Development of Randomized Trials in Adults with Medulloblastoma-The Example of EORTC 1634-BTG/NOA-23.

adult cerebrospinal fluid chemotherapy clinical trial magnetic resonance imaging medulloblastoma radiotherapy randomized subgrouping targeted therapy

Journal

Cancers
ISSN: 2072-6694
Titre abrégé: Cancers (Basel)
Pays: Switzerland
ID NLM: 101526829

Informations de publication

Date de publication:
09 Jul 2021
Historique:
received: 16 06 2021
revised: 07 07 2021
accepted: 08 07 2021
entrez: 24 7 2021
pubmed: 25 7 2021
medline: 25 7 2021
Statut: epublish

Résumé

Medulloblastoma is a rare brain malignancy. Patients after puberty are rare and bear an intermediate prognosis. Standard treatment consists of maximal resection plus radio-chemotherapy. Treatment toxicity is high and produces disabling long-term side effects. The sonic hedgehog (SHH) subgroup is highly overrepresented in the post-pubertal and adult population and can be targeted by smoothened (SMO) inhibitors. No practice-changing prospective randomized data have been generated in adults. The EORTC 1634-BTG/NOA-23 trial will randomize patients between standard-dose vs. reduced-dosed craniospinal radiotherapy and SHH-subgroup patients between the SMO inhibitor sonidegib (Odomzo

Identifiants

pubmed: 34298664
pii: cancers13143451
doi: 10.3390/cancers13143451
pmc: PMC8303185
pii:
doi:

Types de publication

Journal Article Review

Langues

eng

Subventions

Organisme : Deutsche Krebshilfe
ID : 70113453
Organisme : Cancer Australia
ID : 1165910
Organisme : CanTeen
ID : none
Organisme : KWF Kankerbestrijding
ID : 2021-1/13555
Organisme : Ministère des Affaires Sociales et de la Santé
ID : PHRC-K20-179
Organisme : Swiss Brain Tumor Foundation
ID : none
Organisme : EORTC Brain Tumor Group
ID : none
Organisme : Sun Pharmaceuticals Industries Ltd.
ID : none

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Auteurs

Peter Hau (P)

Wilhelm Sander-NeuroOncology Unit, Regensburg University Hospital, 93053 Regensburg, Germany.
Department of Neurology, Regensburg University Hospital, 93053 Regensburg, Germany.

Didier Frappaz (D)

Neuro-Oncology Unit, Centre Léon Bérard, 69008 Lyon, France.

Elizabeth Hovey (E)

Department of Medical Oncology, Sydney 2052, Australia.
Nelune Comprehensive Cancer Centre, Prince of Wales Cancer Centre, Sydney 2031, Australia.

Martin G McCabe (MG)

Faculty of Medicine, Biology and Health, University of Manchester, Manchester Academic Health Science Centre, Manchester M20 4GJ, UK.

Kristian W Pajtler (KW)

Hopp-Children's Cancer Center Heidelberg (KiTZ), Division of Pediatric Neurooncology, German Cancer Research Center (DKFZ), 69120 Heidelberg, Germany.
Department of Pediatric Hematology and Oncology, Heidelberg University Hospital, 69120 Heidelberg, Germany.

Benedikt Wiestler (B)

Department of Diagnostic and Interventional Neuroradiology, Klinikum Rechts der Isar der Technischen Universität München, TUM School of Medicine, 81675 Munich, Germany.

Clemens Seidel (C)

Department of Radiation-Oncology, University Hospital Leipzig, 04103 Leipzig, Germany.

Stephanie E Combs (SE)

Department of Radiation Oncology, Klinikum Rechts der Isar der Technischen Universität München, TUM School of Medicine, 81675 Munich, Germany.

Linda Dirven (L)

Department of Neurology, Leiden University Medical Center, 2300 RC Leiden, The Netherlands.
Department of Neurology, Haaglanden Medical Center, 2501 CK The Hague, The Netherlands.

Martin Klein (M)

Department of Medical Psychology, Amsterdam UMC, Vrije Universiteit Amsterdam, 1081 HV Amsterdam, The Netherlands.
Brain Tumor Center Amsterdam at Amsterdam UMC, Vrije Universiteit Amsterdam, 1081 HV Amsterdam, The Netherlands.

Antoinette Anazodo (A)

Nelune Comprehensive Cancer Centre, Prince of Wales Cancer Centre, Sydney 2031, Australia.
Kids Cancer Centre, Sydney Children's Hospital, Sydney 2031, Australia.
School of Women's and Children's Health, University of New South Wales, Sydney 2031, Australia.

Elke Hattingen (E)

Department of Neuroradiology, University Hospital Frankfurt, Goethe University, 60528 Frankfurt, Germany.

Silvia Hofer (S)

Department of Neurology, University Hospital Zurich, 8091 Zurich, Switzerland.

Stefan M Pfister (SM)

Hopp-Children's Cancer Center Heidelberg (KiTZ), Division of Pediatric Neurooncology, German Cancer Research Center (DKFZ), 69120 Heidelberg, Germany.
Department of Pediatric Hematology and Oncology, Heidelberg University Hospital, 69120 Heidelberg, Germany.

Claus Zimmer (C)

Department of Diagnostic and Interventional Neuroradiology, Klinikum Rechts der Isar der Technischen Universität München, TUM School of Medicine, 81675 Munich, Germany.

Rolf-Dieter Kortmann (RD)

Department of Radiation-Oncology, University Hospital Leipzig, 04103 Leipzig, Germany.

Marie-Pierre Sunyach (MP)

Department of Radiation Oncology, Centre Leon Berard, 69008 Lyon, France.

Ronan Tanguy (R)

Department of Radiation Oncology, Centre Leon Berard, 69008 Lyon, France.

Rachel Effeney (R)

Department of Radiation Oncology, Royal Brisbane and Women's Hospital, Brisbane 4029, Australia.

Andreas von Deimling (A)

Department of Neuropathology, University Hospital Heidelberg, 69120 Heidelberg, Germany.
Clinical Cooperation Unit Neuropathology, German Consortium for Translational Cancer Research (DKTK), German Cancer Research, 69120 Heidelberg, Germany.

Felix Sahm (F)

Department of Neuropathology, University Hospital Heidelberg, 69120 Heidelberg, Germany.
Clinical Cooperation Unit Neuropathology, German Consortium for Translational Cancer Research (DKTK), German Cancer Research, 69120 Heidelberg, Germany.

Stefan Rutkowski (S)

Department of Pediatric Hematology and Oncology, University Medical Center Hamburg-Eppendorf, 20246 Hamburg, Germany.

Anna S Berghoff (AS)

Division of Oncology, Department of Medicine I, Medical University of Vienna, 1090 Vienna, Austria.

Enrico Franceschi (E)

Medical Oncology Department, Azienda USL/IRCCS Institute of Neurological Sciences, 40139 Bologna, Italy.

Estela Pineda (E)

Barcelona Translational Genomics and Targeted Therapeutics in Solid Tumors Group, Department of Medical Oncology, Hospital Clinic Barcelona, 08036 Barcelona, Spain.

Dagmar Beier (D)

Department of Neurology, Odense University Hospital, DK-5000 Odense, Denmark.

Ellen Peeters (E)

EORTC Headquarters, 1200 Brussels, Belgium.

Thierry Gorlia (T)

EORTC Headquarters, 1200 Brussels, Belgium.

Maureen Vanlancker (M)

EORTC Headquarters, 1200 Brussels, Belgium.

Jacoline E C Bromberg (JEC)

Erasmus Medical Center Cancer Institute, Department of Neuro-Oncology, 3015 GD Rotterdam, The Netherlands.

Julien Gautier (J)

Clinical Research Department, Centre Léon Bérard, 69008 Lyon, France.

David S Ziegler (DS)

Kids Cancer Centre, Sydney Children's Hospital, Sydney 2031, Australia.
School of Women's and Children's Health, University of New South Wales, Sydney 2031, Australia.
Children's Cancer Institute, University of New South Wales, Sydney 2031, Australia.

Matthias Preusser (M)

Division of Oncology, Department of Medicine I, Medical University of Vienna, 1090 Vienna, Austria.

Wolfgang Wick (W)

Department of Neurology, University Hospital Heidelberg, 69120 Heidelberg, Germany.
Clinical Cooperation Unit Neuro-Oncology, German Consortium for Translational Cancer Research (DKTK), German Cancer Research, 69120 Heidelberg, Germany.

Michael Weller (M)

Department of Neurology, University Hospital Zurich, 8091 Zurich, Switzerland.

Classifications MeSH