BTK inhibition sensitizes acute lymphoblastic leukemia to asparaginase by suppressing the amino acid response pathway.


Journal

Blood
ISSN: 1528-0020
Titre abrégé: Blood
Pays: United States
ID NLM: 7603509

Informations de publication

Date de publication:
09 12 2021
Historique:
received: 19 03 2021
accepted: 02 07 2021
pubmed: 20 7 2021
medline: 4 1 2022
entrez: 19 7 2021
Statut: ppublish

Résumé

Asparaginase (ASNase) therapy has been a mainstay of acute lymphoblastic leukemia (ALL) protocols for decades and shows promise in the treatment of a variety of other cancers. To improve the efficacy of ASNase treatment, we used a CRISPR/Cas9-based screen to identify actionable signaling intermediates that improve the response to ASNase. Both genetic inactivation of Bruton's tyrosine kinase (BTK) and pharmacological inhibition by the BTK inhibitor ibrutinib strongly synergize with ASNase by inhibiting the amino acid response pathway, a mechanism involving c-Myc-mediated suppression of GCN2 activity. This synthetic lethal interaction was observed in 90% of patient-derived xenografts, regardless of the genomic subtype. Moreover, ibrutinib substantially improved ASNase treatment response in a murine PDX model. Hence, ibrutinib may be used to enhance the clinical efficacy of ASNase in ALL. This trial was registered at www.clinicaltrials.gov as # NCT02884453.

Identifiants

pubmed: 34280258
pii: S0006-4971(21)01372-0
doi: 10.1182/blood.2021011787
pmc: PMC8832462
doi:

Substances chimiques

Amino Acids 0
Antineoplastic Agents 0
Piperidines 0
ibrutinib 1X70OSD4VX
Agammaglobulinaemia Tyrosine Kinase EC 2.7.10.2
Asparaginase EC 3.5.1.1
Adenine JAC85A2161

Banques de données

ClinicalTrials.gov
['NCT02884453']

Types de publication

Clinical Trial Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

2383-2395

Informations de copyright

© 2021 by The American Society of Hematology.

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Auteurs

Miriam Butler (M)

Princess Maxima Center for Pediatric Oncology, Utrecht, The Netherlands.
Laboratory of Pediatric Oncology, Department of Pediatrics, and.

Dorette S van Ingen Schenau (DS)

Princess Maxima Center for Pediatric Oncology, Utrecht, The Netherlands.

Jiangyan Yu (J)

Princess Maxima Center for Pediatric Oncology, Utrecht, The Netherlands.
Department of Human Genetics, Radboud Institute for Molecular Life Sciences, Radboud University Medical Center, Nijmegen, The Netherlands Radboud University Medical Center, Nijmegen, The Netherlands.

Silvia Jenni (S)

Department of Pediatric Oncology, Children's Research Centre, University Children's Hospital Zurich, Zurich, Switzerland.

Maria P Dobay (MP)

Department of Pediatric Oncology, Children's Research Centre, University Children's Hospital Zurich, Zurich, Switzerland.

Rico Hagelaar (R)

Princess Maxima Center for Pediatric Oncology, Utrecht, The Netherlands.

Britt M T Vervoort (BMT)

Princess Maxima Center for Pediatric Oncology, Utrecht, The Netherlands.

Trisha M Tee (TM)

Princess Maxima Center for Pediatric Oncology, Utrecht, The Netherlands.

Fieke W Hoff (FW)

Department of Leukemia and Department of Stem Cell Transplantation and Cellular Therapy, MD Anderson Cancer Center, Houston, TX.
Department of Pediatric Oncology/Hematology, Beatrix Children's Hospital University Medical Center Groningen, University of Groningen, Groningen, The Netherlands; and.

Jules P Meijerink (JP)

Princess Maxima Center for Pediatric Oncology, Utrecht, The Netherlands.

Steven M Kornblau (SM)

Department of Leukemia and Department of Stem Cell Transplantation and Cellular Therapy, MD Anderson Cancer Center, Houston, TX.

Beat Bornhauser (B)

Department of Pediatric Oncology, Children's Research Centre, University Children's Hospital Zurich, Zurich, Switzerland.

Jean-Pierre Bourquin (JP)

Department of Pediatric Oncology, Children's Research Centre, University Children's Hospital Zurich, Zurich, Switzerland.

Roland P Kuiper (RP)

Princess Maxima Center for Pediatric Oncology, Utrecht, The Netherlands.
Department of Genetics, University Medical Center Utrecht, Utrecht, The Netherlands.

Laurens T van der Meer (LT)

Princess Maxima Center for Pediatric Oncology, Utrecht, The Netherlands.

Frank N van Leeuwen (FN)

Princess Maxima Center for Pediatric Oncology, Utrecht, The Netherlands.

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Classifications MeSH