Evaluation of switch-mediated costimulation in trans on universal CAR-T cells (UniCAR) targeting CD123-positive AML.

4-1BB CD123 Chimeric antigen receptor (CAR) acute myeloid leukemia (AML) costimulation in trans switchable CAR platform

Journal

Oncoimmunology
ISSN: 2162-402X
Titre abrégé: Oncoimmunology
Pays: United States
ID NLM: 101570526

Informations de publication

Date de publication:
2021
Historique:
entrez: 22 7 2021
pubmed: 23 7 2021
medline: 3 8 2021
Statut: epublish

Résumé

Chimeric antigen receptor T cells (CAR-T) targeting CD19 have achieved significant success in patients with B cell malignancies. To date, implementation of CAR-T in other indications remains challenging due to the lack of truly tumor-specific antigens as well as control of CAR-T activity in patients. CD123 is highly expressed in acute myeloid leukemia (AML) blasts including leukemia-initiating cells making it an attractive immunotherapeutic target. However, CD123 expression in normal hematopoietic progenitor cells and endothelia bears the risk of severe toxicities and may limit CAR-T applications lacking fine-tuned control mechanisms. Therefore, we recently developed a rapidly switchable universal CAR-T platform (UniCAR), in which CAR-T activity depends on the presence of a soluble adapter called targeting module (TM), and confirmed clinical proof-of-concept for targeting CD123 in AML with improved safety. As costimulation via 4-1BB ligand (4-1BBL) can enhance CAR-T expansion, persistence, and effector functions, a novel CD123-specific TM variant (TM123-4-1BBL) comprising trimeric single-chain 4-1BBL was developed for transient costimulation of UniCAR-T cells (UniCAR-T) at the leukemic site

Identifiants

pubmed: 34290907
doi: 10.1080/2162402X.2021.1945804
pii: 1945804
pmc: PMC8274446
doi:

Substances chimiques

Antigens, Neoplasm 0
Interleukin-3 Receptor alpha Subunit 0

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

1945804

Informations de copyright

© 2021 The Author(s). Published with license by Taylor & Francis Group, LLC.

Déclaration de conflit d'intérêts

Conflict-of-interest-disclosure: GE and AE are shareholders of GEMoaB GmbH and CPT Cellex Patient Treatment GmbH. JEM, SL, JD, JS, GJJ, MC, and AE are employees at GEMoaB GmbH and/or its subsidiary company CPT Cellex Patient Treatment GmbH.

Références

Nat Biotechnol. 2017 Jan 10;35(1):6-7
pubmed: 28072774
J Clin Invest. 1993 Jun;91(6):2887-92
pubmed: 7685775
Oncotarget. 2017 Sep 18;8(65):108584-108603
pubmed: 29312553
Mol Ther. 2010 Apr;18(4):843-51
pubmed: 20179677
Leukemia. 2014 Jan;28(1):59-69
pubmed: 23958923
BioDrugs. 2015 Aug;29(4):215-39
pubmed: 26177629
Leuk Res. 2019 Sep;84:106178
pubmed: 31326578
Mol Ther. 2018 Apr 4;26(4):976-985
pubmed: 29503204
Sci Rep. 2017 Oct 30;7(1):14366
pubmed: 29085043
Leukemia. 2000 Oct;14(10):1777-84
pubmed: 11021753
N Engl J Med. 2018 Feb 1;378(5):439-448
pubmed: 29385370
Nat Med. 2015 Jun;21(6):581-90
pubmed: 25939063
Annu Rev Med. 2013;64:101-17
pubmed: 23121181
J Clin Invest. 2016 Oct 3;126(10):3814-3826
pubmed: 27571406
Blood. 1993 Aug 1;82(3):752-61
pubmed: 7687890
J Hematol Oncol. 2017 Jul 25;10(1):142
pubmed: 28743264
Transfus Med Hemother. 2019 Feb;46(1):15-24
pubmed: 31244578
Blood. 2013 Feb 14;121(7):1077-82
pubmed: 23243288
Mol Ther. 2009 Aug;17(8):1453-64
pubmed: 19384291
Mol Ther. 2017 Jan 4;25(1):285-295
pubmed: 28129122
Cancer Res. 2015 Sep 1;75(17):3505-18
pubmed: 26330164
Mol Ther. 2017 Aug 2;25(8):1933-1945
pubmed: 28479045
Nat Rev Clin Oncol. 2012 Oct;9(10):579-90
pubmed: 22949046
Blood Cancer J. 2014 Jun 13;4:e218
pubmed: 24927407
Blood. 2014 Apr 10;123(15):2343-54
pubmed: 24596416
Oncotarget. 2018 May 22;9(39):25597-25616
pubmed: 29876011
BMJ Open. 2020 Feb 9;10(2):e034629
pubmed: 32041862
J Immunother. 2012 Jun;35(5):418-29
pubmed: 22576347
Immunol Cell Biol. 1996 Feb;74(1):1-7
pubmed: 8934648
Proc Natl Acad Sci U S A. 2009 Mar 3;106(9):3360-5
pubmed: 19211796
J Clin Med. 2019 Feb 06;8(2):
pubmed: 30736352
Leukemia. 2018 May;32(5):1168-1179
pubmed: 29472720
Nat Med. 2019 Sep;25(9):1408-1414
pubmed: 31477906
Semin Oncol. 2015 Aug;42(4):640-55
pubmed: 26320067
Cell Stem Cell. 2009 Jul 2;5(1):31-42
pubmed: 19570512
Clin Cancer Res. 2019 Jul 1;25(13):4014-4025
pubmed: 30979735
Expert Opin Biol Ther. 2016 Jul;16(7):903-15
pubmed: 26967759
Best Pract Res Clin Haematol. 2019 Dec;32(4):101104
pubmed: 31779970
Ther Adv Hematol. 2019 Jul 10;10:2040620719860645
pubmed: 31321011
Onco Targets Ther. 2019 Jun 24;12:4907-4925
pubmed: 31417286
Sci Transl Med. 2015 May 27;7(289):289ra82
pubmed: 26019218
J Immunol. 2012 Sep 15;189(6):3249-59
pubmed: 22875801
N Engl J Med. 2017 Dec 28;377(26):2545-2554
pubmed: 29226764
N Engl J Med. 2019 Jan 3;380(1):45-56
pubmed: 30501490
Oncoimmunology. 2017 Jun 20;6(10):e1342909
pubmed: 29123951
Retrovirology. 2010 May 17;7:45
pubmed: 20478027
Mol Ther. 2018 Dec 5;26(12):2727-2737
pubmed: 30309819
Oncoimmunology. 2016 Sep 27;5(11):e1238540
pubmed: 27999756
Oncotarget. 2017 May 9;8(19):31368-31385
pubmed: 28404896
Oncotarget. 2017 Dec 21;9(7):7487-7500
pubmed: 29484126
Hemasphere. 2019 Feb 01;3(1):e172
pubmed: 31723811
Blood Cancer J. 2016 Aug 12;6(8):e458
pubmed: 27518241
Cancer Immunol Res. 2018 Jan;6(1):36-46
pubmed: 29180536
Blood. 2021 Jun 3;137(22):3145-3148
pubmed: 33624009
Cancer Cell. 2015 Oct 12;28(4):415-428
pubmed: 26461090
Cancer Immunol Immunother. 2010 Aug;59(8):1223-33
pubmed: 20336294
Clin Lymphoma Myeloma Leuk. 2020 Oct;20(10):e673-e684
pubmed: 32561191
Mol Ther Oncolytics. 2020 Apr 29;17:408-420
pubmed: 32462078
J Immunol. 2014 Jul 1;193(1):244-51
pubmed: 24860188
N Engl J Med. 2018 Feb 1;378(5):449-459
pubmed: 29385376
Cancers (Basel). 2019 Sep 12;11(9):
pubmed: 31547472
Blood. 2005 Dec 15;106(13):4086-92
pubmed: 16131573
N Engl J Med. 2017 Dec 28;377(26):2531-2544
pubmed: 29226797

Auteurs

Jan-Erik Meyer (JE)

GEMoaB GmbH, Dresden, Germany.

Simon Loff (S)

GEMoaB GmbH, Dresden, Germany.

Josephine Dietrich (J)

GEMoaB GmbH, Dresden, Germany.

Johannes Spehr (J)

GEMoaB GmbH, Dresden, Germany.

Gabriel Jurado Jiménez (G)

GEMoaB GmbH, Dresden, Germany.

Malte von Bonin (M)

Division of Hematology, Oncology and Stem Cell Transplantation, Medical Clinic I, Department of Medicine I, University Hospital Carl Gustav Carus, Technical University Dresden, Dresden, Germany.

Gerhard Ehninger (G)

GEMoaB GmbH, Dresden, Germany.

Marc Cartellieri (M)

GEMoaB GmbH, Dresden, Germany.

Armin Ehninger (A)

GEMoaB GmbH, Dresden, Germany.

Articles similaires

[Redispensing of expensive oral anticancer medicines: a practical application].

Lisanne N van Merendonk, Kübra Akgöl, Bastiaan Nuijen
1.00
Humans Antineoplastic Agents Administration, Oral Drug Costs Counterfeit Drugs

Smoking Cessation and Incident Cardiovascular Disease.

Jun Hwan Cho, Seung Yong Shin, Hoseob Kim et al.
1.00
Humans Male Smoking Cessation Cardiovascular Diseases Female
Humans United States Aged Cross-Sectional Studies Medicare Part C
1.00
Humans Yoga Low Back Pain Female Male

Classifications MeSH