An iPSC model of hereditary sensory neuropathy-1 reveals L-serine-responsive deficits in neuronal ganglioside composition and axoglial interactions.


Journal

Cell reports. Medicine
ISSN: 2666-3791
Titre abrégé: Cell Rep Med
Pays: United States
ID NLM: 101766894

Informations de publication

Date de publication:
20 07 2021
Historique:
received: 03 07 2020
revised: 23 04 2021
accepted: 15 06 2021
entrez: 2 8 2021
pubmed: 3 8 2021
medline: 3 8 2021
Statut: epublish

Résumé

Hereditary sensory neuropathy type 1 (HSN1) is caused by mutations in the

Identifiants

pubmed: 34337561
doi: 10.1016/j.xcrm.2021.100345
pii: S2666-3791(21)00194-4
pmc: PMC8324498
doi:

Substances chimiques

Gangliosides 0
Nerve Growth Factors 0
Nodal Protein 0
Sphingolipids 0
Serine 452VLY9402
Caspase 3 EC 3.4.22.-

Types de publication

Journal Article Research Support, N.I.H., Extramural Research Support, Non-U.S. Gov't

Langues

eng

Pagination

100345

Subventions

Organisme : Wellcome Trust
ID : 202747/Z/16/Z
Pays : United Kingdom
Organisme : Wellcome Trust
ID : 202834/Z/16/Z
Pays : United Kingdom
Organisme : NINDS NIH HHS
ID : U54 NS065712
Pays : United States

Informations de copyright

© 2021 The Author(s).

Déclaration de conflit d'intérêts

The authors declare no competing interests.

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Auteurs

Alex J Clark (AJ)

Neural Injury Group, Nuffield Department of Clinical Neuroscience, John Radcliffe Hospital, University of Oxford, Oxford OX3 9DU, UK.

Umaiyal Kugathasan (U)

Centre for Neuromuscular Diseases, Department of Neuromuscular Diseases, UCL Queen Square Institute of Neurology and National Hospital for Neurology and Neurosurgery, London WC1N 3BG, UK.

Georgios Baskozos (G)

Neural Injury Group, Nuffield Department of Clinical Neuroscience, John Radcliffe Hospital, University of Oxford, Oxford OX3 9DU, UK.

David A Priestman (DA)

Department of Pharmacology, University of Oxford, Mansfield Road, Oxford OX1 3QT, UK.

Nadine Fugger (N)

Neural Injury Group, Nuffield Department of Clinical Neuroscience, John Radcliffe Hospital, University of Oxford, Oxford OX3 9DU, UK.

Museer A Lone (MA)

Institute of Clinical Chemistry, University Hospital Zurich, 8091 Zurich, Switzerland.

Alaa Othman (A)

Institute of Clinical Chemistry, University Hospital Zurich, 8091 Zurich, Switzerland.

Ka Hing Chu (KH)

Neural Injury Group, Nuffield Department of Clinical Neuroscience, John Radcliffe Hospital, University of Oxford, Oxford OX3 9DU, UK.

Iulia Blesneac (I)

Neural Injury Group, Nuffield Department of Clinical Neuroscience, John Radcliffe Hospital, University of Oxford, Oxford OX3 9DU, UK.

Emma R Wilson (ER)

Centre for Neuromuscular Diseases, Department of Neuromuscular Diseases, UCL Queen Square Institute of Neurology and National Hospital for Neurology and Neurosurgery, London WC1N 3BG, UK.
Department of Neuromuscular Diseases, UCL Queen Square Institute of Neurology, Queen Square, London WC1N 3BG, UK.

Matilde Laurà (M)

Centre for Neuromuscular Diseases, Department of Neuromuscular Diseases, UCL Queen Square Institute of Neurology and National Hospital for Neurology and Neurosurgery, London WC1N 3BG, UK.
Department of Neuromuscular Diseases, UCL Queen Square Institute of Neurology, Queen Square, London WC1N 3BG, UK.

Bernadett Kalmar (B)

Department of Neuromuscular Diseases, UCL Queen Square Institute of Neurology, Queen Square, London WC1N 3BG, UK.

Linda Greensmith (L)

Centre for Neuromuscular Diseases, Department of Neuromuscular Diseases, UCL Queen Square Institute of Neurology and National Hospital for Neurology and Neurosurgery, London WC1N 3BG, UK.
Department of Neuromuscular Diseases, UCL Queen Square Institute of Neurology, Queen Square, London WC1N 3BG, UK.

Thorsten Hornemann (T)

Institute of Clinical Chemistry, University Hospital Zurich, 8091 Zurich, Switzerland.

Frances M Platt (FM)

Department of Pharmacology, University of Oxford, Mansfield Road, Oxford OX1 3QT, UK.

Mary M Reilly (MM)

Centre for Neuromuscular Diseases, Department of Neuromuscular Diseases, UCL Queen Square Institute of Neurology and National Hospital for Neurology and Neurosurgery, London WC1N 3BG, UK.
Department of Neuromuscular Diseases, UCL Queen Square Institute of Neurology, Queen Square, London WC1N 3BG, UK.

David L Bennett (DL)

Neural Injury Group, Nuffield Department of Clinical Neuroscience, John Radcliffe Hospital, University of Oxford, Oxford OX3 9DU, UK.

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