A novel JAK/ROCK inhibitor, CPL409116, demonstrates potent efficacy in the mouse model of systemic lupus erythematosus.


Journal

Journal of pharmacological sciences
ISSN: 1347-8648
Titre abrégé: J Pharmacol Sci
Pays: Japan
ID NLM: 101167001

Informations de publication

Date de publication:
Apr 2021
Historique:
received: 13 10 2020
revised: 20 01 2021
accepted: 01 02 2021
entrez: 13 3 2021
pubmed: 14 3 2021
medline: 11 9 2021
Statut: ppublish

Résumé

Systemic lupus erythematosus is a chronic inflammatory disease, in which treatment is still limited due to suboptimal efficacy and toxicities associated with the available therapies. JAK kinases are well known to play an important role in systemic lupus erythematous. There is growing evidence that ROCK kinases are also important in disease development. In this paper, we present the results of the development of CPL409116, a dual JAK and ROCK inhibitor. The studies we performed demonstrate that this molecule is an effective JAK and ROCK inhibitor which efficiently blocks disease progression in NZBWF1/J mouse models of systemic lupus erythematous.

Identifiants

pubmed: 33712286
pii: S1347-8613(21)00013-X
doi: 10.1016/j.jphs.2021.02.002
pii:
doi:

Substances chimiques

Janus Kinase Inhibitors 0
Piperidines 0
Pyrimidines 0
tofacitinib 87LA6FU830
Janus Kinases EC 2.7.10.2
rho-Associated Kinases EC 2.7.11.1

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

340-348

Informations de copyright

Copyright © 2021 The Authors. Production and hosting by Elsevier B.V. All rights reserved.

Déclaration de conflit d'intérêts

Declaration of competing interest All authors of this paper were employees of Celon Pharma S.A. MW and JSP owns stocks of Celon Pharma S.A.

Auteurs

Maria Dulak-Lis (M)

Celon Pharma S.A., Preclinical Department, Mokra 41a, Kiełpin, 05-092, Łomianki, Poland.

Anna Bujak (A)

Celon Pharma S.A., Preclinical Department, Mokra 41a, Kiełpin, 05-092, Łomianki, Poland.

Kamila Gala (K)

Celon Pharma S.A., Preclinical Department, Mokra 41a, Kiełpin, 05-092, Łomianki, Poland.

Martyna Banach (M)

Celon Pharma S.A., Preclinical Department, Mokra 41a, Kiełpin, 05-092, Łomianki, Poland.

Urszula Kędzierska (U)

Celon Pharma S.A., Preclinical Department, Mokra 41a, Kiełpin, 05-092, Łomianki, Poland.

Joanna Miszkiel (J)

Celon Pharma S.A., Preclinical Department, Mokra 41a, Kiełpin, 05-092, Łomianki, Poland.

Joanna Hucz-Kalitowska (J)

Celon Pharma S.A., Preclinical Department, Mokra 41a, Kiełpin, 05-092, Łomianki, Poland.

Michał Mroczkiewicz (M)

Celon Pharma S.A., Medicinal Chemistry Department, Mokra 41a, Kiełpin, 05-092, Łomianki, Poland.

Bartosz Stypik (B)

Celon Pharma S.A., Medicinal Chemistry Department, Mokra 41a, Kiełpin, 05-092, Łomianki, Poland.

Krzysztof Szymczak (K)

Celon Pharma S.A., Medicinal Chemistry Department, Mokra 41a, Kiełpin, 05-092, Łomianki, Poland.

Paweł Gunerka (P)

Celon Pharma S.A., Preclinical Department, Mokra 41a, Kiełpin, 05-092, Łomianki, Poland.

Krzysztof Dubiel (K)

Celon Pharma S.A., Medicinal Chemistry Department, Mokra 41a, Kiełpin, 05-092, Łomianki, Poland.

Beata M Zygmunt (BM)

Celon Pharma S.A., Preclinical Department, Mokra 41a, Kiełpin, 05-092, Łomianki, Poland. Electronic address: beata.zygmunt@celonpharma.com.

Maciej Wieczorek (M)

Celon Pharma S.A., Preclinical Department, Mokra 41a, Kiełpin, 05-092, Łomianki, Poland.

Jerzy S Pieczykolan (JS)

Celon Pharma S.A., Preclinical Department, Mokra 41a, Kiełpin, 05-092, Łomianki, Poland.

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Classifications MeSH