HLA-G gene editing in tumor cell lines as a novel alternative in cancer immunotherapy.


Journal

Scientific reports
ISSN: 2045-2322
Titre abrégé: Sci Rep
Pays: England
ID NLM: 101563288

Informations de publication

Date de publication:
12 11 2021
Historique:
received: 22 01 2021
accepted: 22 10 2021
entrez: 13 11 2021
pubmed: 14 11 2021
medline: 27 1 2022
Statut: epublish

Résumé

Cancer immunotherapies based mainly on the blockade of immune-checkpoint (IC) molecules by anti-IC antibodies offer new alternatives for treatment in oncological diseases. However, a considerable proportion of patients remain unresponsive to them. Hence, the development of novel clinical immunotherapeutic approaches and/or targets are crucial.W In this context, targeting the immune-checkpoint HLA-G/ILT2/ILT4 has caused great interest since it is abnormally expressed in several malignancies generating a tolerogenic microenvironment. Here, we used CRISPR/Cas9 gene editing to block the HLA-G expression in two tumor cell lines expressing HLA-G, including a renal cell carcinoma (RCC7) and a choriocarcinoma (JEG-3). Different sgRNA/Cas9 plasmids targeting HLA-G exon 1 and 2 were transfected in both cell lines. Downregulation of HLA-G was reached to different degrees, including complete silencing. Most importantly, HLA-G - cells triggered a higher in vitro response of immune cells with respect to HLA-G + wild type cells. Altogether, we demonstrated for the first time the HLA-G downregulation through gene editing. We propose this approach as a first step to develop novel clinical immunotherapeutic approaches in cancer.

Identifiants

pubmed: 34773056
doi: 10.1038/s41598-021-01572-0
pii: 10.1038/s41598-021-01572-0
pmc: PMC8589947
doi:

Substances chimiques

HLA-G Antigens 0
RNA, Guide 0

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

22158

Subventions

Organisme : Consejo Nacional de Investigaciones Científicas y Técnicas
ID : PIP 112-20150100723
Organisme : Scientific and Technical Research Fund (FONCyT)
ID : PICT-2015-1469

Informations de copyright

© 2021. The Author(s).

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Auteurs

María Belén Palma (MB)

Cátedra de Citología, Histología y Embriología, Facultad de Ciencias Médicas, Universidad Nacional de La Plata, La Plata, Argentina.
LIAN-CONICET, Fundación FLENI, Buenos Aires, Argentina.

Diana Tronik-Le Roux (D)

Atomic Energy and Alternative Energies Agency (CEA), Hematology and Immunology Research Division, Saint-Louis Hospital, Paris, France.
U976 HIPI Unit, University of Paris, Paris, France.

Guadalupe Amín (G)

LIAN-CONICET, Fundación FLENI, Buenos Aires, Argentina.

Sheila Castañeda (S)

LIAN-CONICET, Fundación FLENI, Buenos Aires, Argentina.

Alan M Möbbs (AM)

LIAN-CONICET, Fundación FLENI, Buenos Aires, Argentina.

María Agustina Scarafia (MA)

LIAN-CONICET, Fundación FLENI, Buenos Aires, Argentina.

Alejandro La Greca (A)

LIAN-CONICET, Fundación FLENI, Buenos Aires, Argentina.

Marina Daouya (M)

Atomic Energy and Alternative Energies Agency (CEA), Hematology and Immunology Research Division, Saint-Louis Hospital, Paris, France.
U976 HIPI Unit, University of Paris, Paris, France.

Isabelle Poras (I)

Atomic Energy and Alternative Energies Agency (CEA), Hematology and Immunology Research Division, Saint-Louis Hospital, Paris, France.
U976 HIPI Unit, University of Paris, Paris, France.

Ana María Inda (AM)

Cátedra de Citología, Histología y Embriología, Facultad de Ciencias Médicas, Universidad Nacional de La Plata, La Plata, Argentina.
Comisión de Investigaciones Científicas (CIC), Buenos Aires, Argentina.

Lucía N Moro (LN)

LIAN-CONICET, Fundación FLENI, Buenos Aires, Argentina.
Consejo Nacional de Investigaciones Científicas y Técnicas (CONICET), Buenos Aires, Argentina.

Edgardo D Carosella (ED)

Atomic Energy and Alternative Energies Agency (CEA), Hematology and Immunology Research Division, Saint-Louis Hospital, Paris, France.
U976 HIPI Unit, University of Paris, Paris, France.

Marcela N García (MN)

Cátedra de Citología, Histología y Embriología, Facultad de Ciencias Médicas, Universidad Nacional de La Plata, La Plata, Argentina. mngarcia@med.unlp.edu.ar.

Santiago G Miriuka (SG)

LIAN-CONICET, Fundación FLENI, Buenos Aires, Argentina. smiriuka@fleni.org.ar.
Consejo Nacional de Investigaciones Científicas y Técnicas (CONICET), Buenos Aires, Argentina. smiriuka@fleni.org.ar.

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