Ancestral patterns of recessive dystrophic epidermolysis bullosa mutations in Hispanic populations suggest sephardic ancestry.


Journal

American journal of medical genetics. Part A
ISSN: 1552-4833
Titre abrégé: Am J Med Genet A
Pays: United States
ID NLM: 101235741

Informations de publication

Date de publication:
11 2021
Historique:
revised: 11 07 2021
received: 24 05 2021
accepted: 14 07 2021
pubmed: 27 8 2021
medline: 19 2 2022
entrez: 26 8 2021
Statut: ppublish

Résumé

Recessive dystrophic epidermolysis bullosa (RDEB) is a rare genodermatosis caused by mutations in the gene coding for type VII collagen (COL7A1). More than 800 different pathogenic mutations in COL7A1 have been described to date; however, the ancestral origins of many of these mutations have not been precisely identified. In this study, 32 RDEB patient samples from the Southwestern United States, Mexico, Chile, and Colombia carrying common mutations in the COL7A1 gene were investigated to determine the origins of these mutations and the extent to which shared ancestry contributes to disease prevalence. The results demonstrate both shared European and American origins of RDEB mutations in distinct populations in the Americas and suggest the influence of Sephardic ancestry in at least some RDEB mutations of European origins. Knowledge of ancestry and relatedness among RDEB patient populations will be crucial for the development of future clinical trials and the advancement of novel therapeutics.

Identifiants

pubmed: 34435747
doi: 10.1002/ajmg.a.62456
pmc: PMC8668271
mid: NIHMS1745069
doi:

Substances chimiques

COL7A1 protein, human 0
Collagen Type VII 0

Types de publication

Journal Article Research Support, N.I.H., Extramural Research Support, Non-U.S. Gov't Research Support, U.S. Gov't, Non-P.H.S.

Langues

eng

Sous-ensembles de citation

IM

Pagination

3390-3400

Subventions

Organisme : NIAMS NIH HHS
ID : U01 AR075932
Pays : United States
Organisme : NIAMS NIH HHS
ID : P30 AR069632
Pays : United States
Organisme : NIAMS NIH HHS
ID : R01 AR059947
Pays : United States
Organisme : NIAMS NIH HHS
ID : R01AR059947
Pays : United States
Organisme : NIAMS NIH HHS
ID : U01AR075932
Pays : United States

Informations de copyright

© 2021 Wiley Periodicals LLC.

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Auteurs

Emily Mira Warshauer (EM)

Department of Dermatology, University of Colorado School of Medicine, Anschutz Medical Campus, Aurora, Colorado, USA.
Charles C. Gates Center for Regenerative Medicine, University of Colorado School of Medicine, Anschutz Medical Campus, Aurora, Colorado, USA.

Adam Brown (A)

Avotaynu Research Partnership LLC, Englewood, New Jersey, USA.

Ignacia Fuentes (I)

Centro de Genética y Genómica, Facultad de Medicina Clínica Alemana, Universidad del Desarrollo, Santiago, Chile.
Fundación DEBRA Chile, Santiago, Chile.

Jonathan Shortt (J)

Colorado Center for Personalized Medicine, University of Colorado Anschutz Medical Campus, Aurora, Colorado, USA.

Chris Gignoux (C)

Colorado Center for Personalized Medicine, University of Colorado Anschutz Medical Campus, Aurora, Colorado, USA.

Francesco Montinaro (F)

Estonian Biocentre, Institute of Genomics, University of Tartu, Tartu, Estonia.
Department of Biology and Genetics, University of Bari, Bari, Italy.

Mait Metspalu (M)

Estonian Biocentre, Institute of Genomics, University of Tartu, Tartu, Estonia.

Leila Youssefian (L)

Department of Dermatology and Cutaneous Biology, Sidney Kimmel Medical College and Jefferson Institute of Molecular Medicine, Thomas Jefferson University, Philadelphia, Pennsylvania, USA.

Hassan Vahidnezhad (H)

Department of Dermatology and Cutaneous Biology, Sidney Kimmel Medical College and Jefferson Institute of Molecular Medicine, Thomas Jefferson University, Philadelphia, Pennsylvania, USA.

Joanna Jacków (J)

Department of Dermatology, Columbia University, New York, New York, USA.
St. John's Institute of Dermatology, King's College London (Guy's Campus), London, UK.

Angela M Christiano (AM)

Department of Dermatology, Columbia University, New York, New York, USA.
Department of Genetics and Development, Columbia University, New York, New York, USA.

Jouni Uitto (J)

Department of Dermatology and Cutaneous Biology, Sidney Kimmel Medical College and Jefferson Institute of Molecular Medicine, Thomas Jefferson University, Philadelphia, Pennsylvania, USA.

Óscar R Fajardo-Ramírez (ÓR)

DEBRA Mexico, Azteca Guadalupe, Mexico.
Tecnologico de Monterrey, Escuela de Medicina y Ciencias de la Salud, Monterrey, Mexico.

Julio C Salas-Alanis (JC)

DEBRA Mexico, Azteca Guadalupe, Mexico.
Instituto Dermatologico de Jalisco, Zapopan, Mexico.

John A McGrath (JA)

St. John's Institute of Dermatology, King's College London (Guy's Campus), London, UK.

Liliana Consuegra (L)

Fundación DEBRA Colombia, Bogotá, Colombia.

Carolina Rivera (C)

Fundación DEBRA Colombia, Bogotá, Colombia.
Department of Medical Genetics, Pediatric Hospital, Fundacion Cardioinfantil-Universidad del Rosario, Bogotá, Colombia.

Paul A Maier (PA)

Gene by Gene, Genomic Research Center, Houston, Texas, USA.

Goran Runfeldt (G)

Gene by Gene, Genomic Research Center, Houston, Texas, USA.

Doron M Behar (DM)

Estonian Biocentre, Institute of Genomics, University of Tartu, Tartu, Estonia.
Gene by Gene, Genomic Research Center, Houston, Texas, USA.

Karl Skorecki (K)

Azrieli Faculty of Medicine of the Galilee, Bar-Ilan University, Safed, Israel.

Eli Sprecher (E)

Department of Dermatology, Tel-Aviv Sourasky Medical Center, Tel Aviv, Israel.
Department of Human Molecular Genetics, Sackler Faculty of Medicine, Tel-Aviv University, Tel Aviv, Israel.

Francis Palisson (F)

Fundación DEBRA Chile, Santiago, Chile.
Facultad de Medicina Clínica Alemana Universidad del Desarrollo, Santiago, Chile.

David A Norris (DA)

Department of Dermatology, University of Colorado School of Medicine, Anschutz Medical Campus, Aurora, Colorado, USA.
Charles C. Gates Center for Regenerative Medicine, University of Colorado School of Medicine, Anschutz Medical Campus, Aurora, Colorado, USA.

Anna L Bruckner (AL)

Department of Dermatology, University of Colorado School of Medicine, Anschutz Medical Campus, Aurora, Colorado, USA.

Igor Kogut (I)

Department of Dermatology, University of Colorado School of Medicine, Anschutz Medical Campus, Aurora, Colorado, USA.
Charles C. Gates Center for Regenerative Medicine, University of Colorado School of Medicine, Anschutz Medical Campus, Aurora, Colorado, USA.

Ganna Bilousova (G)

Department of Dermatology, University of Colorado School of Medicine, Anschutz Medical Campus, Aurora, Colorado, USA.
Charles C. Gates Center for Regenerative Medicine, University of Colorado School of Medicine, Anschutz Medical Campus, Aurora, Colorado, USA.

Dennis R Roop (DR)

Department of Dermatology, University of Colorado School of Medicine, Anschutz Medical Campus, Aurora, Colorado, USA.
Charles C. Gates Center for Regenerative Medicine, University of Colorado School of Medicine, Anschutz Medical Campus, Aurora, Colorado, USA.

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