Modified RANO, Immunotherapy RANO, and Standard RANO Response to Convection-Enhanced Delivery of IL4R-Targeted Immunotoxin MDNA55 in Recurrent Glioblastoma.


Journal

Clinical cancer research : an official journal of the American Association for Cancer Research
ISSN: 1557-3265
Titre abrégé: Clin Cancer Res
Pays: United States
ID NLM: 9502500

Informations de publication

Date de publication:
15 07 2021
Historique:
received: 03 02 2021
revised: 16 03 2021
accepted: 13 04 2021
pubmed: 18 4 2021
medline: 1 4 2022
entrez: 17 4 2021
Statut: ppublish

Résumé

The current study compared the standard response assessment in neuro-oncology (RANO), immunotherapy RANO (iRANO), and modified RANO (mRANO) criteria as well as quantified the association between progression-free (PFS) and overall survival (OS) in an immunotherapy trial in recurrent glioblastoma (rGBM). A total of 47 patients with rGBM were enrolled in a prospective phase II convection-enhanced delivery of an IL4R-targeted immunotoxin (MDNA55-05, NCT02858895). Bidirectional tumor measurements were created by local sites and centrally by an independent radiologic faculty, then standard RANO, iRANO, and mRANO criteria were applied. A total of 41 of 47 patients (mean age 56 ± 11.7) were evaluable for response. PFS was significantly shorter using standard RANO compared with iRANO (log-rank, No correlation between radiographic PFS and OS was observed for standard RANO or iRANO, but a correlation was observed between PFS and OS using the mRANO criteria. Also, the iRANO criteria was difficult to implement due to need to confirm progression 3 months after initial progression, censoring more than half the patients.

Identifiants

pubmed: 33863808
pii: 1078-0432.CCR-21-0446
doi: 10.1158/1078-0432.CCR-21-0446
pmc: PMC8282697
mid: NIHMS1696668
doi:

Substances chimiques

IL4R protein, human 0
Immunotoxins 0
Interleukin-4 Receptor alpha Subunit 0

Banques de données

ClinicalTrials.gov
['NCT02858895']

Types de publication

Clinical Trial, Phase II Comparative Study Journal Article Research Support, N.I.H., Extramural Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

3916-3925

Subventions

Organisme : NCI NIH HHS
ID : R21 CA223757
Pays : United States
Organisme : NCI NIH HHS
ID : P50 CA211015
Pays : United States
Organisme : EPA
ID : EP-C-15-003
Pays : United States
Organisme : NCI NIH HHS
ID : R01 CA227136
Pays : United States
Organisme : NINDS NIH HHS
ID : R01 NS079697
Pays : United States

Informations de copyright

©2021 American Association for Cancer Research.

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Auteurs

Benjamin M Ellingson (BM)

UCLA Brain Tumor Imaging Laboratory (BTIL), Center for Computer Vision and Imaging Biomarkers, David Geffen School of Medicine, University of California Los Angeles, Los Angeles, California. bellingson@mednet.ucla.edu.
Department of Radiological Sciences, David Geffen School of Medicine, University of California Los Angeles, Los Angeles, California.
UCLA Neuro Oncology Program, David Geffen School of Medicine, University of California Los Angeles, Los Angeles, California.

John Sampson (J)

Department of Neurosurgery, Duke University Medical Center, Durham, North Carolina.

Achal Singh Achrol (AS)

Department of Neurosurgery, Loma Linda University Medical Center, Loma Linda, California.
Department of Translational Neurosciences and Neurotherapeutics, Pacific Neurosciences Institute, Santa Monica, California.

Manish K Aghi (MK)

Department of Neurological Surgery, University of California San Francisco, San Francisco, California.

Krystof Bankiewicz (K)

Department of Neurological Surgery, Ohio State University College of Medicine, Columbus, Ohio.
Department of Neurosurgery, Mazovian Brodnowski Hospital, Warsaw, Poland.

Chencai Wang (C)

UCLA Brain Tumor Imaging Laboratory (BTIL), Center for Computer Vision and Imaging Biomarkers, David Geffen School of Medicine, University of California Los Angeles, Los Angeles, California.
Department of Radiological Sciences, David Geffen School of Medicine, University of California Los Angeles, Los Angeles, California.

Martin Bexon (M)

Medicenna BioPharma, Houston, Texas.

Steven Brem (S)

Department of Neurosurgery, Glioblastoma Translational Center of Excellence, Penn Brain Tumor Center, Abramson Cancer Center, University of Pennsylvania, Philadelphia, Pennsylvania.

Andrew Brenner (A)

University of Texas Health Science Center at San Antonio, San Antonio, Texas.

Sajeel Chowdhary (S)

Marcus Neuroscience Institute and Neuro-Oncology Program, Boca Raton Regional Hospital, Boca Raton, Florida.

John R Floyd (JR)

University of Texas Health Science Center at San Antonio, San Antonio, Texas.

Seunggu Han (S)

Department of Neurological Surgery, Oregon Health & Science University, Portland, Oregon.

Santosh Kesari (S)

Department of Translational Neurosciences and Neurotherapeutics, Pacific Neurosciences Institute, Santa Monica, California.

Dina Randazzo (D)

Department of Neurosurgery, Duke University Medical Center, Durham, North Carolina.

Michael A Vogelbaum (MA)

Department of Neuro-Oncology, H. Lee Moffitt Cancer Center & Research Institute, Tampa, Florida.

Frank Vrionis (F)

Marcus Neuroscience Institute and Neuro-Oncology Program, Boca Raton Regional Hospital, Boca Raton, Florida.

Miroslaw Zabek (M)

Department of Neurosurgery, Mazovian Brodnowski Hospital, Warsaw, Poland.

Nicholas Butowski (N)

Department of Neurological Surgery, University of California San Francisco, San Francisco, California.

Melissa Coello (M)

Medicenna BioPharma, Houston, Texas.

Nina Merchant (N)

Medicenna BioPharma, Houston, Texas.

Fahar Merchant (F)

Medicenna BioPharma, Houston, Texas.

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