with an improved metabolic profile relative to our previously described stimulator, IWP-051. CYR715 addressed potential idiosyncratic drug toxicity (IDT) liabilities associated with the formation of reactive, migrating acyl glucuronides (AG) found in related carboxylic acid-containing analogs and demonstrated high oral bioavailability in rat and dose-dependent hemodynamic pharmacology in normotensive Sprague-Dawley rats.

Identifiants

pubmed: 33662540
pii: S0960-894X(21)00112-8
doi: 10.1016/j.bmcl.2021.127886
pii:
doi:

Substances chimiques

Carboxylic Acids 0
Glucuronides 0
Vasodilator Agents 0
Nitric Oxide 31C4KY9ESH
Soluble Guanylyl Cyclase EC 4.6.1.2

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

127886

Informations de copyright

Copyright © 2021 Elsevier Ltd. All rights reserved.

Auteurs

Glen R Rennie (GR)

Cyclerion Therapeutics, Inc., 301 Binney Street Cambridge, MA 02142, United States.

Timothy C Barden (TC)

Cyclerion Therapeutics, Inc., 301 Binney Street Cambridge, MA 02142, United States.

Sylvie G Bernier (SG)

Cyclerion Therapeutics, Inc., 301 Binney Street Cambridge, MA 02142, United States.

Andrew Carvalho (A)

Cyclerion Therapeutics, Inc., 301 Binney Street Cambridge, MA 02142, United States.

Renee Deming (R)

Cyclerion Therapeutics, Inc., 301 Binney Street Cambridge, MA 02142, United States.

Peter Germano (P)

Cyclerion Therapeutics, Inc., 301 Binney Street Cambridge, MA 02142, United States.

Colleen Hudson (C)

Cyclerion Therapeutics, Inc., 301 Binney Street Cambridge, MA 02142, United States.

G-Yoon J Im (GJ)

Cyclerion Therapeutics, Inc., 301 Binney Street Cambridge, MA 02142, United States.

Rajesh R Iyengar (RR)

Cyclerion Therapeutics, Inc., 301 Binney Street Cambridge, MA 02142, United States.

Lei Jia (L)

Cyclerion Therapeutics, Inc., 301 Binney Street Cambridge, MA 02142, United States.

Joon Jung (J)

Cyclerion Therapeutics, Inc., 301 Binney Street Cambridge, MA 02142, United States.

Elise Kim (E)

Cyclerion Therapeutics, Inc., 301 Binney Street Cambridge, MA 02142, United States.

Thomas W-H Lee (TW)

Cyclerion Therapeutics, Inc., 301 Binney Street Cambridge, MA 02142, United States.

Ara Mermerian (A)

Cyclerion Therapeutics, Inc., 301 Binney Street Cambridge, MA 02142, United States.

Joel Moore (J)

Cyclerion Therapeutics, Inc., 301 Binney Street Cambridge, MA 02142, United States.

Takashi Nakai (T)

Cyclerion Therapeutics, Inc., 301 Binney Street Cambridge, MA 02142, United States.

Nicholas R Perl (NR)

Cyclerion Therapeutics, Inc., 301 Binney Street Cambridge, MA 02142, United States.

Jenny Tobin (J)

Cyclerion Therapeutics, Inc., 301 Binney Street Cambridge, MA 02142, United States.

Daniel P Zimmer (DP)

Cyclerion Therapeutics, Inc., 301 Binney Street Cambridge, MA 02142, United States.

Paul A Renhowe (PA)

Cyclerion Therapeutics, Inc., 301 Binney Street Cambridge, MA 02142, United States. Electronic address: prenhowe@gmail.com.

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Classifications MeSH