Expanding the genotypic spectrum of


Journal

Cold Spring Harbor molecular case studies
ISSN: 2373-2873
Titre abrégé: Cold Spring Harb Mol Case Stud
Pays: United States
ID NLM: 101660017

Informations de publication

Date de publication:
06 2021
Historique:
received: 11 01 2021
accepted: 30 03 2021
pubmed: 23 4 2021
medline: 15 12 2021
entrez: 22 4 2021
Statut: epublish

Résumé

Visceral myopathies (VMs) encompass a spectrum of disorders characterized by chronic disruption of gastrointestinal function, with or without urinary system involvement. Pathogenic missense variation in smooth muscle γ-actin gene (

Identifiants

pubmed: 33883208
pii: mcs.a006085
doi: 10.1101/mcs.a006085
pmc: PMC8208046
pii:
doi:

Substances chimiques

ACTG2 protein, human 0
Actins 0

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Informations de copyright

© 2021 James et al.; Published by Cold Spring Harbor Laboratory Press.

Références

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Auteurs

Kiely N James (KN)

Rady Children's Institute for Genomic Medicine, San Diego, California 92123, USA.

Megan Lau (M)

UC San Diego School of Medicine, La Jolla, California 92093, USA.

Katayoon Shayan (K)

Pathology Department, Hepatology and Nutrition, Rady Children's Hospital, San Diego, California 92123, USA.

Jerica Lenberg (J)

Rady Children's Institute for Genomic Medicine, San Diego, California 92123, USA.

Rebecca Mardach (R)

Rady Children's Institute for Genomic Medicine, San Diego, California 92123, USA.

Romeo Ignacio (R)

Division of Pediatric Surgery, Hepatology and Nutrition, Rady Children's Hospital, San Diego, California 92123, USA.

Jonathan Halbach (J)

Division of Pediatric Surgery, Hepatology and Nutrition, Rady Children's Hospital, San Diego, California 92123, USA.

Lillian Choi (L)

Division of Gastroenterology, Hepatology and Nutrition, Rady Children's Hospital, San Diego, California 92123, USA.

Soma Kumar (S)

Division of Gastroenterology, Hepatology and Nutrition, Rady Children's Hospital, San Diego, California 92123, USA.

Katarzyna A Ellsworth (KA)

Rady Children's Institute for Genomic Medicine, San Diego, California 92123, USA.

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Classifications MeSH