A Role for Vasoactive Intestinal Peptide Interneurons in Neurodevelopmental Disorders.


Journal

Developmental neuroscience
ISSN: 1421-9859
Titre abrégé: Dev Neurosci
Pays: Switzerland
ID NLM: 7809375

Informations de publication

Date de publication:
2021
Historique:
received: 15 12 2020
accepted: 10 02 2021
pubmed: 2 4 2021
medline: 28 1 2022
entrez: 1 4 2021
Statut: ppublish

Résumé

GABAergic inhibitory interneurons of the cerebral cortex expressing vasoactive intestinal peptide (VIP-INs) are rapidly emerging as important regulators of network dynamics and normal circuit development. Several recent studies have also identified VIP-IN dysfunction in models of genetically determined neurodevelopmental disorders (NDDs). In this article, we review the known circuit functions of VIP-INs and how they may relate to accumulating evidence implicating VIP-INs in the mechanisms of prominent NDDs. We highlight recurring VIP-IN-mediated circuit motifs that are shared across cerebral cortical areas and how VIP-IN activity can shape sensory input, development, and behavior. Ultimately, we extract a set of themes that inform our understanding of how VIP-INs influence pathogenesis of NDDs. Using publicly available single-cell RNA sequencing data from the Allen Institute, we also identify several underexplored disease-associated genes that are highly expressed in VIP-INs. We survey these genes and their shared related disease phenotypes that may broadly implicate VIP-INs in autism spectrum disorder and intellectual disability rather than epileptic encephalopathy. Finally, we conclude with a discussion of the relevance of cell type-specific investigations and therapeutics in the age of genomic diagnosis and targeted therapeutics.

Identifiants

pubmed: 33794534
pii: 000515264
doi: 10.1159/000515264
pmc: PMC8440337
mid: NIHMS1676689
doi:

Substances chimiques

Vasoactive Intestinal Peptide 37221-79-7

Types de publication

Journal Article Research Support, N.I.H., Extramural Research Support, Non-U.S. Gov't Review

Langues

eng

Sous-ensembles de citation

IM

Pagination

168-180

Subventions

Organisme : NINDS NIH HHS
ID : F31 NS111803
Pays : United States
Organisme : NINDS NIH HHS
ID : K08 NS097633
Pays : United States
Organisme : NINDS NIH HHS
ID : R01 NS110869
Pays : United States

Informations de copyright

© 2021 S. Karger AG, Basel.

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Auteurs

Kevin M Goff (KM)

Medical Scientist Training Program (MSTP), The University of Pennsylvania Perelman School of Medicine, Philadelphia, Pennsylvania, USA.
Neuroscience Graduate Group, The University of Pennsylvania Perelman School of Medicine, Philadelphia, Pennsylvania, USA.

Ethan M Goldberg (EM)

Neuroscience Graduate Group, The University of Pennsylvania Perelman School of Medicine, Philadelphia, Pennsylvania, USA.
Division of Neurology, Department of Pediatrics, The Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, USA.
The Epilepsy NeuroGenetics Initiative, The Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, USA.
Departments of Neurology, The University of Pennsylvania Perelman School of Medicine, Philadelphia, Pennsylvania, USA.
Departments of Neuroscience, The University of Pennsylvania Perelman School of Medicine, Philadelphia, Pennsylvania, USA.

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