Parkinson's disease-dementia in trans LRP10 and GBA variants: Response to deep brain stimulation.


Journal

Parkinsonism & related disorders
ISSN: 1873-5126
Titre abrégé: Parkinsonism Relat Disord
Pays: England
ID NLM: 9513583

Informations de publication

Date de publication:
11 2021
Historique:
received: 23 08 2021
revised: 06 10 2021
accepted: 16 10 2021
pubmed: 29 10 2021
medline: 4 2 2022
entrez: 28 10 2021
Statut: ppublish

Résumé

We report on a patient with Parkinson's disease and dementia who underwent DBS with excellent response in motor features; the genotype is heterozygous for a novel LRP10 variant in trans with a GBA variant. He had a more severe phenotype compared to the father who only carries the LRP10 variant.

Identifiants

pubmed: 34710740
pii: S1353-8020(21)00375-8
doi: 10.1016/j.parkreldis.2021.10.020
pii:
doi:

Substances chimiques

LDL-Receptor Related Proteins 0
LRP10 protein, human 0
GBA protein, human EC 3.2.1.45
Glucosylceramidase EC 3.2.1.45

Types de publication

Case Reports Letter

Langues

eng

Sous-ensembles de citation

IM

Pagination

72-75

Commentaires et corrections

Type : CommentIn
Type : CommentIn

Informations de copyright

Copyright © 2021 Elsevier Ltd. All rights reserved.

Auteurs

Marcella Neri (M)

Unit of Medical Genetics, Department of Medical Sciences, University of Ferrara, Ferrara, Italy. Electronic address: nremcl@unife.it.

Arianna Braccia (A)

Department of Neuroscience and Rehabilitation, Azienda Ospedaliera-Universitaria S. Anna, Fer-rara, Italy.

Celeste Panteghini (C)

Medical Genetics and Neurogenetics Unit, Fondazione IRCCS Istituto Neurologico "Carlo Besta", Milan, Italy.

Barbara Garavaglia (B)

Medical Genetics and Neurogenetics Unit, Fondazione IRCCS Istituto Neurologico "Carlo Besta", Milan, Italy.

Francesca Gualandi (F)

Unit of Medical Genetics, Department of Medical Sciences, University of Ferrara, Ferrara, Italy.

Michele Alessandro Cavallo (MA)

Department of Neuroscience and Rehabilitation, Azienda Ospedaliera-Universitaria S. Anna, Fer-rara, Italy.

Alba Scerrati (A)

Department of Neuroscience and Rehabilitation, Azienda Ospedaliera-Universitaria S. Anna, Fer-rara, Italy.

Alessandra Ferlini (A)

Unit of Medical Genetics, Department of Medical Sciences, University of Ferrara, Ferrara, Italy.

Mariachiara Sensi (M)

Department of Neuroscience and Rehabilitation, Azienda Ospedaliera-Universitaria S. Anna, Fer-rara, Italy.

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Classifications MeSH