Quality of life and phonatory and morphological outcomes in cognitively unimpaired adolescents with Pierre Robin sequence: a cross-sectional study of 72 patients.

Generic quality of life Oral quality of life Outcome Pierre Robin sequence Vocal quality of life

Journal

Orphanet journal of rare diseases
ISSN: 1750-1172
Titre abrégé: Orphanet J Rare Dis
Pays: England
ID NLM: 101266602

Informations de publication

Date de publication:
20 10 2021
Historique:
received: 23 05 2021
accepted: 10 10 2021
entrez: 21 10 2021
pubmed: 22 10 2021
medline: 3 11 2021
Statut: epublish

Résumé

Pierre Robin sequence (PRS) is a heterogeneous condition involving retro(micro)gnathia, glossoptosis and upper airway obstruction, very often with posterior cleft palate. Patients with PRS, either isolated or associated with Stickler syndrome have good intellectual prognosis. Nevertheless, the quality of life in adolescence and the phonatory and morphological outcomes are rarely analysed. We assessed the phonatory and morphological outcomes of 72 cognitively unimpaired adolescents with PRS, studied their oral (COHIP-SF19), vocal (VHI-9i) and generic quality of life (QoL; KIDSCREEN-52), and searched for determinants of these outcomes. Two-thirds of our adolescents retained low or moderate phonation difficulties, but risk factors were not identified. For 14%, morphological results were considered disharmonious, with no link to neonatal retrognathia severity. Only one vs two-stage surgery seemed to affect final aesthetic results. The oral QoL of these adolescents was comparable to that of control patients and was significantly better than that of children with other craniofacial malformations (COHIP-SF19 = 17.5, 15.4 and 25.7, respectively). The oral QoL of the adolescents with non-isolated PRS was significantly worse (COHIP-SF19 = 24.2) than that of control patients and close to that of children with other craniofacial malformations. The vocal QoL of the adolescents (mean [SD] VHI-9i = 7.5 [5.4]) was better than that of patients with other voice pathologies and better when phonation was good. The generic QoL of the adolescents was satisfactory but slightly lower than that of controls, especially in dimensions concerning physical well-being, relationships and autonomy. QoL results were lower for adolescents with non-isolated than isolated PRS. Only non-isolated PRS and low oral QoL affected generic QoL. Morphological or phonatory impairments remain non-rare in adolescents with PRS but do not seem to be directly responsible for altered QoL. These adolescents, especially those with non-isolated PRS, show self-confidence and social-relation fragility. We must focus on long-term functional and psychological results for PRS patients and improve therapy protocols and follow-up, notably those affecting the oral aspects of the disease.

Sections du résumé

BACKGROUND
Pierre Robin sequence (PRS) is a heterogeneous condition involving retro(micro)gnathia, glossoptosis and upper airway obstruction, very often with posterior cleft palate. Patients with PRS, either isolated or associated with Stickler syndrome have good intellectual prognosis. Nevertheless, the quality of life in adolescence and the phonatory and morphological outcomes are rarely analysed. We assessed the phonatory and morphological outcomes of 72 cognitively unimpaired adolescents with PRS, studied their oral (COHIP-SF19), vocal (VHI-9i) and generic quality of life (QoL; KIDSCREEN-52), and searched for determinants of these outcomes.
RESULTS
Two-thirds of our adolescents retained low or moderate phonation difficulties, but risk factors were not identified. For 14%, morphological results were considered disharmonious, with no link to neonatal retrognathia severity. Only one vs two-stage surgery seemed to affect final aesthetic results. The oral QoL of these adolescents was comparable to that of control patients and was significantly better than that of children with other craniofacial malformations (COHIP-SF19 = 17.5, 15.4 and 25.7, respectively). The oral QoL of the adolescents with non-isolated PRS was significantly worse (COHIP-SF19 = 24.2) than that of control patients and close to that of children with other craniofacial malformations. The vocal QoL of the adolescents (mean [SD] VHI-9i = 7.5 [5.4]) was better than that of patients with other voice pathologies and better when phonation was good. The generic QoL of the adolescents was satisfactory but slightly lower than that of controls, especially in dimensions concerning physical well-being, relationships and autonomy. QoL results were lower for adolescents with non-isolated than isolated PRS. Only non-isolated PRS and low oral QoL affected generic QoL.
CONCLUSION
Morphological or phonatory impairments remain non-rare in adolescents with PRS but do not seem to be directly responsible for altered QoL. These adolescents, especially those with non-isolated PRS, show self-confidence and social-relation fragility. We must focus on long-term functional and psychological results for PRS patients and improve therapy protocols and follow-up, notably those affecting the oral aspects of the disease.

Identifiants

pubmed: 34670591
doi: 10.1186/s13023-021-02072-0
pii: 10.1186/s13023-021-02072-0
pmc: PMC8527704
doi:

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

442

Informations de copyright

© 2021. The Author(s).

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Auteurs

Béatrice Thouvenin (B)

General Paediatrics Unit, Necker University Hospital, APHP, 149 rue de Sèvres, 75015, Paris, France.
Referral Centre for Rare Diseases "Syndrome de Pierre Robin et troubles de succion-déglutition congénitaux», Necker University Hospital, APHP, Paris, France.

Véronique Soupre (V)

Referral Centre for Rare Diseases "Syndrome de Pierre Robin et troubles de succion-déglutition congénitaux», Necker University Hospital, APHP, Paris, France.
Paediatric Maxillofacial and Plastic Surgery Unit, Necker University Hospital, APHP, Paris, France.

Marie-Anne Caillaud (MA)

IQVIA, Paris, France.

Charlotte Henry-Mestelan (C)

General Paediatrics Unit, Necker University Hospital, APHP, 149 rue de Sèvres, 75015, Paris, France.

Christel Chalouhi (C)

General Paediatrics Unit, Necker University Hospital, APHP, 149 rue de Sèvres, 75015, Paris, France.
Referral Centre for Rare Diseases "Syndrome de Pierre Robin et troubles de succion-déglutition congénitaux», Necker University Hospital, APHP, Paris, France.

Bachar Houssamo (B)

Referral Centre for Rare Diseases "Syndrome de Pierre Robin et troubles de succion-déglutition congénitaux», Necker University Hospital, APHP, Paris, France.
Paediatric Maxillofacial and Plastic Surgery Unit, Necker University Hospital, APHP, Paris, France.

Cécile Chapuis (C)

Paediatric Maxillofacial and Plastic Surgery Unit, Necker University Hospital, APHP, Paris, France.

Katia Lind (K)

General Paediatrics Unit, Necker University Hospital, APHP, 149 rue de Sèvres, 75015, Paris, France.

Aurélie Royer (A)

General Paediatrics Unit, Necker University Hospital, APHP, 149 rue de Sèvres, 75015, Paris, France.
Referral Centre for Rare Diseases "Syndrome de Pierre Robin et troubles de succion-déglutition congénitaux», Necker University Hospital, APHP, Paris, France.

Nancy Vegas (N)

General Paediatrics Unit, Necker University Hospital, APHP, 149 rue de Sèvres, 75015, Paris, France.
Referral Centre for Rare Diseases "Syndrome de Pierre Robin et troubles de succion-déglutition congénitaux», Necker University Hospital, APHP, Paris, France.
Imagine Institute, Paris, France.

Jeanne Amiel (J)

Imagine Institute, Paris, France.
Genetics Department, Necker University Hospital, APHP, Paris, France.
Paris University, Paris, France.

Gérard Couly (G)

Paediatric Maxillofacial and Plastic Surgery Unit, Necker University Hospital, APHP, Paris, France.
Paris University, Paris, France.

Arnaud Picard (A)

Referral Centre for Rare Diseases "Syndrome de Pierre Robin et troubles de succion-déglutition congénitaux», Necker University Hospital, APHP, Paris, France.
Paediatric Maxillofacial and Plastic Surgery Unit, Necker University Hospital, APHP, Paris, France.
Paris University, Paris, France.

Laurence Vaivre-Douret (L)

Imagine Institute, Paris, France.
Paris University, Paris, France.
INSERM Unit 1178, CESP, Paris, France.

Véronique Abadie (V)

General Paediatrics Unit, Necker University Hospital, APHP, 149 rue de Sèvres, 75015, Paris, France. veronique.abadie@aphp.fr.
Referral Centre for Rare Diseases "Syndrome de Pierre Robin et troubles de succion-déglutition congénitaux», Necker University Hospital, APHP, Paris, France. veronique.abadie@aphp.fr.
Imagine Institute, Paris, France. veronique.abadie@aphp.fr.
Paris University, Paris, France. veronique.abadie@aphp.fr.
INSERM Unit 1178, CESP, Paris, France. veronique.abadie@aphp.fr.

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